6 completed, 3 recruiting, 3 terminated, 2 active not recruiting. 5 Phase 2, 4 Not applicable, 2 Phase 1, 1 Early Phase 1, 1 Phase 3.
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Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Haloperidol For Outpatient Symptom Management in Patients Diagnosed With Cannabinoid Hyperemesis Syndrome in the Emergrency Department Haloperidol - Cannabinoid Hyperemesis Syndrome | Early Phase 1 | Not yet recruiting | University of Illinois at Chicago | 100 | 2026-11-01 | 2026-09-01 |
| Baby Detect : Genomic Newborn Screening Congenital Adrenal Hyperplasia, Familial Hyperinsulinemic Hypoglycemia 1 | Completed | Centre Hospitalier Universitaire de Liege | 6824 | 2022-09-01 | 2025-08-12 | |
| Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC data collection - Primary Immunodeficiency (PID), Congenital Bone Marrow Failure Syndromes | Recruiting | Paul Szabolcs | 50 | 2020-08-20 | 2026-01-13 | |
| Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT Hydroxyurea, Alemtuzumab, Fludarabine - Primary Immunodeficiency (PID), Congenital Bone Marrow Failure Syndromes | Phase 2 | Recruiting | Paul Szabolcs | 100 | 2014-02-04 | 2025-12-15 |
| Bone Marrow Transplant With Abatacept for Non-Malignant Diseases Abatacept - Hurler Syndrome, Fanconi Anemia | Phase 1 | Completed | Emory University | 10 | 2014-01-01 | 2019-12-26 |
| Immune Disorder HSCT Protocol Transplant preparative regimen of alemtuzumab, fludarabine, thiotepa, and melphalan - Immune Deficiency Disorders, Severe Combined Immunodeficiency | Phase 2 | Active not recruiting | Washington University School of Medicine | 20 | 2013-04-29 | 2026-02-19 |
| Allogeneic Hematopoietic Stem Cell Transplant for Patients With Primary Immune Deficiencies Alemtuzumab 0.3 mg, Cyclophosphamide, Busulfan - SCID, Omenn's Syndrome | Not applicable | Active not recruiting | Masonic Cancer Center, University of Minnesota | 57 | 2012-09-04 | 2026-06-17 |
| Alefacept and Allogeneic Hematopoietic Stem Cell Transplantation Alefacept - Thalassemia, Sickle Cell Disease | Not applicable | Terminated | Emory University | 3 | 2010-09-01 | 2017-07-27 |
| Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells Hematopoietic stem cell transplantation - Sickle Cell Disease, Thalassemia | Phase 1 / Phase 2 | Completed | Children's Hospital Los Angeles | 25 | 2008-08-01 | 2016-06-23 |
| Study of Megakaryocytes From Patients With Abnormal Platelet Vesicles Blood Coagulation Disorders | Completed | National Human Genome Research Institute (NHGRI) | 3 | 2004-06-29 | 2017-07-02 | |
| Study of Chediak-Higashi Syndrome Chediak-Higashi Syndrome | Recruiting | National Human Genome Research Institute (NHGRI) | 60 | 2002-09-10 | 2026-08-28 | |
| Stem Cell Transplant for Immunologic or Histiocytic Disorders Stem Cell Transplant, Fludarabine, Melphalan - Hemophagocytic Lymphohistiocytosis, X-Linked Lymphoproliferative Disorders | Phase 2 | Completed | Masonic Cancer Center, University of Minnesota | 19 | 2002-08-01 | 2017-12-28 |
| T-Cell Depletion and Stem Cell Transplant for Immune Deficiencies and Histiocytic Disorders Stem Cell Transplant, Myeloablative conditioning regimen - Hemophagocytic Lymphohistiocytosis, X-Linked Lymphoproliferative Disorders | Phase 2 / Phase 3 | Terminated | Masonic Cancer Center, University of Minnesota | 22 | 2000-09-01 | 2018-01-23 |
| Learning and Behavior Problems in Children With Chronic Granulomatous Disease and Related Disorders Chediak Higashi Syndrome, Chronic Granulomatous Disease | Completed | National Institute of Allergy and Infectious Diseases (NIAID) | 150 | 2000-06-01 | 2008-03-04 | |
| Pilot Study of Unrelated Donor Hematopoietic Stem Cell Transplantation in Patients With Life Threatening Hemophagocytic Disorders anti-thymocyte globulin, busulfan, cyclophosphamide - Chediak-Higashi Syndrome, Graft Versus Host Disease | Not applicable | Unknown | Fairview University Medical Center | 40 | 2000-03-01 | 2005-06-24 |
| Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies anti-thymocyte globulin, busulfan, cyclophosphamide - Immunologic Deficiency Syndromes, Chediak-Higashi Syndrome | Not applicable | Terminated | Fairview University Medical Center | 2000-03-01 | 2009-10-15 |
Granulomatous Disease, Chronic (10) · Lymphohistiocytosis, Hemophagocytic (10) · Wiskott-Aldrich Syndrome (10) · Lymphoproliferative Disorders (7) · Anemia, Sickle Cell (6) · Severe Combined Immunodeficiency (6) · Anemia, Diamond-Blackfan (5) · Mucopolysaccharidosis I (5) · Histiocytosis, Langerhans-Cell (4) · Hyper-IgM Immunodeficiency Syndrome (4) · Immune System Diseases (4) · Immunologic Deficiency Syndromes (4) · Leukocyte adhesion deficiency type 1 (4) · Neutropenia, Severe Congenital, Autosomal Recessive 3 (4)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (16) · Eye Diseases (16) · Eye Diseases, Hereditary (16) · Hemic and Lymphatic Diseases (16) · Phagocyte Bactericidal Dysfunction (16) · Albinism (15) · Leukocyte Disorders (15) · Genetic Diseases, Inborn (13) · Hematologic Diseases (13) · Immune System Diseases (12) · Immunologic Deficiency Syndromes (12) · Pathological Conditions, Signs and Symptoms (12) · Primary Immunodeficiency Diseases (12) · Disease Attributes (11) · Genetic Diseases, X-Linked (11)
Busulfan (4) · Cyclophosphamide (4) · Melphalan (4) · Alemtuzumab (3) · Antilymphocyte Serum (3) · Cyclosporine (3) · Stem Cell Transplantation (3) · fludarabine (3) · fludarabine phosphate (3) · Etoposide (2) · Methotrexate (2) · Thiotepa (2) · Abatacept (1) · Alefacept (1) · Data Collection (1)
Masonic Cancer Center, University of Minnesota (3) · Emory University (2) · Fairview University Medical Center (2) · National Human Genome Research Institute (NHGRI) (2) · Paul Szabolcs (2) · Centre Hospitalier Universitaire de Liege (1) · Children's Hospital Los Angeles (1) · National Institute of Allergy and Infectious Diseases (NIAID) (1) · University of Illinois at Chicago (1) · Washington University School of Medicine (1)
United States (15) · Belgium (1)
Angela Smith, MD (2) · K. Scott Baker (2) · Paul Szabolcs, MD (2) · Hisham Abdel-Azim, MD (1) · John Horan, MD (1) · John T Horan, MD (1) · Laurent Servais (1) · Meera Srikanthan, MD (1) · Wendy J Introne, M.D. (1) · Wesley Eilbert, MD (1)