Neurodegenerative Disease, Hereditary: Clinical Trials

5 trials for Neurodegenerative Disease, Hereditary, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 completed, 2 recruiting, 1 not yet recruiting. 1 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 21Not yet recruiting 1
Phase 31Recruiting 1

Follow Neurodegenerative Disease, Hereditary: new trials by email Literature Review of Neurodegenerative Disease, Hereditary trials Research Report on Neurodegenerative Disease, Hereditary

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
MCLENA-2: A Phase II Clinical Trial for the Assessment of Lenalidomide in Patients With Mild Cognitive Impairment
Lenalidomide 10 mg - Cognitive Impairment, Mild, Cognitive Dysfunction
Phase 2Not yet recruitingSt. Joseph's Hospital and Medical Center, Phoenix452025-06-012025-05-18
A Phase 3 Study of NTLA-2001 in ATTRv-PN
nexiguran ziclumeran, Normal Saline as Placebo - Neuromuscular Disease, Neuromuscular Diseases (NMD)
Phase 3RecruitingIntellia Therapeutics602024-11-222026-04-16
Molecular and Functional Imaging in Monogenic PD.
Positron Emission Tomography (PET) scan using DASB tracer - Parkinson Disease, Nervous System Disorder
RecruitingUniversity of Exeter452022-07-012025-10-07
Natural History Study of FDXR Mutation-related Mitochondriopathy
Mutation analysis - Neurodegenerative Disease, Hereditary, Mitochondrial Diseases
CompletedState University of New York at Buffalo332020-11-032024-03-08
Natural History Study of SLC25A46 Mutation-related Mitochondriopathy
Mutation analysis - Neurodegenerative Disease, Hereditary, Mitochondrial Diseases
CompletedState University of New York at Buffalo92020-11-032024-03-08

Narrower conditions

Heredodegenerative Disorders, Nervous System (5)  ·  Mitochondrial Diseases (2)  ·  Nerve Degeneration (2)  ·  Nervous System Diseases (2)  ·  Neurodegenerative Diseases (2)  ·  Optic Atrophy (2)  ·  Alzheimer Disease (1)  ·  Amyloid Neuropathies (1)  ·  Amyloid Neuropathies, Familial (1)  ·  Amyloidosis (1)  ·  Amyloidosis, Familial (1)  ·  Amyloidosis, Hereditary, Transthyretin-Related (1)  ·  Cognitive Dysfunction (1)  ·  Encephalitis (1)  ·  Genetic Diseases, Inborn (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5)  ·  Genetic Diseases, Inborn (4)  ·  Nervous System Diseases (3)  ·  Neurodegenerative Diseases (3)  ·  Nutritional and Metabolic Diseases (3)  ·  Pathological Conditions, Signs and Symptoms (3)  ·  Brain Diseases (2)  ·  Central Nervous System Diseases (2)  ·  Cranial Nerve Diseases (2)  ·  Eye Diseases (2)  ·  Metabolic Diseases (2)  ·  Optic Nerve Diseases (2)  ·  Pathologic Processes (2)  ·  Basal Ganglia Diseases (1)  ·  Cognition Disorders (1)

Interventions

2-phenyl-6-(2'-(4'-(ethoxycarbonyl)thiazolyl))thiazolo(3,2-b)(1,2,4)triazole (1)  ·  Lenalidomide (1)  ·  Magnetic Resonance Spectroscopy (1)  ·  NTLA-2001 (1)  ·  Saline Solution (1)  ·  Spinal Puncture (1)

Sponsors

State University of New York at Buffalo (2)  ·  Intellia Therapeutics (1)  ·  St. Joseph's Hospital and Medical Center, Phoenix (1)  ·  University of Exeter (1)

Countries

United States (2)  ·  Argentina (1)  ·  Brazil (1)  ·  Mexico (1)  ·  Singapore (1)  ·  Taiwan (1)  ·  Thailand (1)  ·  United Kingdom (1)

Top investigators

Taosheng Huang (2)  ·  Marios Politits, Professor (1)