Glanzmann Thrombasthenia: Clinical Trials

4 trials for Glanzmann Thrombasthenia, newest first

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2 terminated, 1 active not recruiting, 1 recruiting. 4 Phase 2, 2 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 24Terminated 2, Active not recruiting 1, Recruiting 1
Phase 12Active not recruiting 1, Terminated 1

Follow Glanzmann Thrombasthenia: new trials by email Literature Review of Glanzmann Thrombasthenia trials Research Report on Glanzmann Thrombasthenia

Trials (filtered) newest first · largest first

All 4 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Eptacog Beta in Glanzmann's (HeT_LFB-Strength-Study_FID531)
EPTACOG BETA - Glanzmann Thrombasthenia
Phase 2RecruitingEmory University62025-10-022025-12-01
A Phase 1/2 Study to Investigate Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of HMB-001 in Glanzmann Thrombasthenia
HMB-001 - Glanzmann Thrombasthenia
Phase 1 / Phase 2Active not recruitingHemab ApS572022-12-132026-09-25
Study of Coagulation Factor VIIa Marzeptacog Alfa (Activated) in Subjects With Inherited Bleeding Disorders
Coagulation Factor VIIa variant - Factor VII Deficiency, Glanzmann Thrombasthenia
Phase 1 / Phase 2TerminatedCatalyst Biosciences192021-05-172021-12-21
Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood Cancer
Cyclophosphamide, Fludarabine Phosphate, Laboratory Biomarker Analysis - Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission
Phase 2TerminatedRoswell Park Cancer Institute312017-12-072025-07-04

Narrower conditions

Thrombasthenia (4)  ·  Anemia, Aplastic (1)  ·  Anemia, Diamond-Blackfan (1)  ·  Anemia, Sickle Cell (1)  ·  Congenital amegakaryocytic thrombocytopenia (1)  ·  Factor VII Deficiency (1)  ·  Granulomatous Disease, Chronic (1)  ·  Hemoglobinuria, Paroxysmal (1)  ·  Hemorrhage (1)  ·  Immunologic Deficiency Syndromes (1)  ·  Leukemia, Lymphocytic, Chronic, B-Cell (1)  ·  Leukemia, Myelogenous, Chronic, BCR-ABL Positive (1)  ·  Leukemia, Myeloid, Accelerated Phase (1)  ·  Leukemia, Myeloid, Acute (1)  ·  Leukemia, Myeloid, Chronic-Phase (1)

Broader conditions

Blood Coagulation Disorders (4)  ·  Blood Coagulation Disorders, Inherited (4)  ·  Blood Platelet Disorders (4)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4)  ·  Genetic Diseases, Inborn (4)  ·  Hematologic Diseases (4)  ·  Hemic and Lymphatic Diseases (4)  ·  Hemorrhagic Disorders (4)  ·  Pathologic Processes (2)  ·  Pathological Conditions, Signs and Symptoms (2)  ·  Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Anemia, Hypoplastic, Congenital (1)  ·  Blood Protein Disorders (1)

Interventions

Cyclophosphamide (1)  ·  Peripheral Blood Stem Cell Transplantation (1)  ·  Whole-Body Irradiation (1)  ·  fludarabine phosphate (1)  ·  recombinant FVIIa (1)

Sponsors

Catalyst Biosciences (1)  ·  Emory University (1)  ·  Hemab ApS (1)  ·  Roswell Park Cancer Institute (1)

Countries

United States (4)  ·  Italy (2)  ·  Belgium (1)  ·  France (1)  ·  India (1)  ·  Netherlands (1)  ·  Russia (1)  ·  Ukraine (1)  ·  United Kingdom (1)

Top investigators

Karen Zimowski, MD (1)  ·  Philip McCarthy, MD (1)