Diabetes Mellitus, Permanent Neonatal: Clinical Trials

3 trials for Diabetes Mellitus, Permanent Neonatal, newest first

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1 active not recruiting, 1 completed, 1 unknown. 2 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 42Completed 1, Unknown 1

Follow Diabetes Mellitus, Permanent Neonatal: new trials by email Literature Review of Diabetes Mellitus, Permanent Neonatal trials Research Report on Diabetes Mellitus, Permanent Neonatal

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Long-Term Sulfonylurea Response in ABCC8 Neonatal Diabetes (SuResponsSUR)
Sulfonylurea - Permanent Neonatal Diabetes Mellitus
Phase 4UnknownHaukeland University Hospital302019-02-152020-02-12
Early Check: Expanded Screening in Newborns
Confirmatory Testing - Spinal Muscular Atrophy, Fragile X Syndrome
Active not recruitingRTI International300002018-10-152026-07-01
Long-Term Sulfonylurea Response in KCNJ11 Neonatal Diabetes
Sulfonylurea - Permanent Neonatal Diabetes Mellitus
Phase 4CompletedHaukeland University Hospital902015-12-012017-10-03

Narrower conditions

3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency (1)  ·  3-Hydroxyacyl-CoA Dehydrogenase Deficiency (1)  ·  3-methylcrotonyl CoA carboxylase 1 deficiency (1)  ·  3-methylcrotonyl CoA carboxylase 2 deficiency (1)  ·  Acidemia, isovaleric (1)  ·  Acrodermatitis enteropathica (1)  ·  Adenine phosphoribosyltransferase deficiency (1)  ·  Adrenal hyperplasia, congenital, type 5 (1)  ·  Adrenocorticotropic hormone deficiency (1)  ·  Amaurosis congenita of Leber, type 2 (1)  ·  Anemia, Sickle Cell (1)  ·  Angelman Syndrome (1)  ·  Aortic Stenosis, Supravalvular (1)  ·  Arginine-Glycine Amidinotransferase Deficiency (1)

Broader conditions

Abnormalities, Multiple (1)  ·  Albinism (1)  ·  Albinism, Oculocutaneous (1)  ·  Amino Acid Metabolism, Inborn Errors (1)  ·  Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Aortic Valve Disease (1)  ·  Aortic Valve Stenosis (1)  ·  Arrhythmias, Cardiac (1)  ·  Avitaminosis (1)  ·  Basal Ganglia Diseases (1)  ·  Blood Coagulation Disorders (1)  ·  Blood Coagulation Disorders, Inherited (1)  ·  Blood Platelet Disorders (1)

Interventions

Glyburide (2)  ·  Sulfonylurea Compounds (2)

Sponsors

Haukeland University Hospital (2)  ·  RTI International (1)

Countries

Norway (2)  ·  United States (1)

Top investigators

Curt Scharfe, MD, PhD (1)

Results publications

PMID 11372010, PMID 15115830, PMID 15448106, PMID 16885549, PMID 16885550, PMID 18025408, PMID 29880308, PMID 31315600, PMID 31932458, PMID 33184150, PMID 35142618, PMID 8988180