Cytopenia: Clinical Trials

1,567 trials for Cytopenia, newest first

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747 completed, 274 unknown, 208 recruiting, 136 terminated. 499 Phase 2, 285 Phase 3, 193 Phase 1, 165 Not applicable, 108 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 2499Completed 218, Unknown 82, Recruiting 69, Terminated 64, Not yet recruiting 25, Withdrawn 23, Active not recruiting 16, Enrolling by invitation 1, Suspended 1
Phase 3285Completed 156, Unknown 41, Terminated 31, Recruiting 23, Withdrawn 13, Active not recruiting 12, Not yet recruiting 9
Phase 1193Completed 107, Terminated 25, Recruiting 24, Unknown 13, Not yet recruiting 9, Withdrawn 8, Active not recruiting 5, Enrolling by invitation 2
Not applicable165Completed 73, Recruiting 27, Unknown 22, Not yet recruiting 19, Terminated 10, Withdrawn 8, Active not recruiting 6
Phase 4108Completed 46, Unknown 33, Recruiting 10, Terminated 9, Not yet recruiting 5, Withdrawn 5
Early Phase 122Recruiting 7, Completed 6, Unknown 4, Not yet recruiting 3, Withdrawn 2

Follow Cytopenia: new trials by email Literature Review of Cytopenia trials Research Report on Cytopenia

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of NM8074 in Patients With aHUS With Evidence of Ongoing Thrombotic Microangiopathy
NM8074 - aHUS - Atypical Hemolytic Uremic Syndrome
Phase 2Not yet recruitingNovelMed Therapeutics122027-11-012026-04-13
Restrictive Versus Standard Antibiotic Treatment During CAR-T Therapy
ceftazidime, ciprofloxacin, Standard-of-Care Antibiotic Strategy - Large B-Cell Lymphoma (LBCL), Multiple Myeloma (MM)
Phase 2Not yet recruitingZealand University Hospital1502027-03-012026-09-25
G-CSF In Neonatal Sepsis With Neutropenia
Granulocyte-colony stimulating factor (G-CSF), Standard Sepsis Management - Neonatal Sepsis, Neutropenia
Not applicableNot yet recruitingUniversity of Health Sciences Lahore522027-02-152026-10-22
A Study of Ianalumab in Addition to Eltrombopag in Pediatric Patients With Primary ITP Who Failed Corticosteroids.
Ianalumab, Eltrombopag - Primary Immune Thrombocytopenia (ITP)
Phase 2Not yet recruitingNovartis Pharmaceuticals362027-02-082026-06-25
Phase 1 Dose Escalation Study of RXIM002 in Autoimmune Cytopenias
RXIM002 - Immune Thrombocytopenia (ITP)
Phase 1Not yet recruitingRiboX Therapeutics Ltd.272027-02-012026-10-28
Diagnostic Accuracy, Clinical Utility and Implementation of Point-of-Care Absolute Neutrophil Count in Suspected Neutropenic Fever (DUCATIS) - Diagnostic Accuracy (S1)
Hemocue® WBC DIFF system - Suspected Neutropenic Fever, Confirmed Neutropenic Fever
Not applicableNot yet recruitingThe University of Hong Kong3172027-01-012026-10-28
An Open-label Phase I/II Safety and Feasibility Basket Study of UKT-CART19.1
CAR-T cells targeting CD19 - Pemphigus Vulgaris (PV), ANCA Associated Vasculitis (AAV)
Phase 1 / Phase 2Not yet recruitingUniversity Hospital Tuebingen362027-01-012026-11-12
A Clinical Study Evaluating the Safety and Preliminary Effectiveness of Induced Pluripotent Stem Cell-derived Platelets in Patients With Thrombocytopenia Caused by Allogeneic Hematopoietic Stem Cell Transplantation
iPSC-derived platelets - Thrombocytopenia
Early Phase 1Not yet recruitingRuijin Hospital92026-12-302026-10-29
A Study to Compare the Pharmacokinetics, Pharmacodynamics, Immunogenicity, Safety and Tolerability of Filgrastim Biosimilar and Neupogen Reference Product in Healthy Volunteers
Biofilgragen, Neupogen (filgrastim) - Neutropenia (Low White Blood Cell Count)
Phase 1Not yet recruitingBioGeneric Pharma502026-12-152026-10-20
Impact of a Telemonitoring Device on the Occurever at Home in Children at Risk of Chemotherapy-Induced Neutropenia
Remote temperature monitoring device, Home temperature monitoring by a nurse - Oncopediatrics, Febrile Neutropenia
Not applicableNot yet recruitingCentre Hospitalier Universitaire de la Réunion302026-12-012026-10-23
Acupuncture as add-on to G-CSF for Febrile Neutropenia-related Hospitalization in Doxorubicin-treated Patients With Sarcoma
Acupuncture - Febrile Neutropenia, Sarcoma
Not applicableNot yet recruitingShaare Zedek Medical Center602026-12-012026-04-29
A Phase 1b/2a Study of Velinotamig in Adults With Relapsed/Refractory ITP and wAIHA
Velinotamig specified dose on specified days. - Immune Thrombocytopenia (ITP), Warm Autoimmune Hemolytic Anemia (WAIHA)
Phase 1 / Phase 2Not yet recruitingCullinan Therapeutics Inc.722026-12-012026-07-31
Study of LusPACercept in Participants With Myelofibrosis Associated Anemia and Thrombocytopenia
Luspatercept, Pacritinib - Myelofibrosis
Phase 2Not yet recruitingCase Comprehensive Cancer Center502026-12-012026-11-13
Sequential Hetrombopag and Recombinant Human Thrombopoietin for Cancer Therapy-Induced Thrombocytopenia
Hetrombopag and recombinant human thrombopoietin, Recombinant Human Thrombopoietin - Thrombocytopenia
Phase 2Not yet recruitingThe First Affiliated Hospital of Zhengzhou University962026-12-012026-11-12
Optimal Dose of Zanubrutinib to Treat Adult Immune Thrombocytopenia
Zanubrutinib 80mg/d, High dose dexamethasone, Zanubrutinib 160mg/d - Immune Thrombocytopenia
Phase 2Not yet recruitingPeking University People's Hospital902026-12-012026-11-12
Hematological Safety of Dipyrone Versus Paracetamol After Dental Extractions
Dipyrone administration, Paracetamol (drug), blood sampling - Hematologic Test, Agranulocytosis
Phase 4RecruitingMatheus Furtado de Carvalho502026-11-132026-11-06
Time-limited Treatment With Avatrombopag Pre- and Post-CAR T-cell Therapy to Prevent Post-CAR T-cell Cytopenias
Avatrombopag - Thrombocytopenia
Phase 2Not yet recruitingUniversity of Virginia262026-11-012026-10-26
Efficacy and Safety of Romiplostim N01 for Injection in Promoting Platelet Reconstitution After Allogeneic Hematopoietic Stem Cell Transplantation
Romiplostim N01 - Thrombocytopenia, Allogeneic Hematopoietic Stem Cell Transplantation
Phase 2Not yet recruitingThe First Affiliated Hospital of Henan University of Science and Technology872026-11-012026-09-21
Study of Thyroid Dysfunction in Immune Thrombocytopenic Purpura Patients
Laboratory tests TSH, FT3, FT4 ,anti thyroglobulin antibodies, Anti -TPO antibodies - Thyroid Dysfunction, Immune Thrombocytopenic Purpura
Not yet recruitingSohag University502026-10-252026-10-28
TGD001 Treatment in Thrombotic Microangiopathies
TGD001 - Thrombotic Microangiopathies, ITP Immune-Mediated Thrombocytopenia
Phase 1 / Phase 2RecruitingTargED Biopharmaceuticals B.V.702026-10-252026-11-12

Showing 20 of 1567. Sign in to see all of them.

Narrower conditions

Purpura, Thrombocytopenic, Idiopathic (483)  ·  Thrombocytopenia (415)  ·  Neutropenia (293)  ·  Febrile Neutropenia (145)  ·  Myelodysplastic Syndromes (66)  ·  Purpura, Thrombotic Thrombocytopenic (65)  ·  Neoplasms (64)  ·  Breast Neoplasms (62)  ·  Anemia (59)  ·  Hematologic Diseases (58)  ·  Leukemia, Myeloid, Acute (54)  ·  Thrombotic Microangiopathies (49)  ·  Hematologic Neoplasms (48)  ·  Fever (47)

Broader conditions

Hemic and Lymphatic Diseases (1567)  ·  Hematologic Diseases (1509)  ·  Blood Platelet Disorders (1010)  ·  Pathological Conditions, Signs and Symptoms (781)  ·  Pathologic Processes (726)  ·  Immune System Diseases (723)  ·  Signs and Symptoms (621)  ·  Thrombocytopenia (600)  ·  Blood Coagulation Disorders (599)  ·  Thrombotic Microangiopathies (590)  ·  Hemorrhagic Disorders (559)  ·  Skin Manifestations (550)  ·  Hemorrhage (545)  ·  Purpura (531)

Interventions

eltrombopag (106)  ·  romiplostim (54)  ·  Dexamethasone (49)  ·  Rituximab (48)  ·  Filgrastim (43)  ·  avatrombopag (42)  ·  pegfilgrastim (40)  ·  Cyclophosphamide (27)  ·  Thrombopoietin (22)  ·  Blood Specimen Collection (21)  ·  Immunoglobulins, Intravenous (21)  ·  Prednisone (19)  ·  Cyclosporine (16)  ·  eculizumab (15)  ·  Danazol (14)

Sponsors

Peking University People's Hospital (55)  ·  Shandong University (44)  ·  Amgen (43)  ·  Institute of Hematology & Blood Diseases Hospital, China (40)  ·  National Heart, Lung, and Blood Institute (NHLBI) (32)  ·  GlaxoSmithKline (29)  ·  Novartis Pharmaceuticals (27)  ·  Assistance Publique - Hôpitaux de Paris (26)  ·  Alexion Pharmaceuticals, Inc. (21)  ·  Assiut University (21)  ·  Pfizer (17)  ·  M.D. Anderson Cancer Center (16)  ·  Eisai Inc. (13)  ·  National Cancer Institute (NCI) (13)  ·  National Institute of Allergy and Infectious Diseases (NIAID) (13)

Countries

United States (515)  ·  China (326)  ·  France (197)  ·  Italy (135)  ·  Germany (123)  ·  United Kingdom (117)  ·  Spain (110)  ·  Canada (89)  ·  Poland (71)  ·  South Korea (70)  ·  Australia (69)  ·  Netherlands (68)  ·  Belgium (58)  ·  Japan (54)  ·  Russia (53)

Top investigators

Lei Zhang, MD (18)  ·  Xiao-Hui Zhang, MD (14)  ·  Xiaohui Zhang, MD (10)  ·  Ming Hou, Dr (6)  ·  James Bussel, MD (5)  ·  Ming Hou (5)  ·  Ming Hou, Dr. (5)  ·  Cindy Leissinger, MD (4)

Results publications

PMID 33783815, PMID 19005182, PMID 19846889, PMID 29958797, PMID 39903535, PMID 40277027, PMID 19671919, PMID 23738544, PMID 24802773, PMID 29419434, PMID 29674506, PMID 32031570, PMID 32171076, PMID 34219224, PMID 34724566, PMID 24254965, PMID 26231455, PMID 26688484, PMID 29515037, PMID 33995988, PMID 35075289, PMID 12944568, PMID 17077333, PMID 18242413, PMID 19549917, PMID 20546023, PMID 21533818, PMID 22067384, PMID 22117897, PMID 22409309, PMID 22494019, PMID 23053510, PMID 23293082, PMID 23317527, PMID 23470153, PMID 23492914, PMID 24802775, PMID 25566808, PMID 26480931, PMID 27658437, PMID 27734464, PMID 28637287, PMID 29042367, PMID 29536526, PMID 29778606, PMID 30900158, PMID 30992268, PMID 32047671, PMID 33031789, PMID 33275766

NIH funding

2023 (15), 2014 (10), 2018 (10), 2019 (7), 2016 (6), U01HL072268 (6), 2009 (5), 2017 (4), 2025 (4), P30CA016672 (3), 2015 (2), P01HL046925 (2), P30CA015083 (2), P30CA015704 (2), U10CA095861 (2)