26 completed, 11 unknown, 3 not yet recruiting, 3 recruiting. 52 Not applicable.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 52 | Completed 26, Unknown 11, Not yet recruiting 3, Recruiting 3, Terminated 3, Withdrawn 3, Enrolling by invitation 2, Active not recruiting 1 |
Follow Dwarfism: new trials by email Literature Review of Dwarfism trials Research Report on Dwarfism
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Evaluation of (Cardio)Metabolic and Auxological Outcomes of GHD Patients Under rhGH or LAGH With Stratification According to IGF-1 Levels metabolic and auxological outcomes - Growth Hormone Deficiency | Not applicable | Not yet recruiting | Cliniques universitaires Saint-Luc- Université Catholique de Louvain | 300 | 2026-07-01 | 2026-05-11 |
| REMS25: Study on the Use of REMS Technology in Diseases Commonly Associated With Reduced Bone Mineral Density (BMD) REMS - Osteogenesis Imperfecta, Osteoporosis | Not applicable | Recruiting | Meyer Children's Hospital IRCCS | 100 | 2025-12-04 | 2026-02-17 |
| Palliative Care Needs of Children With Rare Diseases and Their Families Family Centered pediatric palliative care for family caregivers of children with rare diseases. - Trisomy 13 Syndrome, Arthrogryposis Congenita Multiplex With Intestinal Atresia | Not applicable | Enrolling by invitation | Children's National Research Institute | 480 | 2025-10-02 | 2026-01-28 |
| Prospective Evaluation of OptiThyDose OptiThyDose - Thyroid Diseases, Congenital Hypothyroidism | Not applicable | Recruiting | University Children's Hospital Basel | 150 | 2025-08-28 | 2026-10-02 |
| BELux Children OutcoME During A(@)Dulthood With GHD Biological Sample - Growth Hormone Deficiency, Adult Growth Hormone Deficiency | Not applicable | Recruiting | Cliniques universitaires Saint-Luc- Université Catholique de Louvain | 200 | 2025-05-21 | 2026-09-21 |
| The Dosage Exploration Study of PEG-rhGH for Treating Short Stature in Prepubertal and Pubertal Children PEG-rhGH, GnRHa - Short Stature | Not applicable | Not yet recruiting | Second Affiliated Hospital of Wenzhou Medical University | 240 | 2025-01-15 | 2025-01-10 |
| Growing up With the Young Endocrine Support System (YESS!) YESS! game, Snake '97, Transition-toolkit - Congenital Adrenal Hyperplasia, Hypogonadotropic Hypogonadism | Not applicable | Not yet recruiting | dr. Laura C. G. de Graaff-Herder | 160 | 2024-12-01 | 2023-09-07 |
| Quality of Life and Long-term Outcome of Adequately Treated Congenital Hypothyroidism SF36 test, WAIS IV test, SCL-90 psychopathological screening questionnaire - Congenital Hypothyroidism | Not applicable | Enrolling by invitation | Federico II University | 150 | 2024-09-06 | 2025-03-07 |
| Evaluation of the Propensity of Patients Under rhGH to Envision a Modification of Their Treatment Regimen Toward LAGH Questionnaire - Growth Hormone Deficiency | Not applicable | Completed | Cliniques universitaires Saint-Luc- Université Catholique de Louvain | 500 | 2024-04-15 | 2026-09-21 |
| Mauriac Syndrome: Isotopic Techniques and Genetic Analysis oral glucose load, exercise test - Diabetes Mellitus, Short Stature | Not applicable | Completed | University of Lausanne | 6 | 2022-01-17 | 2024-05-08 |
| The Effect of Myofascial Release Technique on Sportive Performance, Balance and Injury Risk in Runners Myofascial therapy - Runt | Not applicable | Unknown | Istanbul Medipol University Hospital | 49 | 2021-09-01 | 2022-05-26 |
| Fluids Administration During Combined Clonidine-Arginine Growth Hormone Stimulation Test 9% Sodium Chloride (NaCl) IV - Growth Hormone Deficiency | Not applicable | Withdrawn | Rabin Medical Center | 2020-12-01 | 2022-02-22 | |
| Nutritional Stimulation of Growth in Children With Short Stature Essential Amino Acid (EAA) group, Placebo - Nutritional Stunting, Growth Failure | Not applicable | Completed | Arkansas Children's Hospital Research Institute | 24 | 2020-09-09 | 2024-07-31 |
| Effects of Growth Hormone and IGF-1 on Anabolic Signals and Stem Cell Recruitment in Human Skeletal Muscle Genotropin miniquick 0.5 mg, injection - Growth Hormone Deficiency, Growth Hormone Treatment | Not applicable | Unknown | University of Aarhus | 12 | 2019-04-30 | 2019-09-26 |
| Intervention in Chronic Pediatric Patients and Their Families. Ten Vida (10Vida) - Type 1 Diabetes, Allergic Rhinitis | Not applicable | Completed | University of Valencia | 500 | 2019-02-04 | 2024-03-20 |
| Assessment of the Acute Effect of IP Placebo, IP - Deficiency Growth Hormone | Not applicable | Completed | Vedic Lifesciences Pvt. Ltd. | 32 | 2018-07-19 | 2019-05-31 |
| Long Term Effects of Nutritional Supplementation on Final Height Gender specific nutritional standardized formula, Follow-up only - Growth Disorders, Low Weight | Not applicable | Withdrawn | Rabin Medical Center | 2018-06-01 | 2019-12-27 | |
| Development and Validation of a Self-assessment System Based on a Mobile App to Manage Adult Growth Hormone Deficiency Use of "MAGHD App/MAGHD Framework" - Growth Hormone Deficiency | Not applicable | Completed | Azienda Ospedaliero-Universitaria di Modena | 83 | 2018-01-17 | 2025-03-14 |
| Effect of Nutritional Formula Supplementation on Growth Rate of Growth Hormone (GH) Treated Children With Growth Hormone Deficiency (GHD) After the Second Year of Therapy Nutritional supplementation standardized formula, Placebo - IGHD - Isolated Growth Hormone Deficiency, Growth Retardation | Not applicable | Unknown | Rabin Medical Center | 64 | 2017-11-01 | 2024-03-26 |
| Bone Age Assessment in Children Using Ultrasound Compared to Wrist X-ray SonicBone Ultrasound, Wrist X-ray - Short Stature, Growth Disorders | Not applicable | Unknown | Meir Medical Center | 300 | 2017-06-01 | 2019-12-09 |
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Dwarfism, Pituitary (29) · Congenital Hypothyroidism (6) · Insulin Resistance (3) · Acromegaly (2) · Anxiety Disorders (2) · Bone Diseases, Metabolic (2) · Cockayne Syndrome (2) · Depression (2) · Diabetes Mellitus (2) · Growth Disorders (2) · Obesity (2) · Osteoporosis (2) · Pituitary Diseases (2) · Prader-Willi Syndrome (2)
Musculoskeletal Diseases (52) · Bone Diseases (50) · Bone Diseases, Developmental (50) · Endocrine System Diseases (47) · Bone Diseases, Endocrine (35) · Nervous System Diseases (33) · Brain Diseases (29) · Central Nervous System Diseases (29) · Hypopituitarism (29) · Hypothalamic Diseases (29) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (28) · Genetic Diseases, Inborn (28) · Pituitary Diseases (27) · Nutritional and Metabolic Diseases (16)
Growth Hormone (6) · Human Growth Hormone (5) · Blood Specimen Collection (2) · Sodium Chloride (2) · Thyroxine (2) · Amino Acids, Essential (1) · Anastrozole (1) · Arginine (1) · Calcium (1) · Desflurane (1) · Excitatory Amino Acids (1) · Exercise Test (1) · Hematologic Tests (1) · High-Intensity Interval Training (1) · Injections (1)
Rabin Medical Center (5) · University of Aarhus (4) · Assistance Publique - Hôpitaux de Paris (3) · Cliniques universitaires Saint-Luc- Université Catholique de Louvain (3) · Federico II University (2) · Massachusetts General Hospital (2) · Meir Medical Center (2) · Arkansas Children's Hospital Research Institute (1) · Azienda Ospedaliero-Universitaria di Modena (1) · Baylor College of Medicine (1) · Bilen, Fikri Erkal, M.D. (1) · Boston Children's Hospital (1) · Children's Mercy Hospital Kansas City (1) · Children's National Research Institute (1) · Connecticut Children's Medical Center (1)
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PMID 16394080, PMID 16522693, PMID 16675931, PMID 17164301, PMID 17652219, PMID 18252944, PMID 19181452, PMID 19366847, PMID 20061426, PMID 20598930, PMID 20610593, PMID 20719837, PMID 21525160, PMID 22416078, PMID 23264396, PMID 23967125, PMID 24030943, PMID 25894639, PMID 28025328, PMID 29059381, PMID 30446499, PMID 31145125, PMID 35079678, PMID 35226254, PMID 36107810, PMID 36662765
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