Permanent Neonatal Diabetes Mellitus: Clinical Trials

1 active not recruiting, 1 completed, 1 unknown. 2 Phase 4.

By phase and status

Phase	Trials	Status
Phase 4	2	Completed 1, Unknown 1

Follow Permanent Neonatal Diabetes Mellitus: new trials by email Literature Review of Permanent Neonatal Diabetes Mellitus trials Research Report on Permanent Neonatal Diabetes Mellitus

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

Trial	Phase	Status	Sponsor	Enrollment	Start	Updated
Long-Term Sulfonylurea Response in ABCC8 Neonatal Diabetes (SuResponsSUR) Sulfonylurea - Permanent Neonatal Diabetes Mellitus	Phase 4	Unknown	Haukeland University Hospital	30	2019-02-15	2020-02-12
Early Check: Expanded Screening in Newborns Confirmatory Testing - Spinal Muscular Atrophy, Fragile X Syndrome		Active not recruiting	RTI International	30000	2018-10-15	2026-07-01
Long-Term Sulfonylurea Response in KCNJ11 Neonatal Diabetes Sulfonylurea - Permanent Neonatal Diabetes Mellitus	Phase 4	Completed	Haukeland University Hospital	90	2015-12-01	2017-10-03

Narrower conditions

Diabetes Mellitus, Permanent Neonatal (3)  ·  3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency (1)  ·  3-Hydroxyacyl-CoA Dehydrogenase Deficiency (1)  ·  3-methylcrotonyl CoA carboxylase 1 deficiency (1)  ·  3-methylcrotonyl CoA carboxylase 2 deficiency (1)  ·  Acidemia, isovaleric (1)  ·  Acrodermatitis enteropathica (1)  ·  Adenine phosphoribosyltransferase deficiency (1)  ·  Adrenal hyperplasia, congenital, type 5 (1)  ·  Adrenocorticotropic hormone deficiency (1)  ·  Amaurosis congenita of Leber, type 2 (1)  ·  Anemia, Sickle Cell (1)  ·  Angelman Syndrome (1)  ·  Aortic Stenosis, Supravalvular (1)  ·  Arginine-Glycine Amidinotransferase Deficiency (1)

Broader conditions

Abnormalities, Multiple (1)  ·  Albinism (1)  ·  Albinism, Oculocutaneous (1)  ·  Amino Acid Metabolism, Inborn Errors (1)  ·  Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Aortic Valve Disease (1)  ·  Aortic Valve Stenosis (1)  ·  Arrhythmias, Cardiac (1)  ·  Avitaminosis (1)  ·  Basal Ganglia Diseases (1)  ·  Blood Coagulation Disorders (1)  ·  Blood Coagulation Disorders, Inherited (1)  ·  Blood Platelet Disorders (1)

Interventions

Glyburide (2)  ·  Sulfonylurea Compounds (2)

Sponsors

Haukeland University Hospital (2)  ·  RTI International (1)

Countries

Norway (2)  ·  United States (1)

Top investigators

Curt Scharfe, MD, PhD (1)

Results publications

PMID 11372010, PMID 15115830, PMID 15448106, PMID 16885549, PMID 16885550, PMID 18025408, PMID 29880308, PMID 31315600, PMID 31932458, PMID 33184150, PMID 35142618, PMID 8988180