Muscular Dystrophy: Clinical Trials

50 trials for Muscular Dystrophy, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

21 completed, 12 recruiting, 7 unknown, 2 active not recruiting. 19 Not applicable, 5 Phase 2, 4 Phase 1, 1 Early Phase 1, 1 Phase 4.

By phase and status

PhaseTrialsStatus
Not applicable19Completed 9, Recruiting 5, Unknown 2, Active not recruiting 1, Enrolling by invitation 1, Not yet recruiting 1
Phase 25Recruiting 2, Unknown 2, Active not recruiting 1
Phase 14Unknown 2, Active not recruiting 1, Withdrawn 1
Early Phase 11Terminated 1
Phase 41Completed 1

Follow Muscular Dystrophy: new trials by email Literature Review of Muscular Dystrophy trials Research Report on Muscular Dystrophy

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
iBCI Optimization for Veterans With Paralysis
Mobile neural decoding platform (mobile iBCI) - Spinal Cord Injury, Amyotrophic Lateral Sclerosis
Not applicableNot yet recruitingVA Office of Research and Development22026-10-022026-07-27
Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients
VM100 Nutritional Supplement - Duchenne Muscular Dystrophy, Duchenne Disease
Phase 2RecruitingUniversity of Florida202026-07-272026-10-08
A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese Children
No interventions are applied; participants are followed for natural history observation only - Muscular Dystrophy, Becker, Muscular Dystrophy
Not yet recruitingWest China Second University Hospital5002026-04-202026-04-06
Amino Acids and Exercise in FSHD
Essential Amino Acids Supplementation intervention, Exercise, Diet - FSH Muscular Dystrophy, Muscular Dystrophy
Not applicableRecruitingUniversity of Pavia482026-04-082026-04-21
Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic Volunteers
Gait analysis via video capture - Spinal Muscular Atrophy (SMA), Charcot-Marie-Tooth
Not applicableRecruitingInstitut de Myologie, France302026-03-032026-05-19
Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.
Digital respiratory intervention program - Duchenne Muscular Dystrophy, Becker Muscular Dystrophy
Not applicableEnrolling by invitationUniversity of Malaga122025-02-052025-04-01
Vasodilator and Exercise Study for DMD (VASO-REx)
Tadalafil, Placebo, Exercise Training - Duchenne Muscular Dystrophy, Duchenne Disease
Phase 2RecruitingUniversity of Florida502024-06-052026-05-15
Nomad P-KAFO Study
Indego Nomad® Powered Knee-Ankle-Foot Orthosis (P-KAFO) (Parker Hannifin Corp., Cleveland, OH) - Cerebrovascular Accident, Post-polio Syndrome
Not applicableRecruitingShirley Ryan AbilityLab362024-03-012026-05-11
Follow-up Study on Female Carriers With DMD Gene Variants
No intervention - Muscular Dystrophy, Duchenne Muscular Dystrophy
Enrolling by invitationCopenhagen University Hospital, Rigshospitalet1032023-05-182025-06-06
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)
AB-1003 dose level 1, AB-1003 dose level 2, Placebo - Limb Girdle Muscular Dystrophy, Limb-Girdle Muscular Dystrophy Type 2
Phase 1 / Phase 2Active not recruitingAskBio Inc92023-05-152026-08-26
Evaluating Long-term Use of a Pediatric Robotic Exoskeleton (P.REX/Agilik) to Improve Gait in Children With Movement Disorders
EA-KAFO - Cerebral Palsy, Muscular Dystrophy
Not applicableRecruitingNational Institutes of Health Clinical Center (CC)442023-05-022026-10-26
Investigational Use of Neuromuscular Ultrasound
Muscular Dystrophy, Peripheral Neuropathy
RecruitingNational Institute of Neurological Disorders and Stroke (NINDS)1502022-04-182026-09-17
Study of Home Use of the Jaco Robotic Manipulation Device by Individuals With Tetraplegia
Use of the JACO robotic arm for a period of 2 months - Tetraplegia, Functional Tetraplegia
Not applicableCompletedAssociation APPROCHE182022-03-302026-07-02
Using NPT to Evaluate Providing PPC as ELNEC-PPC WBT for Nurses
end-of-life nursing education consortium-pediatric palliative care as web based-training plus usual care - Cancer, Cardiac Anomaly
Not applicableUnknownAltoosi University College1722020-07-012020-07-27
Effect of Aquatic Therapy on Pulmonary Functions in Patients With Muscular Dystrophy
aquatic therapy - Muscular Dystrophy
Not applicableUnknownSouth Valley University302020-06-012020-10-05
Evaluation of a Textile Scapula Orthosis
Scapula orthosis assistance, Manual scapula assistance, No assistance - Muscular Dystrophies, Scapular Dyskinesis
Not applicableCompletedSwiss Federal Institute of Technology82019-11-012020-12-16
Clinical Trial Readiness Network FSHD France: Prospective 24 Months MRI Study
Validation of new COA for FSHD patients - Muscular Dystrophy, Facioscapulohumeral
Not applicableActive not recruitingCentre Hospitalier Universitaire de Nice1002019-09-162025-12-03
Awareness Levels of Caregivers of Disabled Children
All of the disabled children's caregivers will answer the Questionnaire of Disease, Physiotherapy and Sports Awareness - Cerebral Palsy, Caregiver Burden
CompletedKahramanmaras Sutcu Imam University562019-04-152022-02-08
The Study of Skeletal Muscle Blood Flow in Becker Muscular Dystrophy
Tadalafil 20 MG, beetroot juice extract - Muscular Dystrophy
Early Phase 1TerminatedCedars-Sinai Medical Center62017-11-012020-01-14
Investigation of Parents' Anxiety Level and Health Related Quality of Life in Different Types of Physical Disabilities
Questionnaire - Cerebral Palsy, Down Syndrome
CompletedSanko University912017-05-012019-07-29

Showing 20 of 50. Sign in to see all of them.

Narrower conditions

Muscular Dystrophies (50)  ·  Muscular Dystrophy, Duchenne (9)  ·  Spinal Cord Injuries (9)  ·  Cerebral Palsy (8)  ·  Amyotrophic Lateral Sclerosis (7)  ·  Spinal Dysraphism (7)  ·  Muscular Diseases (6)  ·  Multiple Sclerosis (5)  ·  Muscular Atrophy, Spinal (5)  ·  Arrhythmias, Cardiac (3)  ·  Brain Stem Infarctions (3)  ·  Cystic Fibrosis (3)  ·  Motor Neuron Disease (3)  ·  Muscular Dystrophy, Facioscapulohumeral (3)  ·  Quadriplegia (3)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (50)  ·  Genetic Diseases, Inborn (50)  ·  Muscular Disorders, Atrophic (50)  ·  Nervous System Diseases (50)  ·  Musculoskeletal Diseases (49)  ·  Neuromuscular Diseases (48)  ·  Muscular Diseases (44)  ·  Central Nervous System Diseases (23)  ·  Spinal Cord Diseases (18)  ·  Neurodegenerative Diseases (16)  ·  Brain Diseases (14)  ·  Congenital Abnormalities (13)  ·  Cardiovascular Diseases (11)  ·  Metabolic Diseases (11)  ·  Nutritional and Metabolic Diseases (11)

Interventions

Brain-Computer Interfaces (2)  ·  Exercise (2)  ·  Tadalafil (2)  ·  Alendronate (1)  ·  Aquatic Therapy (1)  ·  Biopsy (1)  ·  Blood Specimen Collection (1)  ·  Diet (1)  ·  Genetic Testing (1)  ·  Hematologic Tests (1)  ·  High-Energy Shock Waves (1)  ·  Mass Screening (1)  ·  Neural Prostheses (1)  ·  Physical Therapy Modalities (1)  ·  Risedronic Acid (1)

Sponsors

National Institute of Neurological Disorders and Stroke (NINDS) (3)  ·  Chaitanya Hospital, Pune (2)  ·  Copenhagen University Hospital, Rigshospitalet (2)  ·  National Institutes of Health Clinical Center (CC) (2)  ·  Nemours Children's Clinic (2)  ·  University of Florida (2)  ·  Ain Shams University (1)  ·  Altoosi University College (1)  ·  AskBio Inc (1)  ·  Association APPROCHE (1)  ·  Baylor College of Medicine (1)  ·  Beth Israel Deaconess Medical Center (1)  ·  Cedars-Sinai Medical Center (1)  ·  Centre Hospitalier Universitaire de Nice (1)  ·  Centre Hospitalier Universitaire de Saint Etienne (1)

Countries

United States (29)  ·  France (4)  ·  India (3)  ·  Canada (2)  ·  Denmark (2)  ·  Egypt (2)  ·  Turkey (Türkiye) (2)  ·  China (1)  ·  Germany (1)  ·  Iraq (1)  ·  Italy (1)  ·  Mali (1)  ·  Spain (1)  ·  Switzerland (1)

Top investigators

Thomas C Bulea, Ph.D. (2)  ·  A. Reghan Foley, M.D. (1)  ·  Amean A Yaser, Ph.D (1)  ·  Andrew E Arai, M.D. (1)  ·  Benjamin R Brooks, MD (1)  ·  Elizabeth McNally, MD PhD (1)  ·  Gilles Boire, MD, MSc (1)  ·  Ivan R Molton, PhD (1)  ·  Jeffrey A Towbin, MD (1)  ·  Jennifer L Collinger, PhD (1)  ·  Johann Hamel, MD (1)

Results publications

PMID 12030525, PMID 12409823, PMID 14510658, PMID 14760317, PMID 17336067, PMID 18565861, PMID 19251627, PMID 19734901, PMID 20031619, PMID 20117437, PMID 20582942, PMID 20646909, PMID 20685689, PMID 20801717, PMID 21035565, PMID 21146669, PMID 21220724, PMID 21436513, PMID 21438137, PMID 22035077, PMID 22596161, PMID 22609118, PMID 22801503, PMID 22938880, PMID 23152587, PMID 23836708, PMID 23838067, PMID 24526712, PMID 25385765, PMID 25568299, PMID 26247043, PMID 26310427, PMID 26413781, PMID 27872178, PMID 27900953, PMID 28087826, PMID 28220753, PMID 28278476, PMID 28284873, PMID 28363483, PMID 29101272, PMID 29146566, PMID 29160240, PMID 29363625, PMID 29759639, PMID 31041397, PMID 31518302, PMID 31518315, PMID 32066871, PMID 32115343

NIH funding

I01RX003803 (1), K24NS060951 (1), R01DC009899 (1), R01DC014034 (1), R21AR079755 (1), U01DC017844 (1), U01NS123101 (1), U54NS048843 (1), U54NS053672 (1), UH2NS095548 (1)