Bone Diseases, Developmental: Clinical Trials

1,035 trials for Bone Diseases, Developmental, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

544 completed, 133 recruiting, 126 unknown, 103 terminated. 225 Not applicable, 191 Phase 2, 124 Phase 3, 84 Phase 1, 75 Phase 4.

By phase and status

PhaseTrialsStatus
Not applicable225Completed 116, Unknown 42, Recruiting 21, Terminated 15, Not yet recruiting 12, Active not recruiting 10, Withdrawn 6, Enrolling by invitation 2, Suspended 1
Phase 2191Completed 96, Terminated 35, Active not recruiting 17, Recruiting 15, Unknown 13, Withdrawn 6, Enrolling by invitation 5, Not yet recruiting 3, Suspended 1
Phase 3124Completed 70, Terminated 18, Unknown 12, Recruiting 10, Active not recruiting 7, Enrolling by invitation 2, Not yet recruiting 2, Withdrawn 2, Suspended 1
Phase 184Completed 53, Terminated 12, Active not recruiting 6, Recruiting 5, Unknown 3, Not yet recruiting 2, Withdrawn 2, Suspended 1
Phase 475Completed 39, Terminated 18, Unknown 11, Recruiting 4, Withdrawn 3
Early Phase 14Unknown 3, Completed 1

Follow Bone Diseases, Developmental: new trials by email Literature Review of Bone Diseases, Developmental trials Research Report on Bone Diseases, Developmental

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
The AgRP and GH/IGF-1 Axis in Children
Growth Hormone Deficiency
Not yet recruitingColumbia University1562027-06-102026-09-25
Evaluation of an Intensified Systematic Screening for Congenital Hypothyroidism in Premature Newborns
Blood test - Congenital Hypothyroidism
Not yet recruitingUniversity Hospital, Lille16002027-03-012026-05-22
Phase 3 Long Term Safety Extension Study of LUM-201 in Children With Growth Hormone Deficiency
LUM-201 - Growth Hormone Deficiency (GHD)
Phase 3Not yet recruitingLumos Pharma1502027-02-012026-07-08
Mesenchymal Cell Therapy in Osteogenesis Imperfecta (OI)
Bone marrow-derived mesenchymal stromal cells (MSCs) - Osteogenesis Imperfecta, Osteogenesis Imperfecta Type III
Phase 1 / Phase 2Not yet recruitingEmory University122027-01-012026-05-08
Morbidity in Adults With Craniofacial Fibrous Dysplasia: The CRANIO-DF Study
No Intervention: Observational Cohort - Craniofacial Fibrous Dysplasia
Not yet recruitingCentre Hospitalier Universitaire de Nice5002026-12-012026-10-13
Biopsychosocial Risk Influences on the Development and Generation of Early-Onset Chronic Pain
Not applicable- observational study - Juvenile Idiopathic Arthritis (JIA), Fibromyalgia
RecruitingChildren's Hospital Medical Center, Cincinnati6002026-10-012026-10-16
Effects of Tummy Time Associated With Therapeutic Positioning in Premature Newborns With Cranial Asymmetry
Tummy Time Protocol - Premature Newborns, Cranial Asymmetry
Not applicableNot yet recruitingHospital de Clinicas de Porto Alegre3002026-10-012026-09-18
Frontal Reconstruction Without Orbital Advancement for Moderate Metopic Craniosynostosis
Frontal vault remodelling without orbital advancement - Metopic Craniosynostosis, Craniosynostosis
Not applicableNot yet recruitingAssiut University152026-10-012026-09-23
A Study Evaluating Ficerafusp Alfa (BCA101) QW in Combination With Pembrolizumab vs Alternative Ficerafusp Alfa Dosing in 1L R or M HNSCC
Ficerafusp alfa, Pembrolizumab (KEYTRUDA®) - Metastatic Head and Neck Squamous Cell Carcinoma, Recurrent Head and Neck Squamous Cell Carcinoma
Phase 2RecruitingBicara Therapeutics1602026-09-012026-10-13
Multimodal Mechanical, Tissue, Architectural, and Histological Evaluation of the Bone and Sutures of the Parietal Bone in an Infant With Craniosynostosis.
Biological sample, bones sample and questionaires. - Craniostenosis
Not yet recruitingHospices Civils de Lyon802026-09-012026-06-16
Morphology in Oral Rare Syndromes & Artificial Intelligence for Clinical Diagnosis
intra-oral 3D optical impression - Osteogenesis Imperfecta, Rare Bone Disorders
Not applicableNot yet recruitingUniversity Hospital, Bordeaux2402026-09-012026-06-24
Treatment for "Asymmetric Crying Facies"
Botulinium toxin type A injection - Hemifacial Microsomia, Facial Nerve Paralysis
Not applicableRecruitingXiaolei Jin602026-08-072026-09-28
A Dose REgimen-Finding Study of AGA2115 in Chinese Patients With Osteogenesis ImpeRfecta (EIR)
AGA2115 - Osteogenesis Imperfecta (OI)
Phase 2RecruitingAngitia Biopharmaceuticals Guangzhou Limited482026-07-142026-09-22
Evaluation of (Cardio)Metabolic and Auxological Outcomes of GHD Patients Under rhGH or LAGH With Stratification According to IGF-1 Levels
metabolic and auxological outcomes - Growth Hormone Deficiency
Not applicableNot yet recruitingCliniques universitaires Saint-Luc- Université Catholique de Louvain3002026-07-012026-05-11
Evaluation of the Safety and Effectiveness of the CORUS™ Posterior Cervical Stabilization System 3D (PCSS 3D) for the Treatment of 2-level Cervical Degenerative Disease
Circumferential Cervical Fusion (CCF), Anterior Cervical Discectomy and Fusion - Degenerative Disc Disease(DDD)
Not applicableNot yet recruitingProvidence Medical Technology, Inc.2252026-06-302026-07-23
Futibatinib (TAS-120) in Patients With Advanced Biliary Tract Cancer
Futibatinib, Zimberelimab, Durvalumab - Biliary Tract Cancer
Phase 3RecruitingTaiho Pharmaceutical Co., Ltd.7842026-06-242026-07-17
SPSIPB Versus SAPB for Postoperative Analgesia After Minimally Invasive Repair of Pectus Excavatum
Postoperative Analgesia Protocol, Bispectral Index Monitoring, Serratus Posterior Superior Intercostal Plane Block - Pectus Excavatum, Chest Deformities
RecruitingMarmara University802026-06-222026-07-13
Gene-Modified Stem Cell Therapy for Children With Autosomal Recessive Osteopetrosis (ARO)
FT024 - Osteopetrosis
Phase 1 / Phase 2RecruitingFondazione Telethon82026-06-202026-06-24
Safety, Pharmacokinetic (PK) Profile and Efficacy of Inpegsomatropin Injection in Adults With Growth Hormone Deficiency
Inpegsomatropin Injection, Placebo for Inpegsomatropin Injection - Adult Growth Hormone Deficiency
Phase 2RecruitingXiamen Amoytop Biotech Co., Ltd.362026-06-102026-07-22
GB06 Phase III Trial for Pediatric Growth Hormone Deficiency
GB06, Norditropin®FlexProTM - Growth Hormone Deficiency (GHD), Growth Hormone Deficiency in Children
Phase 3RecruitingKexing Biopharm Co., Ltd.1922026-06-062026-06-10

Showing 20 of 1035. Sign in to see all of them.

Narrower conditions

Dwarfism, Pituitary (252)  ·  Dwarfism (99)  ·  Osteogenesis Imperfecta (84)  ·  Funnel Chest (77)  ·  Marfan Syndrome (61)  ·  Camurati-Engelmann Syndrome (58)  ·  Craniosynostoses (49)  ·  Achondroplasia (46)  ·  Basal Cell Nevus Syndrome (35)  ·  Acrocephalosyndactylia (33)  ·  Leg Length Inequality (30)  ·  Bone Diseases (28)  ·  Klippel-Feil Syndrome (27)  ·  Turner Syndrome (27)  ·  Congenital Hypothyroidism (26)

Broader conditions

Musculoskeletal Diseases (1014)  ·  Bone Diseases (1007)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (701)  ·  Genetic Diseases, Inborn (447)  ·  Congenital Abnormalities (396)  ·  Endocrine System Diseases (390)  ·  Nervous System Diseases (343)  ·  Dwarfism (302)  ·  Osteochondrodysplasias (294)  ·  Central Nervous System Diseases (293)  ·  Brain Diseases (287)  ·  Bone Diseases, Endocrine (286)  ·  Musculoskeletal Abnormalities (269)  ·  Hypothalamic Diseases (265)

Interventions

Human Growth Hormone (95)  ·  Growth Hormone (56)  ·  Blood Specimen Collection (16)  ·  vosoritide (13)  ·  somapacitan (11)  ·  Losartan (10)  ·  Sodium Chloride (9)  ·  infigratinib (9)  ·  Atenolol (7)  ·  Exercise (7)  ·  Saline Solution (7)  ·  Surveys and Questionnaires (7)  ·  setrusumab (7)  ·  Cyclophosphamide (6)  ·  Denosumab (6)

Sponsors

Novo Nordisk A/S (29)  ·  Pfizer (24)  ·  Changchun GeneScience Pharmaceutical Co., Ltd. (18)  ·  Hospices Civils de Lyon (18)  ·  BioMarin Pharmaceutical (16)  ·  Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) (16)  ·  Baylor College of Medicine (15)  ·  DePuy International (13)  ·  National Human Genome Research Institute (NHGRI) (13)  ·  Children's Hospital Medical Center, Cincinnati (12)  ·  University of Aarhus (12)  ·  Assistance Publique - Hôpitaux de Paris (10)  ·  Columbia University (10)  ·  Federico II University (10)  ·  Istituto Ortopedico Rizzoli (10)

Countries

United States (412)  ·  France (150)  ·  Italy (122)  ·  United Kingdom (110)  ·  Germany (89)  ·  Spain (80)  ·  Canada (68)  ·  Australia (65)  ·  Turkey (Türkiye) (54)  ·  China (49)  ·  Japan (49)  ·  Belgium (43)  ·  Denmark (42)  ·  Poland (39)  ·  Netherlands (37)

Top investigators

Ervin Epstein, MD (5)  ·  Alison M Boyce, M.D. (4)  ·  Leslie G Biesecker, M.D. (4)  ·  Will Charlton, MD (4)  ·  Christine Alvarez, MD (3)

Results publications

PMID 38649657, PMID 42470570, PMID 30935731, PMID 31269546, PMID 34431071, PMID 36380045, PMID 39740666, PMID 17911499, PMID 18395480, PMID 22508317, PMID 22788856, PMID 23658497, PMID 24291224, PMID 28566441, PMID 28624480, PMID 29671202, PMID 31305924, PMID 31972476, PMID 32461347, PMID 33571362, PMID 33709288, PMID 33754315, PMID 34649967, PMID 35342457, PMID 36947589, PMID 38685585, PMID 39305160, PMID 39510802, PMID 40919719, PMID 42144862, PMID 10022400, PMID 10199767, PMID 10199774, PMID 10372687, PMID 10405442, PMID 10453734, PMID 10535539, PMID 10589640, PMID 10598807, PMID 10831929, PMID 11134092, PMID 11203878, PMID 11207626, PMID 11273062, PMID 11288855, PMID 11344175, PMID 11381256, PMID 11415615, PMID 11415789, PMID 11479750

NIH funding

2016 (11), 2018 (8), 2015 (6), 2017 (6), 2019 (6), 2014 (5), 2023 (5), 2008 (3), 2004 (2), 2005 (2), R01CA109584 (2), R01DK110771 (2), R01HL085268 (2), U01TR001263 (2), 2025 (1)