Muscular Dystrophy: Clinical Trials

4 trials for Muscular Dystrophy, newest first

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2 unknown, 1 active not recruiting, 1 withdrawn. 4 Phase 1, 3 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 14Unknown 2, Active not recruiting 1, Withdrawn 1
Phase 23Unknown 2, Active not recruiting 1

Follow Muscular Dystrophy: new trials by email Literature Review of Muscular Dystrophy trials Research Report on Muscular Dystrophy

Trials (filtered) newest first · largest first

All 4 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)
AB-1003 dose level 1, AB-1003 dose level 2, Placebo - Limb Girdle Muscular Dystrophy, Limb-Girdle Muscular Dystrophy Type 2
Phase 1 / Phase 2Active not recruitingAskBio Inc92023-05-152026-08-26
Study Safety and Efficacy of BMMNC for the Patient With Duchenne Muscular Dystrophy
Intralesional/ Intravenous of Autologous Stem cells. - Muscular Dystrophy, Duchenne Muscular Dystrophy
Phase 1 / Phase 2UnknownChaitanya Hospital, Pune302014-09-012014-09-17
Study Safety and Efficacy of Bone Marrow Derived Autologous Cells for the Treatment of Muscular Dystrophy.
Stem Cell - Muscular Dystrophy, Duchenne Muscular Dystrophy,
Phase 1 / Phase 2UnknownChaitanya Hospital, Pune252014-09-012014-09-17
Stem Cell Therapy in Muscular Dystrophy
Stem Cell - Muscular Dystrophy
Phase 1WithdrawnNeurogen Brain and Spine Institute2009-01-012018-10-25

Narrower conditions

Muscular Dystrophies (4)  ·  Muscular Dystrophy, Duchenne (2)  ·  Limb-girdle muscular dystrophy type 2A (1)  ·  Muscular Diseases (1)  ·  Muscular Dystrophies, Limb-Girdle (1)  ·  Muscular Dystrophy, Limb-Girdle, Type 2I (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4)  ·  Genetic Diseases, Inborn (4)  ·  Muscular Disorders, Atrophic (4)  ·  Musculoskeletal Diseases (4)  ·  Nervous System Diseases (4)  ·  Neuromuscular Diseases (4)  ·  Muscular Diseases (3)  ·  Genetic Diseases, X-Linked (2)

Sponsors

Chaitanya Hospital, Pune (2)  ·  AskBio Inc (1)  ·  Neurogen Brain and Spine Institute (1)

Countries

India (3)  ·  United States (1)