2 recruiting, 1 completed. 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Recruiting 1 |
Follow Inflammatory Conditions: new trials by email Literature Review of Inflammatory Conditions trials Research Report on Inflammatory Conditions
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC data collection - Primary Immunodeficiency (PID), Congenital Bone Marrow Failure Syndromes | Recruiting | Paul Szabolcs | 50 | 2020-08-20 | 2026-01-13 | |
| Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT Hydroxyurea, Alemtuzumab, Fludarabine - Primary Immunodeficiency (PID), Congenital Bone Marrow Failure Syndromes | Phase 2 | Recruiting | Paul Szabolcs | 100 | 2014-02-04 | 2025-12-15 |
| Pharmacokinetics of Understudied Drugs Administered to Children Per Standard of Care The POPS study is collecting PK data on children prescribed the following drugs of interest per standard of care: - Adenovirus, Anesthesia | Completed | Daniel Benjamin | 3520 | 2011-11-01 | 2023-09-06 |
Adrenoleukodystrophy (2) · Anemia, Diamond-Blackfan (2) · Anemia, Sickle Cell (2) · Autoimmune Lymphoproliferative Syndrome (2) · Chediak-Higashi Syndrome (2) · Congenital Bone Marrow Failure Syndromes (2) · Congenital amegakaryocytic thrombocytopenia (2) · Crohn Disease (2) · Gaucher Disease (2) · Granulomatous Disease, Chronic (2) · Immune Dysregulation, Polyendocrinopathy, Enteropathy, X-Linked Syndrome (2) · Inflammatory Bowel Diseases (2) · Leukocyte adhesion deficiency type 1 (2) · Leukodystrophy, Globoid Cell (2) · Leukodystrophy, Metachromatic (2)
Adrenal Gland Diseases (3) · Blood Coagulation Disorders (3) · Blood Coagulation Disorders, Inherited (3) · Brain Diseases (3) · Central Nervous System Diseases (3) · Chronic Disease (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Cytopenia (3) · Disease Attributes (3) · Endocrine System Diseases (3) · Eye Diseases (3) · Genetic Diseases, Inborn (3) · Hematologic Diseases (3) · Hemic and Lymphatic Diseases (3) · Hemorrhagic Disorders (3)
Alemtuzumab (1) · Alfentanil (1) · Amikacin (1) · Aminocaproic Acid (1) · Bosentan (1) · Cefepime (1) · Cidofovir (1) · Ciprofloxacin (1) · Clozapine (1) · Data Collection (1) · Fosfomycin (1) · Haloperidol (1) · Hydroxyurea (1) · Labetalol (1) · Lurasidone Hydrochloride (1)
Paul Szabolcs (2) · Daniel Benjamin (1)
United States (3) · Canada (1) · Israel (1) · Singapore (1) · United Kingdom (1)
Paul Szabolcs, MD (2) · Chi Hornik, PharmD (1)
PMID 24614374, PMID 24949994, PMID 26039810, PMID 26926644, PMID 27522443, PMID 28137820, PMID 28290120, PMID 28779462, PMID 29084742, PMID 29271816, PMID 29435949, PMID 29677389, PMID 30790601, PMID 31317556, PMID 31548185, PMID 31814149, PMID 32324313, PMID 32497307, PMID 32634238, PMID 32750127, PMID 33029806, PMID 33903114, PMID 34302290, PMID 35370711, PMID 35491971, PMID 41247430