3 recruiting, 2 unknown, 1 active not recruiting, 1 completed. 2 Not applicable, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 2 | Recruiting 1, Unknown 1 |
| Phase 3 | 1 | Completed 1 |
Follow Familial Hypercholesterolaemia: new trials by email Literature Review of Familial Hypercholesterolaemia trials Research Report on Familial Hypercholesterolaemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| An Observational Study to Evaluate Treatment Patterns in High, Very High and Extreme Cardiovascular Risk Patients With Hypercholesterolemia, Including Familial Hypercholesterolemia Hypercholesterolaemia, Familial Hypercholesterolaemia | Not yet recruiting | Fondazione SISA (Societa Italiana per lo Studio della Arteriosclerosi) | 2500 | 2026-10-01 | 2026-08-21 | |
| Cardiovascular Risk in Children With Chronic Conditions Study Kidney Transplant, Familial Hypercholesterolaemia | Recruiting | Semmelweis University | 300 | 2025-04-01 | 2025-08-08 | |
| Computerized Decision Support for Identification and Management of Familial Hypercholesterolemia Alert-based computerized decision support - Familial Hypercholesterolaemia | Not applicable | Recruiting | Brigham and Women's Hospital | 450 | 2025-04-01 | 2026-09-29 |
| Specified Drug-use Survey of Leqvio for s.c. Injection. inclisiran - Familial Hypercholesterolaemia, Hypercholesterolaemia | Active not recruiting | Novartis Pharmaceuticals | 585 | 2024-03-04 | 2026-08-06 | |
| Pilot Project of Familial Hypercholesterolemia Screening in Newborns in the Czech Republic Total cholesterol (TC) level test and direct Low density lipoprotein cholesterol (LDL-C) level test, DNA testing - Familial Hypercholesterolaemia | Unknown | Institute of Health Information and Statistics of the Czech Republic | 10000 | 2021-07-01 | 2022-12-06 | |
| Postprandial Lipid Metabolism in Familial Hypercholesterolaemia:Effects of Fish Oils Fish oil capsule, HMG Coenzyme reductase - Hypertriglyceridaemia, Familial Hypercholesterolaemia | Not applicable | Unknown | The University of Western Australia | 30 | 2012-04-01 | 2012-04-13 |
| An Study to Evaluate Rosuvastatin in Children and Adolescents With Familial Hypercholesterolaemia rosuvastatin calcium - Familial Hypercholesterolaemia | Phase 3 | Completed | AstraZeneca | 315 | 2010-02-01 | 2015-04-07 |
| The Spanish Familial Hypercholesterolaemia Cohort Study Familial Hypercholesterolaemia | Recruiting | Fundación Hipercolesterolemia Familiar | 4141 | 2004-01-01 | 2026-09-04 |
Hyperlipoproteinemia Type II (8) · Hypercholesterolemia (3) · Cardiovascular Diseases (2) · Aortic Coarctation (1) · Aortic Valve Stenosis (1) · Diabetes Mellitus, Type 1 (1) · Diabetes Mellitus, Type 2 (1) · HIV Infections (1) · Homozygous Familial Hypercholesterolemia (1) · Hypertension (1) · Hypertension, Pulmonary (1) · Hypertriglyceridemia (1) · Inflammatory Bowel Diseases (1) · Leukemia (1) · Lymphoma (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (8) · Dyslipidemias (8) · Genetic Diseases, Inborn (8) · Hyperlipidemias (8) · Hyperlipoproteinemias (8) · Lipid Metabolism Disorders (8) · Lipid Metabolism, Inborn Errors (8) · Metabolic Diseases (8) · Metabolism, Inborn Errors (8) · Nutritional and Metabolic Diseases (8) · Aortic Valve Disease (1) · Autoimmune Diseases (1) · Blood-Borne Infections (1) · Body Weight (1) · Cardiovascular Abnormalities (1)
ALN-PCS (1) · Fish Oils (1) · Hydroxymethylglutaryl-CoA Reductase Inhibitors (1) · Omacor (1) · Rosuvastatin Calcium (1)
AstraZeneca (1) · Brigham and Women's Hospital (1) · Fondazione SISA (Societa Italiana per lo Studio della Arteriosclerosi) (1) · Fundación Hipercolesterolemia Familiar (1) · Institute of Health Information and Statistics of the Czech Republic (1) · Novartis Pharmaceuticals (1) · Semmelweis University (1) · The University of Western Australia (1)
United States (2) · Australia (1) · Belgium (1) · Canada (1) · Czechia (1) · Hungary (1) · Japan (1) · Netherlands (1) · Norway (1) · Spain (1)
Dick Chan, Phd (1) · John J.P. Kastelein, MD, PhD (1) · Pedro Mata, MD (1) · Tamas Kiss, MD, PhD (1)
PMID 23684512, PMID 24192652, PMID 27444203, PMID 27490922, PMID 27614801, PMID 28275165, PMID 28391894, PMID 28592434, PMID 29753733, PMID 32201274, PMID 33261814, PMID 33437997, PMID 34864959, PMID 36416136, PMID 37202042, PMID 38523000, PMID 39098315, PMID 42290618