Neuromuscular Disease: Clinical Trials

50 trials for Neuromuscular Disease, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

28 completed, 6 recruiting, 6 terminated, 4 not yet recruiting. 20 Not applicable, 6 Phase 1, 6 Phase 2, 1 Phase 3, 1 Phase 4.

By phase and status

PhaseTrialsStatus
Not applicable20Completed 11, Terminated 3, Not yet recruiting 2, Recruiting 2, Unknown 1, Withdrawn 1
Phase 16Completed 5, Unknown 1
Phase 26Completed 3, Terminated 2, Recruiting 1
Phase 31Recruiting 1
Phase 41Unknown 1

Follow Neuromuscular Disease: new trials by email Literature Review of Neuromuscular Disease trials Research Report on Neuromuscular Disease

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Hyperthermia in Patients With Chronic Primary Pain - Effects on Thermoregulation, Somatosensory System and Movement Evoked Pain
serial whole body hyperthermia - Hyperthermia, Chronic Primary Pain
Not applicableNot yet recruitingBern University of Applied Sciences602026-12-012026-09-30
A Clinical Trial of Early Ventilation in Amyotrophic Lateral Sclerosis (EVENT ALS)
Non-invasive ventilation - Amyotrophic Lateral Sclerosis (ALS), Chronic Respiratory Failure
Phase 2RecruitingUniversity of Pennsylvania482026-06-112026-06-26
Connect-One: Early Feasibility Study of Connexus® Brain-Computer Interface (BCI)
Connexus Brain-Computer Interface - Amyotrophic Lateral Sclerosis, Neuromuscular Disease
Not applicableRecruitingParadromics22026-03-312026-04-14
New Technological Pathway for Gait Rehabilitation
Innovative technology pathway for gait neurorehabilitation, Conventional gait rehabilitation strategy - Neurological Diseases or Conditions, Cardiovascular Diseases
Not applicableNot yet recruitingIRCCS Centro Neurolesi Bonino Pulejo602025-03-012025-03-05
Validation and Scaling of Screening Program for Undiagnosed Myasthenia Gravis-Social Media Campaign Paired With a Self-moderated Assessment
Social media recruitment, Self-Assessment, Follow-up - Myasthenia Gravis, Neuromuscular Disease
RecruitingZS Associates10002025-02-262025-03-10
The Prevalence of RYR1-related Disease
Neuromuscular Disease, Malignant Hyperthermia
Not yet recruitingKing's College London20002025-02-012025-01-24
The Effects of a Dynamic Arm Support in Daily Life
Dynamic arm support - Neuromuscular Disease, Neuromuscular Disability
RecruitingHasselt University502024-12-022025-08-13
A Phase 3 Study of NTLA-2001 in ATTRv-PN
nexiguran ziclumeran, Normal Saline as Placebo - Neuromuscular Disease, Neuromuscular Diseases (NMD)
Phase 3RecruitingIntellia Therapeutics602024-11-222026-04-16
Overview: Use of Respiratory Support At Home in Children
Sleep Apnea Syndromes in Children, Obesity in Children
Not yet recruitingUniversity Hospital, Grenoble302024-11-012024-11-18
Ultrasonographic Muscle Assessment and Functional Scales in Spinal Muscular Atrophy
Ultrasonographic Assessment - Spinal Muscular Atrophy (SMA), Neuromuscular Disease
UnknownIstanbul University - Cerrahpasa342024-05-012024-09-24
Ultrasound Detection of Early Facial Muscle Changes in FSHD: Thickness and Echo Intensity Findings
Facioscapulohumeral Muscular Dystrophy, Facioscapulohumeral Muscular Dystrophy 1
CompletedKoç University392023-09-012026-01-09
Manual Therapy and Inspiratory Muscle Training in Neuromuscular Disease
inspiratory muscle training, Manual therapy, Conventional physiotherapy programme - Neuromuscular Disease, Inspiratory Muscle Training
Not applicableCompletedIstinye University282021-08-152026-04-13
B3 for NMD: Bench to Bedside and Back
B3 for NMD: Bench to Bedside and Back - Neuromuscular Disease
Enrolling by invitationOttawa Hospital Research Institute5002019-05-062025-12-30
Feasibility of Virtual Reality in Children With Neuromuscular Disease, Effectiveness of Virtual Reality and Biofeedback
Virtual Reality Training, Biofeedback Training, Conventional rehabilitation - Neuromuscular Disease, Duchenne Muscular Dystrophy
Not applicableCompletedMerve Kurt242019-02-012026-04-23
Comparison of a Hyperinflation Mode and Air Stacking on Neuromuscular Patients Under Volumetric Ventilation
increase of cough peak flow ("Astral ventilator") - Neuromuscular Disease
Not applicableCompletedCentre d'Investigation Clinique et Technologique 805202016-09-012017-04-20
Simplus and Eson Non-Invasive Ventilation (NIV) Evaluation - Germany
Simplus/Eson - Obesity Hypoventilation Syndrome, Obstructive Sleep Apnea
Not applicableTerminatedFisher and Paykel Healthcare42016-04-012018-08-02
Long-Term Effect of LIAM on Respiratory Performance in NIV Patients Suffering From Neuromuscular Disease
non invasive mechanical ventilation - Neuromuscular Disease
Not applicableUnknownCentre d'Investigation Clinique et Technologique 805302015-10-292019-11-18
Prognostic Value of Residual Hypoventilation in Mechanically Ventilated Neuromuscular Patients
Capno-oxymetry monitoring - Home Mechanical Ventilation, Neuromuscular Disease
CompletedCentre d'Investigation Clinique et Technologique 805552015-09-012016-02-26
Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases
sample collection - Spinal Muscular Atrophy, Charcot-Marie-Tooth Disease
CompletedNemours Children's Clinic2302015-06-012024-12-19
Juno Perth Clinical Trial
Juno - Respiratory Insufficiency, Obesity Hypoventilation Syndrome
Not applicableTerminatedResMed252015-05-292021-06-08

Showing 20 of 50. Sign in to see all of them.

Narrower conditions

Neuromuscular Diseases (50)  ·  Pulmonary Disease, Chronic Obstructive (8)  ·  Obesity Hypoventilation Syndrome (7)  ·  Muscular Diseases (6)  ·  Amyotrophic Lateral Sclerosis (5)  ·  Respiratory Insufficiency (5)  ·  Muscular Atrophy, Spinal (4)  ·  Cerebral Palsy (3)  ·  Hypoventilation (3)  ·  Motor Neuron Disease (3)  ·  Disease Progression (2)  ·  Hypercapnia (2)  ·  Hypoxia (2)  ·  Neurodegenerative Diseases (2)  ·  Peripheral Nervous System Diseases (2)

Broader conditions

Nervous System Diseases (49)  ·  Pathological Conditions, Signs and Symptoms (19)  ·  Nutritional and Metabolic Diseases (14)  ·  Respiratory Tract Diseases (13)  ·  Pathologic Processes (12)  ·  Neurodegenerative Diseases (11)  ·  Respiration Disorders (11)  ·  Signs and Symptoms (11)  ·  Central Nervous System Diseases (10)  ·  Musculoskeletal Diseases (10)  ·  Spinal Cord Diseases (10)  ·  Disease Attributes (9)  ·  Lung Diseases (9)  ·  Apnea (8)  ·  Chronic Disease (8)

Interventions

Noninvasive Ventilation (3)  ·  Acetylcysteine (1)  ·  Blood Gas Monitoring, Transcutaneous (1)  ·  Brain-Computer Interfaces (1)  ·  Continuous Positive Airway Pressure (1)  ·  Diagnostic Self Evaluation (1)  ·  Electromyography (1)  ·  Equine-Assisted Therapy (1)  ·  Exercise (1)  ·  L 644711 (1)  ·  Musculoskeletal Manipulations (1)  ·  NTLA-2001 (1)  ·  Nerve Conduction Studies (1)  ·  Neurofeedback (1)  ·  Physical Therapists (1)

Sponsors

Centre d'Investigation Clinique et Technologique 805 (9)  ·  National Institute of Neurological Disorders and Stroke (NINDS) (5)  ·  ResMed (5)  ·  National Institute of Nursing Research (NINR) (3)  ·  Guy's and St Thomas' NHS Foundation Trust (2)  ·  Bern University of Applied Sciences (1)  ·  Columbia University (1)  ·  Fisher and Paykel Healthcare (1)  ·  Hanyang University Seoul Hospital (1)  ·  Hasselt University (1)  ·  Hospital Sao Joao (1)  ·  IRCCS Centro Neurolesi Bonino Pulejo (1)  ·  Institut de Myologie, France (1)  ·  Intellia Therapeutics (1)  ·  Istanbul University - Cerrahpasa (1)

Countries

United States (16)  ·  France (11)  ·  United Kingdom (9)  ·  Turkey (Türkiye) (4)  ·  Argentina (1)  ·  Australia (1)  ·  Brazil (1)  ·  Canada (1)  ·  Germany (1)  ·  Greece (1)  ·  Italy (1)  ·  Mexico (1)  ·  Netherlands (1)  ·  Portugal (1)  ·  Singapore (1)

Top investigators

Anita Simonds, MD, FRCP (3)  ·  Katherine G Meilleur, C.R.N.P. (2)  ·  A Davidson, MA, MD (1)  ·  Adam Ogna, PhD (1)  ·  Anita Simonds (1)  ·  Avraam Ploumis (1)  ·  Barbara K Smith, PhD, PT (1)  ·  Chris Landon, MD (1)  ·  Darryl C De Vivo, MD (1)  ·  David Orlikowski, MD, PhD (1)  ·  David Orlikowski, MDPhD (1)  ·  Dr. Jodi Warman Chardon, MD PhD (1)  ·  Frederic Lofaso, Md-PhD (1)

Results publications

PMID 18467648, PMID 18506712, PMID 19109447, PMID 19251798, PMID 20697104, PMID 23271905, PMID 24396811, PMID 26247043, PMID 26432577, PMID 26515624, PMID 27271157, PMID 27492508, PMID 27679799, PMID 27769560, PMID 28284873, PMID 29970108, PMID 30045959, PMID 30048507, PMID 30430964, PMID 31351076, PMID 31478199, PMID 31941795, PMID 32066871, PMID 32366486, PMID 32493524, PMID 3277050, PMID 33199817, PMID 33415588, PMID 33456041, PMID 33887060, PMID 34980538, PMID 35698232, PMID 35741345, PMID 37037685, PMID 37067602, PMID 40993798

NIH funding

R21HD054697 (1)