2 recruiting, 1 completed, 1 terminated. 1 Phase 1, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
| Phase 3 | 1 | Terminated 1 |
Follow Limb-girdle muscular dystrophy, type 1B: new trials by email Literature Review of Limb-girdle muscular dystrophy, type 1B trials Research Report on Limb-girdle muscular dystrophy, type 1B
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Long-Term Development of Muscular Dystrophy Outcome Assessments LGMD1B, LGMD1C | Recruiting | Virginia Commonwealth University | 1000 | 2023-10-18 | 2025-11-18 | |
| A Study To Evaluate The Pharmacokinetics, Excretion, Mass Balance and Metabolism of PF-07265803 PF-07265803 - Healthy | Phase 1 | Completed | Pfizer | 6 | 2022-03-31 | 2024-03-29 |
| A Study of ARRY-371797 (PF-07265803) in Patients With Symptomatic Dilated Cardiomyopathy Due to a Lamin A/C Gene Mutation ARRY-371797 (PF-07265803), Placebo - Dilated Cardiomyopathy, Lamin A/C Gene Mutation | Phase 3 | Terminated | Pfizer | 77 | 2018-04-17 | 2024-01-09 |
| Natural History Study for Charcot Marie Tooth Disease Charcot-Marie-Tooth Disease, Charcot-Marie-Tooth | Recruiting | Hereditary Neuropathy Foundation | 10000 | 2013-11-01 | 2026-09-17 |
Cardiomyopathies (2) · Heart Failure (2) · Cardiomyopathy, Dilated (1) · Charcot-Marie-Tooth Disease (1) · Charcot-Marie-Tooth Disease, Axonal, Type 2A2 (1) · Charcot-Marie-Tooth Disease, Axonal, Type 2a1 (1) · Charcot-Marie-Tooth Disease, Axonal, Type 2n (1) · Charcot-Marie-Tooth Disease, Type 4H (1) · Charcot-Marie-Tooth disease and deafness (1) · Charcot-Marie-Tooth disease, Type 1C (1) · Charcot-Marie-Tooth disease, Type 1D (1) · Charcot-Marie-Tooth disease, Type 1F (1) · Charcot-Marie-Tooth disease, Type 2A (1) · Charcot-Marie-Tooth disease, Type 2B2 (1)
Cardiovascular Diseases (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Genetic Diseases, Inborn (3) · Heart Diseases (3) · Congenital Abnormalities (2) · Heredodegenerative Disorders, Nervous System (2) · Nervous System Diseases (2) · Nervous System Malformations (2) · Neurodegenerative Diseases (2) · Neuromuscular Diseases (2) · Cardiomegaly (1) · Cardiomyopathies (1) · Cobblestone Lissencephaly (1) · Eye Diseases (1) · Eye Diseases, Hereditary (1)
ARRY-371797 (1)
Pfizer (2) · Hereditary Neuropathy Foundation (1) · Virginia Commonwealth University (1)
United States (4) · Argentina (1) · Belgium (1) · Canada (1) · Italy (1) · Mexico (1) · Netherlands (1) · Norway (1) · Spain (1) · United Kingdom (1)
Allison Moore (1) · Nicholas Johnson, MD (1)
PMID 36718638, PMID 37010012, PMID 38979608, PMID 39145700, PMID 41693767
2017 (1)