Pseudohypoparathyroidism: Clinical Trials

23 trials for Pseudohypoparathyroidism, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

7 completed, 5 recruiting, 3 active not recruiting, 3 unknown. 6 Phase 2, 2 Not applicable, 1 Phase 1, 1 Phase 3, 1 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 26Active not recruiting 2, Completed 2, Enrolling by invitation 2
Not applicable2Active not recruiting 1, Unknown 1
Phase 11Completed 1
Phase 31Unknown 1
Phase 41Recruiting 1

Follow Pseudohypoparathyroidism: new trials by email Literature Review of Pseudohypoparathyroidism trials Research Report on Pseudohypoparathyroidism

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Setmelanotide to Treat Obesity in a Patient With Pseudohypoparathyroidism Type 1a (PHP1a)
Setmelanotide - Pseudohypoparathyroidism Type 1a, Obesity
Phase 2Enrolling by invitationMassachusetts General Hospital12026-07-212026-07-23
Tunisian Clinical Registry on Hypoparathyroidism and Pseudo-hypoparathyroidism
Hypoparathyroidism, Pseudo Hypoparathyroidism
Not yet recruitingDacima Consulting10002025-02-272025-02-21
Institution of an Italian Multicenter Database of Patients Affected by Hypoparathyroidism or Pseudohypoparathyroidism
Hypoparathyroidism, Pseudo Hypoparathyroidism
RecruitingF.I.R.M.O. - Fondazione Italiana Ricerca sulle Malattie dell'Osso - Ente del Terzo Settore6002024-11-042025-01-23
Natural History Study of Parathyroid Disorders
Parathyroid Cancer, Primary Hyperparathyroidism
RecruitingNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)30002021-11-302026-09-17
German Hypoparathyroidism Registry
Hypoparathyroidism, Pseudohypoparathyroidism
RecruitingUniversity Hospital Augsburg1502021-07-062026-10-05
Determination of Circulating Autotaxin in Patients With GNAS or PTH Abnormalities
blood sample - Fibrous Dysplasia, Albright Syndrome
CompletedHospices Civils de Lyon332021-03-102023-03-24
Theophylline Treatment for Pseudohypoparathyroidism - Children 2-12 Years Old
Theophylline, Placebo - Pseudohypoparathyroidism, Albright Hereditary Osteodystrophy
Phase 2Active not recruitingVanderbilt University Medical Center342020-07-132026-04-29
Theophylline for Treatment of Pseudohypoparathyroidism
Theophylline ER - Pseudohypoparathyroidism, Pseudohypoparathyroidism Type 1a
Phase 2Enrolling by invitationJaclyn Tamaroff342020-05-222026-09-02
Effect of Theophylline in Pseudohypoparathyroidism
Theophylline - PHP Ia, PHP IB
Phase 4RecruitingMassachusetts General Hospital1002019-11-112022-07-22
QoL and Cognitive Function in Patients With Hypoparathyroidism
MRI scans, Neuro cognitive tests, Questionnaires on Quality of Life - Hypoparathyroidism, Pseudo Hypoparathyroidism
CompletedUniversity of Aarhus642019-10-012021-12-23
Glucose Homeostasis in Pseudohypoparathyroidism
Pseudohypoparathyroidism and Pseudopseudohypoparathyroidism, Pseudohypoparathyroidism Type Ia
TerminatedVanderbilt University Medical Center142019-06-192026-05-04
Theophylline Treatment for Pseudohypoparathyroidism
Theophylline, Placebos - Pseudohypoparathyroidism, Albright Hereditary Osteodystrophy
Phase 2Active not recruitingVanderbilt University Medical Center292018-09-012026-09-02
IDMet (RaDiCo Cohort) (RaDiCo-IDMet)
Silver Russell Syndrome, Beckwith-Wiedemann Syndrome
RecruitingInstitut National de la Santé Et de la Recherche Médicale, France20002017-03-102026-02-12
Theophylline as a Treatment for Children With Pseudohypoparathyroidism Type 1a (Albright Hereditary Osteodystrophy)
Theophylline - Pseudohypoparathyroidism Type 1a, Albright Hereditary Osteodystrophy
Phase 2CompletedVanderbilt University Medical Center62015-06-012017-06-26
Early-onset Obesity and Cognitive Impairment in Children With Pseudohypoparathyroidism
Pseudohypoparathyroidism, Albright Hereditary Osteodystrophy
CompletedVanderbilt University Medical Center392014-12-012019-11-13
Characterization of Patients With Non-surgical Hypoparathyroidism and Pseudohypoparathyroidism
Idiopathic Hypoparathyroidism, Autosomal Dominant Hypocalcaemia
UnknownUniversity of Aarhus1002014-06-012018-08-07
Clinical Study for Development of Oral Galactose Single Point (OGSP) Solution (G.S.P. Oral Solution®)
G.S.P. Oral Solution 400 mg/ml - Galactose Single Point (GSP), Residual Liver Function
Phase 3UnknownRichever Enterprise Co., Ltd.2002013-09-092018-03-07
Energy Expenditure and Body Composition in Pseudohypoparathyroidism 1a
Pseudohypoparathyroidism Type 1A, Albright Hereditary Osteodystrophy
TerminatedChildren's Hospital of Philadelphia5192011-06-012018-08-22
GSP as an Novel Indicator for Residual Liver Function in Patients With Fatty Liver
Drug: G.S.P. Solution 400 mg/ml I.V. 1.25 ml/kg BW G.S.P. solution after fasting for 6 hours. - Galactose Single Point (GSP), Residual Liver Function
Phase 1 / Phase 2CompletedNational Defense Medical Center, Taiwan2102007-07-052020-09-14
Albright Hereditary Osteodystrophy: Natural History, Growth, and Cognitive/Behavioral Assessments
Neurocognitive and psychosocial testing - Pseudohypoparathyroidism Type 1A, Albright Hereditary Osteodystrophy
Not applicableActive not recruitingConnecticut Children's Medical Center6002003-01-012026-06-02

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Narrower conditions

Hypoparathyroidism (6)  ·  Dwarfism, Pituitary (2)  ·  Hyperparathyroidism (2)  ·  Pseudopseudohypoparathyroidism (2)  ·  Angelman Syndrome (1)  ·  Beckwith-Wiedemann Syndrome (1)  ·  Behavior (1)  ·  Cognitive Dysfunction (1)  ·  Endocrine System Diseases (1)  ·  Fibrous Dysplasia of Bone (1)  ·  Fibrous Dysplasia, Polyostotic (1)  ·  Hypercalciuric Hypocalcemia, Familial (1)  ·  Hyperparathyroidism, Primary (1)  ·  Hypocalcemia (1)

Broader conditions

Bone Diseases (23)  ·  Bone Diseases, Metabolic (23)  ·  Calcium Metabolism Disorders (23)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (23)  ·  Genetic Diseases, Inborn (23)  ·  Metabolic Diseases (23)  ·  Metabolism, Inborn Errors (23)  ·  Metal Metabolism, Inborn Errors (23)  ·  Musculoskeletal Diseases (23)  ·  Nutritional and Metabolic Diseases (23)  ·  Endocrine System Diseases (10)  ·  Parathyroid Diseases (7)  ·  Nutrition Disorders (4)  ·  Bone Diseases, Developmental (3)  ·  Central Nervous System Diseases (3)

Interventions

Theophylline (4)  ·  Blood Specimen Collection (2)  ·  Magnetic Resonance Imaging (1)  ·  setmelanotide (1)

Sponsors

Vanderbilt University Medical Center (5)  ·  Massachusetts General Hospital (2)  ·  National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) (2)  ·  University of Aarhus (2)  ·  Children's Hospital of Philadelphia (1)  ·  Connecticut Children's Medical Center (1)  ·  Dacima Consulting (1)  ·  F.I.R.M.O. - Fondazione Italiana Ricerca sulle Malattie dell'Osso - Ente del Terzo Settore (1)  ·  Hospices Civils de Lyon (1)  ·  Institut National de la Santé Et de la Recherche Médicale, France (1)  ·  Jaclyn Tamaroff (1)  ·  National Center for Research Resources (NCRR) (1)  ·  National Defense Medical Center, Taiwan (1)  ·  Richever Enterprise Co., Ltd. (1)  ·  University Hospital Augsburg (1)

Countries

United States (12)  ·  Denmark (2)  ·  France (2)  ·  Italy (2)  ·  Germany (1)  ·  Tunisia (1)

Top investigators

Jaclyn Tamaroff, MD (3)  ·  Ashley H Shoemaker, MD (1)  ·  Ashley H Shoemaker, MD, MSCI (1)  ·  Ashley Shoemaker, MD (1)  ·  Emily L Germain-Lee, MD (1)  ·  Lars Rejnmark, DmSci, PhD (1)  ·  Lee S Weinstein, M.D. (1)  ·  Michael A Levine, M.D. (1)  ·  Mitchell E. Geffner (1)  ·  Nabila Rekik Mejdoub, MD (1)  ·  Paolo Beck-Peccoz, MD/PhD (1)  ·  Smita Jha, M.D. (1)

Results publications

PMID 16675931, PMID 17164301, PMID 17652219, PMID 18252944, PMID 20610593, PMID 20719837, PMID 21525160, PMID 24030943, PMID 25894639, PMID 26709970, PMID 29059381, PMID 31145125, PMID 35079678, PMID 35226254, PMID 36662765, PMID 37284613, PMID 37288292, PMID 37339334, PMID 38174154, PMID 39946193, PMID 40709359, PMID 41763924, PMID 42484783, PMID 42620272

NIH funding

K23DK101689 (1), R21HD078864 (1)