3 completed, 1 active not recruiting, 1 not yet recruiting, 1 unknown. 1 Early Phase 1, 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Early Phase 1 | 1 | Not yet recruiting 1 |
| Phase 1 | 1 | Completed 1 |
Follow Acidemia, isovaleric: new trials by email Literature Review of Acidemia, isovaleric trials Research Report on Acidemia, isovaleric
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Prospective Single-Arm Study(NCLDR) Low dose radiotherapy regimen, New adjuvant immunotherapy regimen, Surgical treatment - Oral Squamous Cell Carcinoma (OSCC) | Early Phase 1 | Not yet recruiting | Qilu Hospital of Shandong University | 35 | 2025-08-30 | 2025-06-19 |
| Selective Screening of Children for Hereditary Metabolic Diseases by Tandem Mass Spectrometry in Kazakhstan Obtaining Dry Blood Spots From Healthy Newborns (Aged 1-7 Days), Obtaining Dry Blood Spots From Healthy Children Aged 8 Days - 7 Years, Obtaining Dry Blood Spots From Healthy Children Aged 8-18 Years - Propionic/Methylmalonic Acidemias, Maple Syrup Urine Disease | Unknown | West Kazakhstan Medical University | 2250 | 2022-10-03 | 2023-06-18 | |
| Baby Detect : Genomic Newborn Screening Congenital Adrenal Hyperplasia, Familial Hyperinsulinemic Hypoglycemia 1 | Completed | Centre Hospitalier Universitaire de Liege | 6824 | 2022-09-01 | 2025-08-12 | |
| Early Check: Expanded Screening in Newborns Confirmatory Testing - Spinal Muscular Atrophy, Fragile X Syndrome | Active not recruiting | RTI International | 30000 | 2018-10-15 | 2026-07-01 | |
| A Study of Nelfinavir Added to Cisplatin Chemotherapy Concurrent With Pelvic Radiation for Locally Advanced Cervical Cancer (II-IVA) Nelfinavir, Cisplatin - Uterine Cervix Cancer | Phase 1 | Completed | Abramson Cancer Center at Penn Medicine | 6 | 2015-02-01 | 2020-04-06 |
| In Vitro Activation of Dormant Follicles for Patients With Primary Ovarian Insufficiency Ovariotomy, Activate dormant follicles, Ovary tissue transplantation - in Vitro Activation, Dormant Follicle | Completed | The First Affiliated Hospital of Zhengzhou University | 35 | 2014-09-01 | 2026-05-27 |
3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency (3) · Argininosuccinic Aciduria (3) · Beta ketothiolase deficiency (3) · Biotinidase Deficiency (3) · Carbamoyl-Phosphate Synthase I Deficiency Disease (3) · Carnitine palmitoyl transferase 1A deficiency (3) · Carnitine palmitoyl transferase 2 deficiency (3) · Carnitine-Acylcarnitine Translocase Deficiency (3) · Citrullinemia (3) · Glutaric Acidemia I (3) · Homocystinuria (3) · Hyperargininemia (3) · Medium chain acyl CoA dehydrogenase deficiency (3) · Ornithine Carbamoyltransferase Deficiency Disease (3)
Female Urogenital Diseases (4) · Female Urogenital Diseases and Pregnancy Complications (4) · Neoplasms (4) · Neoplasms by Site (4) · Urogenital Diseases (4) · Amino Acid Metabolism, Inborn Errors (3) · Brain Diseases (3) · Brain Diseases, Metabolic (3) · Brain Diseases, Metabolic, Inborn (3) · Carbohydrate Metabolism, Inborn Errors (3) · Central Nervous System Diseases (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Connective Tissue Diseases (3) · Endocrine System Diseases (3) · Genetic Diseases, Inborn (3)
Aging (1) · Cisplatin (1) · Nelfinavir (1) · Surgical Procedures, Operative (1)
Abramson Cancer Center at Penn Medicine (1) · Centre Hospitalier Universitaire de Liege (1) · Qilu Hospital of Shandong University (1) · RTI International (1) · The First Affiliated Hospital of Zhengzhou University (1) · West Kazakhstan Medical University (1)
United States (2) · Belgium (1) · China (1) · Kazakhstan (1)
Curt Scharfe, MD, PhD (1) · Fiona Simpkins, MD (1) · Gulmira M. Zharmakhanova, MD, PhD (1) · Laurent Servais (1) · Lilie Lin, MD (1) · Lyazzat M. Syrlybayeva, MD (1) · Victoria I. Kononets, MD, MS (1) · Yingpu Sun, MD,PhD (1)