2 terminated, 1 active not recruiting, 1 recruiting. 4 Phase 2, 2 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 4 | Terminated 2, Active not recruiting 1, Recruiting 1 |
| Phase 1 | 2 | Active not recruiting 1, Terminated 1 |
Follow Glanzmann Thrombasthenia: new trials by email Literature Review of Glanzmann Thrombasthenia trials Research Report on Glanzmann Thrombasthenia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Eptacog Beta in Glanzmann's (HeT_LFB-Strength-Study_FID531) EPTACOG BETA - Glanzmann Thrombasthenia | Phase 2 | Recruiting | Emory University | 6 | 2025-10-02 | 2025-12-01 |
| A Phase 1/2 Study to Investigate Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of HMB-001 in Glanzmann Thrombasthenia HMB-001 - Glanzmann Thrombasthenia | Phase 1 / Phase 2 | Active not recruiting | Hemab ApS | 57 | 2022-12-13 | 2026-09-25 |
| Study of Coagulation Factor VIIa Marzeptacog Alfa (Activated) in Subjects With Inherited Bleeding Disorders Coagulation Factor VIIa variant - Factor VII Deficiency, Glanzmann Thrombasthenia | Phase 1 / Phase 2 | Terminated | Catalyst Biosciences | 19 | 2021-05-17 | 2021-12-21 |
| Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood Cancer Cyclophosphamide, Fludarabine Phosphate, Laboratory Biomarker Analysis - Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission | Phase 2 | Terminated | Roswell Park Cancer Institute | 31 | 2017-12-07 | 2025-07-04 |
Thrombasthenia (4) · Anemia, Aplastic (1) · Anemia, Diamond-Blackfan (1) · Anemia, Sickle Cell (1) · Congenital amegakaryocytic thrombocytopenia (1) · Factor VII Deficiency (1) · Granulomatous Disease, Chronic (1) · Hemoglobinuria, Paroxysmal (1) · Hemorrhage (1) · Immunologic Deficiency Syndromes (1) · Leukemia, Lymphocytic, Chronic, B-Cell (1) · Leukemia, Myelogenous, Chronic, BCR-ABL Positive (1) · Leukemia, Myeloid, Accelerated Phase (1) · Leukemia, Myeloid, Acute (1) · Leukemia, Myeloid, Chronic-Phase (1)
Blood Coagulation Disorders (4) · Blood Coagulation Disorders, Inherited (4) · Blood Platelet Disorders (4) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4) · Genetic Diseases, Inborn (4) · Hematologic Diseases (4) · Hemic and Lymphatic Diseases (4) · Hemorrhagic Disorders (4) · Pathologic Processes (2) · Pathological Conditions, Signs and Symptoms (2) · Anemia (1) · Anemia, Hemolytic (1) · Anemia, Hemolytic, Congenital (1) · Anemia, Hypoplastic, Congenital (1) · Blood Protein Disorders (1)
Cyclophosphamide (1) · Peripheral Blood Stem Cell Transplantation (1) · Whole-Body Irradiation (1) · fludarabine phosphate (1) · recombinant FVIIa (1)
Catalyst Biosciences (1) · Emory University (1) · Hemab ApS (1) · Roswell Park Cancer Institute (1)
United States (4) · Italy (2) · Belgium (1) · France (1) · India (1) · Netherlands (1) · Russia (1) · Ukraine (1) · United Kingdom (1)
Karen Zimowski, MD (1) · Philip McCarthy, MD (1)