28 completed, 6 recruiting, 6 terminated, 4 not yet recruiting. 20 Not applicable, 6 Phase 1, 6 Phase 2, 1 Phase 3, 1 Phase 4.
Follow Neuromuscular Disease: new trials by email Literature Review of Neuromuscular Disease trials Research Report on Neuromuscular Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Hyperthermia in Patients With Chronic Primary Pain - Effects on Thermoregulation, Somatosensory System and Movement Evoked Pain serial whole body hyperthermia - Hyperthermia, Chronic Primary Pain | Not applicable | Not yet recruiting | Bern University of Applied Sciences | 60 | 2026-12-01 | 2026-09-30 |
| A Clinical Trial of Early Ventilation in Amyotrophic Lateral Sclerosis (EVENT ALS) Non-invasive ventilation - Amyotrophic Lateral Sclerosis (ALS), Chronic Respiratory Failure | Phase 2 | Recruiting | University of Pennsylvania | 48 | 2026-06-11 | 2026-06-26 |
| Connect-One: Early Feasibility Study of Connexus® Brain-Computer Interface (BCI) Connexus Brain-Computer Interface - Amyotrophic Lateral Sclerosis, Neuromuscular Disease | Not applicable | Recruiting | Paradromics | 2 | 2026-03-31 | 2026-04-14 |
| New Technological Pathway for Gait Rehabilitation Innovative technology pathway for gait neurorehabilitation, Conventional gait rehabilitation strategy - Neurological Diseases or Conditions, Cardiovascular Diseases | Not applicable | Not yet recruiting | IRCCS Centro Neurolesi Bonino Pulejo | 60 | 2025-03-01 | 2025-03-05 |
| Validation and Scaling of Screening Program for Undiagnosed Myasthenia Gravis-Social Media Campaign Paired With a Self-moderated Assessment Social media recruitment, Self-Assessment, Follow-up - Myasthenia Gravis, Neuromuscular Disease | Recruiting | ZS Associates | 1000 | 2025-02-26 | 2025-03-10 | |
| The Prevalence of RYR1-related Disease Neuromuscular Disease, Malignant Hyperthermia | Not yet recruiting | King's College London | 2000 | 2025-02-01 | 2025-01-24 | |
| The Effects of a Dynamic Arm Support in Daily Life Dynamic arm support - Neuromuscular Disease, Neuromuscular Disability | Recruiting | Hasselt University | 50 | 2024-12-02 | 2025-08-13 | |
| A Phase 3 Study of NTLA-2001 in ATTRv-PN nexiguran ziclumeran, Normal Saline as Placebo - Neuromuscular Disease, Neuromuscular Diseases (NMD) | Phase 3 | Recruiting | Intellia Therapeutics | 60 | 2024-11-22 | 2026-04-16 |
| Overview: Use of Respiratory Support At Home in Children Sleep Apnea Syndromes in Children, Obesity in Children | Not yet recruiting | University Hospital, Grenoble | 30 | 2024-11-01 | 2024-11-18 | |
| Ultrasonographic Muscle Assessment and Functional Scales in Spinal Muscular Atrophy Ultrasonographic Assessment - Spinal Muscular Atrophy (SMA), Neuromuscular Disease | Unknown | Istanbul University - Cerrahpasa | 34 | 2024-05-01 | 2024-09-24 | |
| Ultrasound Detection of Early Facial Muscle Changes in FSHD: Thickness and Echo Intensity Findings Facioscapulohumeral Muscular Dystrophy, Facioscapulohumeral Muscular Dystrophy 1 | Completed | Koç University | 39 | 2023-09-01 | 2026-01-09 | |
| Manual Therapy and Inspiratory Muscle Training in Neuromuscular Disease inspiratory muscle training, Manual therapy, Conventional physiotherapy programme - Neuromuscular Disease, Inspiratory Muscle Training | Not applicable | Completed | Istinye University | 28 | 2021-08-15 | 2026-04-13 |
| B3 for NMD: Bench to Bedside and Back B3 for NMD: Bench to Bedside and Back - Neuromuscular Disease | Enrolling by invitation | Ottawa Hospital Research Institute | 500 | 2019-05-06 | 2025-12-30 | |
| Feasibility of Virtual Reality in Children With Neuromuscular Disease, Effectiveness of Virtual Reality and Biofeedback Virtual Reality Training, Biofeedback Training, Conventional rehabilitation - Neuromuscular Disease, Duchenne Muscular Dystrophy | Not applicable | Completed | Merve Kurt | 24 | 2019-02-01 | 2026-04-23 |
| Comparison of a Hyperinflation Mode and Air Stacking on Neuromuscular Patients Under Volumetric Ventilation increase of cough peak flow ("Astral ventilator") - Neuromuscular Disease | Not applicable | Completed | Centre d'Investigation Clinique et Technologique 805 | 20 | 2016-09-01 | 2017-04-20 |
| Simplus and Eson Non-Invasive Ventilation (NIV) Evaluation - Germany Simplus/Eson - Obesity Hypoventilation Syndrome, Obstructive Sleep Apnea | Not applicable | Terminated | Fisher and Paykel Healthcare | 4 | 2016-04-01 | 2018-08-02 |
| Long-Term Effect of LIAM on Respiratory Performance in NIV Patients Suffering From Neuromuscular Disease non invasive mechanical ventilation - Neuromuscular Disease | Not applicable | Unknown | Centre d'Investigation Clinique et Technologique 805 | 30 | 2015-10-29 | 2019-11-18 |
| Prognostic Value of Residual Hypoventilation in Mechanically Ventilated Neuromuscular Patients Capno-oxymetry monitoring - Home Mechanical Ventilation, Neuromuscular Disease | Completed | Centre d'Investigation Clinique et Technologique 805 | 55 | 2015-09-01 | 2016-02-26 | |
| Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases sample collection - Spinal Muscular Atrophy, Charcot-Marie-Tooth Disease | Completed | Nemours Children's Clinic | 230 | 2015-06-01 | 2024-12-19 | |
| Juno Perth Clinical Trial Juno - Respiratory Insufficiency, Obesity Hypoventilation Syndrome | Not applicable | Terminated | ResMed | 25 | 2015-05-29 | 2021-06-08 |
Showing 20 of 50. Sign in to see all of them.
Neuromuscular Diseases (50) · Pulmonary Disease, Chronic Obstructive (8) · Obesity Hypoventilation Syndrome (7) · Muscular Diseases (6) · Amyotrophic Lateral Sclerosis (5) · Respiratory Insufficiency (5) · Muscular Atrophy, Spinal (4) · Cerebral Palsy (3) · Hypoventilation (3) · Motor Neuron Disease (3) · Disease Progression (2) · Hypercapnia (2) · Hypoxia (2) · Neurodegenerative Diseases (2) · Peripheral Nervous System Diseases (2)
Nervous System Diseases (49) · Pathological Conditions, Signs and Symptoms (19) · Nutritional and Metabolic Diseases (14) · Respiratory Tract Diseases (13) · Pathologic Processes (12) · Neurodegenerative Diseases (11) · Respiration Disorders (11) · Signs and Symptoms (11) · Central Nervous System Diseases (10) · Musculoskeletal Diseases (10) · Spinal Cord Diseases (10) · Disease Attributes (9) · Lung Diseases (9) · Apnea (8) · Chronic Disease (8)
Noninvasive Ventilation (3) · Acetylcysteine (1) · Blood Gas Monitoring, Transcutaneous (1) · Brain-Computer Interfaces (1) · Continuous Positive Airway Pressure (1) · Diagnostic Self Evaluation (1) · Electromyography (1) · Equine-Assisted Therapy (1) · Exercise (1) · L 644711 (1) · Musculoskeletal Manipulations (1) · NTLA-2001 (1) · Nerve Conduction Studies (1) · Neurofeedback (1) · Physical Therapists (1)
Centre d'Investigation Clinique et Technologique 805 (9) · National Institute of Neurological Disorders and Stroke (NINDS) (5) · ResMed (5) · National Institute of Nursing Research (NINR) (3) · Guy's and St Thomas' NHS Foundation Trust (2) · Bern University of Applied Sciences (1) · Columbia University (1) · Fisher and Paykel Healthcare (1) · Hanyang University Seoul Hospital (1) · Hasselt University (1) · Hospital Sao Joao (1) · IRCCS Centro Neurolesi Bonino Pulejo (1) · Institut de Myologie, France (1) · Intellia Therapeutics (1) · Istanbul University - Cerrahpasa (1)
United States (16) · France (11) · United Kingdom (9) · Turkey (Türkiye) (4) · Argentina (1) · Australia (1) · Brazil (1) · Canada (1) · Germany (1) · Greece (1) · Italy (1) · Mexico (1) · Netherlands (1) · Portugal (1) · Singapore (1)
Anita Simonds, MD, FRCP (3) · Katherine G Meilleur, C.R.N.P. (2) · A Davidson, MA, MD (1) · Adam Ogna, PhD (1) · Anita Simonds (1) · Avraam Ploumis (1) · Barbara K Smith, PhD, PT (1) · Chris Landon, MD (1) · Darryl C De Vivo, MD (1) · David Orlikowski, MD, PhD (1) · David Orlikowski, MDPhD (1) · Dr. Jodi Warman Chardon, MD PhD (1) · Frederic Lofaso, Md-PhD (1)
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R21HD054697 (1)