Muscular Dystrophy: Clinical Trials

5 trials for Muscular Dystrophy, newest first

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2 recruiting, 2 unknown, 1 active not recruiting. 5 Phase 2, 3 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 25Recruiting 2, Unknown 2, Active not recruiting 1
Phase 13Unknown 2, Active not recruiting 1

Follow Muscular Dystrophy: new trials by email Literature Review of Muscular Dystrophy trials Research Report on Muscular Dystrophy

Trials (filtered) newest first · largest first

All 5 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients
VM100 Nutritional Supplement - Duchenne Muscular Dystrophy, Duchenne Disease
Phase 2RecruitingUniversity of Florida202026-07-272026-10-08
Vasodilator and Exercise Study for DMD (VASO-REx)
Tadalafil, Placebo, Exercise Training - Duchenne Muscular Dystrophy, Duchenne Disease
Phase 2RecruitingUniversity of Florida502024-06-052026-05-15
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)
AB-1003 dose level 1, AB-1003 dose level 2, Placebo - Limb Girdle Muscular Dystrophy, Limb-Girdle Muscular Dystrophy Type 2
Phase 1 / Phase 2Active not recruitingAskBio Inc92023-05-152026-08-26
Study Safety and Efficacy of BMMNC for the Patient With Duchenne Muscular Dystrophy
Intralesional/ Intravenous of Autologous Stem cells. - Muscular Dystrophy, Duchenne Muscular Dystrophy
Phase 1 / Phase 2UnknownChaitanya Hospital, Pune302014-09-012014-09-17
Study Safety and Efficacy of Bone Marrow Derived Autologous Cells for the Treatment of Muscular Dystrophy.
Stem Cell - Muscular Dystrophy, Duchenne Muscular Dystrophy,
Phase 1 / Phase 2UnknownChaitanya Hospital, Pune252014-09-012014-09-17

Narrower conditions

Muscular Dystrophies (5)  ·  Muscular Dystrophy, Duchenne (4)  ·  Tabes Dorsalis (2)  ·  Aneurysm (1)  ·  Fatigue (1)  ·  Limb-girdle muscular dystrophy type 2A (1)  ·  Motor Activity (1)  ·  Muscular Diseases (1)  ·  Muscular Dystrophies, Limb-Girdle (1)  ·  Muscular Dystrophy, Limb-Girdle, Type 2I (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5)  ·  Genetic Diseases, Inborn (5)  ·  Muscular Disorders, Atrophic (5)  ·  Musculoskeletal Diseases (5)  ·  Nervous System Diseases (5)  ·  Neuromuscular Diseases (5)  ·  Genetic Diseases, X-Linked (4)  ·  Muscular Diseases (4)  ·  Bacterial Infections (2)  ·  Bacterial Infections and Mycoses (2)  ·  Central Nervous System Bacterial Infections (2)  ·  Central Nervous System Diseases (2)  ·  Central Nervous System Infections (2)  ·  Gram-Negative Bacterial Infections (2)  ·  Infections (2)

Interventions

Exercise (1)  ·  Tadalafil (1)

Sponsors

Chaitanya Hospital, Pune (2)  ·  University of Florida (2)  ·  AskBio Inc (1)

Countries

United States (3)  ·  India (2)

Top investigators

Tanja Taivassalo, MD (1)  ·  Tanja Taivassalo, Ph.D. (1)

NIH funding

R21AR079755 (1)