1 active not recruiting, 1 completed, 1 unknown. 2 Phase 4.
| Phase | Trials | Status |
|---|---|---|
| Phase 4 | 2 | Completed 1, Unknown 1 |
Follow Diabetes Mellitus, Permanent Neonatal: new trials by email Literature Review of Diabetes Mellitus, Permanent Neonatal trials Research Report on Diabetes Mellitus, Permanent Neonatal
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Long-Term Sulfonylurea Response in ABCC8 Neonatal Diabetes (SuResponsSUR) Sulfonylurea - Permanent Neonatal Diabetes Mellitus | Phase 4 | Unknown | Haukeland University Hospital | 30 | 2019-02-15 | 2020-02-12 |
| Early Check: Expanded Screening in Newborns Confirmatory Testing - Spinal Muscular Atrophy, Fragile X Syndrome | Active not recruiting | RTI International | 30000 | 2018-10-15 | 2026-07-01 | |
| Long-Term Sulfonylurea Response in KCNJ11 Neonatal Diabetes Sulfonylurea - Permanent Neonatal Diabetes Mellitus | Phase 4 | Completed | Haukeland University Hospital | 90 | 2015-12-01 | 2017-10-03 |
3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency (1) · 3-Hydroxyacyl-CoA Dehydrogenase Deficiency (1) · 3-methylcrotonyl CoA carboxylase 1 deficiency (1) · 3-methylcrotonyl CoA carboxylase 2 deficiency (1) · Acidemia, isovaleric (1) · Acrodermatitis enteropathica (1) · Adenine phosphoribosyltransferase deficiency (1) · Adrenal hyperplasia, congenital, type 5 (1) · Adrenocorticotropic hormone deficiency (1) · Amaurosis congenita of Leber, type 2 (1) · Anemia, Sickle Cell (1) · Angelman Syndrome (1) · Aortic Stenosis, Supravalvular (1) · Arginine-Glycine Amidinotransferase Deficiency (1)
Abnormalities, Multiple (1) · Albinism (1) · Albinism, Oculocutaneous (1) · Amino Acid Metabolism, Inborn Errors (1) · Anemia (1) · Anemia, Hemolytic (1) · Anemia, Hemolytic, Congenital (1) · Aortic Valve Disease (1) · Aortic Valve Stenosis (1) · Arrhythmias, Cardiac (1) · Avitaminosis (1) · Basal Ganglia Diseases (1) · Blood Coagulation Disorders (1) · Blood Coagulation Disorders, Inherited (1) · Blood Platelet Disorders (1)
Glyburide (2) · Sulfonylurea Compounds (2)
Haukeland University Hospital (2) · RTI International (1)
Norway (2) · United States (1)
PMID 11372010, PMID 15115830, PMID 15448106, PMID 16885549, PMID 16885550, PMID 18025408, PMID 29880308, PMID 31315600, PMID 31932458, PMID 33184150, PMID 35142618, PMID 8988180