1141 completed, 303 unknown, 261 recruiting, 156 terminated. 444 Phase 2, 417 Phase 3, 300 Phase 1, 273 Not applicable, 137 Phase 4.
Follow Blood Coagulation Disorders: new trials by email Literature Review of Blood Coagulation Disorders trials Research Report on Blood Coagulation Disorders
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Lentiviral FIX Gene Therapy YUVA-GT-F901 - Hemophilia B | Phase 1 | Not yet recruiting | Shenzhen Geno-Immune Medical Institute | 10 | 2027-06-01 | 2026-08-26 |
| Lentiviral FVIII Gene Therapy YUVA-GT-F801 - Hemophilia A | Phase 1 | Not yet recruiting | Shenzhen Geno-Immune Medical Institute | 10 | 2027-06-01 | 2026-09-01 |
| Post Approval Phase 4 Study to Learn More About How Safe Octocog Alfa is, and How Well it Works in Patients With Severe Hemophilia A in India Octocog alfa - Severe Hemophilia A | Not yet recruiting | Bayer | 30 | 2027-04-05 | 2026-10-21 | |
| Multicomponent Pain Self-Management in Adults With Haemophilic Arthropathy Multicomponent pain self-management programme - Hemophilic Arthropathy, Chronic Pain | Not applicable | Not yet recruiting | Investigación en Hemofilia y Fisioterapia | 70 | 2027-03-01 | 2026-10-06 |
| A Study of Ianalumab in Addition to Eltrombopag in Pediatric Patients With Primary ITP Who Failed Corticosteroids. Ianalumab, Eltrombopag - Primary Immune Thrombocytopenia (ITP) | Phase 2 | Not yet recruiting | Novartis Pharmaceuticals | 36 | 2027-02-08 | 2026-06-25 |
| Ultrasound Assessment of Joint Health in Patients With Mild Hemophilia (Factor Levels 5-40%) Joint Ultrasound (HEAD-US), Blood Sample for Coagulation Factor Measurement - Mild Hemophilia | Not applicable | Not yet recruiting | Assistance Publique - Hôpitaux de Paris | 150 | 2027-02-01 | 2026-08-17 |
| Phase 1 Dose Escalation Study of RXIM002 in Autoimmune Cytopenias RXIM002 - Immune Thrombocytopenia (ITP) | Phase 1 | Not yet recruiting | RiboX Therapeutics Ltd. | 27 | 2027-02-01 | 2026-09-23 |
| WELL-MPN: A Digital Lifestyle App for Patients With MPNs WELL-MPN Digital App - Myeloproliferative Neoplasms (MPNs) | Not applicable | Not yet recruiting | Brigham and Women's Hospital | 75 | 2027-01-01 | 2026-09-29 |
| Efanesoctocog Prophylaxis Or The Optimization Of Treatment: Real-World Experience Of Taylorizing Clotting Therapy In Hemophilia A Study questionnaires, Clinical/pharmacological data collection - Hemophilia A Patient | Not yet recruiting | Nantes University Hospital | 553 | 2027-01-01 | 2026-09-25 | |
| Study of Efficacy and Safety of FRSW107 in Pediatric Patients With Severe Hemophilia A FRSW107 - Severe Hemophilia A | Phase 3 | Not yet recruiting | Hangzhou Gensciences Biopharmaceutical Co., Ltd. | 76 | 2026-12-25 | 2024-06-20 |
| CD19-B Cell Depletion in PAIS-ME/CFS Patients Inebilizumab, Placebo - Post-acute Infectious Syndrome (PAIS), Post-COVID 19 Condition (PCC or Long COVID) | Phase 2 | Not yet recruiting | Charite University, Berlin, Germany | 38 | 2026-12-01 | 2026-07-24 |
| A Phase 1b/2a Study of Velinotamig in Adults With Relapsed/Refractory ITP and wAIHA Velinotamig specified dose on specified days. - Immune Thrombocytopenia (ITP), Warm Autoimmune Hemolytic Anemia (WAIHA) | Phase 1 / Phase 2 | Not yet recruiting | Cullinan Therapeutics Inc. | 72 | 2026-12-01 | 2026-07-31 |
| Clinical Trial of NXT007 for the Prophylactic Treatment of Hemophilia A in Infants and Children NXT007 - Hemophilia A | Phase 3 | Not yet recruiting | Hoffmann-La Roche | 50 | 2026-11-30 | 2026-10-19 |
| Liver Biopsy Following Gene Therapy For Hemophilia Liver Biopsy - Hemophilia A, Hemophilia B | Not yet recruiting | St. Jude Children's Research Hospital | 8 | 2026-11-01 | 2026-10-22 | |
| TGD001 Treatment in Thrombotic Microangiopathies TGD001 - Thrombotic Microangiopathies, ITP Immune-Mediated Thrombocytopenia | Phase 1 / Phase 2 | Not yet recruiting | TargED Biopharmaceuticals B.V. | 70 | 2026-10-31 | 2026-09-29 |
| A Research Study Investigating Denecimig (Mim8) in Adults With Acquired Haemophilia A Denecimig - Haemophilia A | Phase 3 | Not yet recruiting | Novo Nordisk A/S | 84 | 2026-10-09 | 2026-09-21 |
| "IL-1β Blockade to Prevent Immunothrombosis in Recipients of a Pancreatic Organ" Anakinra 100Mg/0.67Ml Inj Syringe - Pancreatic Transplant | Phase 1 / Phase 2 | Recruiting | Nantes University Hospital | 15 | 2026-10-07 | 2026-10-13 |
| A Study to Describe Patient REal-world FitusiRan ExpeRience Hemophilia A or B | Not yet recruiting | Sanofi | 100 | 2026-10-07 | 2026-10-26 | |
| A Study to Learn About the Study Medicine (Called Marstacimab) in People With Hemophilia A or B Marstacimab - Hemophilia | Not yet recruiting | Pfizer | 100 | 2026-10-05 | 2026-10-05 | |
| Post-acute Infectious Syndrome - Aripiprazole Symptom Evaluation (PAIS-AriSE) Aripiprazole (low-dose, 1mg), Placebo - Post-acute Infectious Syndrome (PAIS), Post-COVID-19 Condition (PCC or Long COVID) | Phase 2 | Not yet recruiting | Christiana Franke | 138 | 2026-10-01 | 2026-07-20 |
Showing 20 of 2139. Sign in to see all of them.
Hemophilia A (788) · Purpura, Thrombocytopenic, Idiopathic (481) · Hemophilia B (260) · Thrombocythemia, Essential (229) · Polycythemia Vera (176) · Primary Myelofibrosis (174) · Myeloproliferative Disorders (145) · von Willebrand Diseases (95) · Leukemia, Myeloid, Acute (89) · Leukemia, Myelomonocytic, Chronic (85) · Myelodysplastic Syndromes (82) · Precursor Cell Lymphoblastic Leukemia-Lymphoma (82) · Leukemia, Lymphocytic, Chronic, B-Cell (79) · Multiple Myeloma (77)
Hemic and Lymphatic Diseases (2139) · Hematologic Diseases (2069) · Hemorrhagic Disorders (1871) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1205) · Genetic Diseases, Inborn (1125) · Blood Coagulation Disorders, Inherited (1105) · Coagulation Protein Disorders (1018) · Pathological Conditions, Signs and Symptoms (953) · Pathologic Processes (913) · Blood Platelet Disorders (894) · Signs and Symptoms (691) · Immune System Diseases (676) · Hemorrhage (653) · Skin Manifestations (627)
Factor VIII (137) · eltrombopag (64) · F8 protein, human (57) · Rituximab (52) · Dexamethasone (49) · romiplostim (36) · Factor IX (34) · emicizumab (34) · Cyclophosphamide (33) · Blood Specimen Collection (31) · fludarabine phosphate (30) · Peripheral Blood Stem Cell Transplantation (26) · BAY 14-2222 (23) · Busulfan (21) · Cyclosporine (21)
Novo Nordisk A/S (84) · Baxalta now part of Shire (63) · Bayer (62) · Peking University People's Hospital (50) · Institute of Hematology & Blood Diseases Hospital, China (49) · Pfizer (46) · CSL Behring (44) · Shandong University (39) · Octapharma (29) · Takeda (27) · Assistance Publique - Hôpitaux de Paris (25) · Assiut University (23) · Novartis Pharmaceuticals (23) · Hoffmann-La Roche (21) · Wyeth is now a wholly owned subsidiary of Pfizer (21)
United States (772) · France (348) · China (318) · United Kingdom (313) · Italy (297) · Spain (287) · Germany (284) · Canada (193) · Turkey (Türkiye) (153) · Japan (147) · Poland (147) · Australia (132) · Netherlands (132) · Austria (128) · Belgium (104)
Lei Zhang, MD (26) · Xiao-Hui Zhang, MD (14)
PMID 40750723, PMID 19005182, PMID 26196195, PMID 36853224, PMID 40386832, PMID 42698050, PMID 19216617, PMID 19671919, PMID 24802773, PMID 35939785, PMID 36408876, PMID 19846889, PMID 25495795, PMID 26231455, PMID 26688484, PMID 26931631, PMID 31697801, PMID 33719084, PMID 33995988, PMID 34922648, PMID 35075289, PMID 36848635, PMID 39091324, PMID 12944568, PMID 17077333, PMID 17687129, PMID 17880439, PMID 18242413, PMID 20546023, PMID 21533818, PMID 22117897, PMID 22149959, PMID 22212248, PMID 22409309, PMID 22494019, PMID 22760174, PMID 22765835, PMID 23293082, PMID 23470153, PMID 23492914, PMID 24254965, PMID 24335249, PMID 24802775, PMID 25273984, PMID 25856035, PMID 26157075, PMID 26480931, PMID 26679394, PMID 27002680, PMID 27734464
2023 (31), 2016 (21), 2009 (20), 2018 (19), 2017 (16), 2015 (14), 2019 (14), 2014 (13), 2008 (12), 2025 (8), P01CA108671 (6), P30CA015083 (6), 2004 (4), 2005 (4), P30CA006973 (4)