5 recruiting. 5 Phase 3, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 5 | Recruiting 5 |
| Phase 2 | 1 | Recruiting 1 |
Follow Dwarfism: new trials by email Literature Review of Dwarfism trials Research Report on Dwarfism
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| GB06 Phase III Trial for Pediatric Growth Hormone Deficiency GB06, Norditropin®FlexProTM - Growth Hormone Deficiency (GHD), Growth Hormone Deficiency in Children | Phase 3 | Recruiting | Kexing Biopharm Co., Ltd. | 192 | 2026-06-06 | 2026-06-10 |
| Phase 3 Study of LUM-201 in Children With Growth Hormone Deficiency LUM-201, Matched Placebo (Capsules) - Growth Hormone Deficiency (GHD) | Phase 3 | Recruiting | Lumos Pharma | 150 | 2026-05-20 | 2026-10-19 |
| Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia BMN 333, Vosoritide Injection [Voxzogo] - Achondroplasia | Phase 2 / Phase 3 | Recruiting | BioMarin Pharmaceutical | 160 | 2026-04-20 | 2026-10-22 |
| Trial Investigating the Efficacy and Safety of Weekly Lonapegsomatropin Compared to Daily Somatropin in Children and Adolescents With Short Stature or Growth Failure Due to Growth Hormone Sufficient Disorders Lonapegsomatropin [SKYTROFA®], Somatropin Pen Injector - Turner Syndrome, Short Stature Homeobox Gene Mutation | Phase 3 | Recruiting | Ascendis Pharma A/S | 186 | 2025-12-12 | 2026-11-05 |
| Growth Hormone Replacement Therapy in Veterans With Mild Traumatic Brain Injury (mTBI) and Adult Growth Hormone Deficiency (AGHD) Somatropin, Placebo - Adult Growth Hormone Deficiency, Mild Traumatic Brain Injury | Phase 3 | Recruiting | VA Office of Research and Development | 172 | 2025-01-13 | 2026-10-13 |
Dwarfism, Pituitary (3) · Achondroplasia (1) · Bone Diseases (1) · Brain Concussion (1) · Chromosome Disorders (1) · Endocrine System Diseases (1) · Failure to Thrive (1) · Genetic Diseases, Inborn (1) · Musculoskeletal Diseases (1) · Noonan Syndrome (1) · Osteochondrodysplasias (1) · Sex Chromosome Disorders (1) · Sex Chromosome Disorders of Sex Development (1) · Turner Syndrome (1)
Bone Diseases, Developmental (5) · Bone Diseases (4) · Musculoskeletal Diseases (4) · Bone Diseases, Endocrine (3) · Brain Diseases (3) · Central Nervous System Diseases (3) · Endocrine System Diseases (3) · Hypopituitarism (3) · Hypothalamic Diseases (3) · Nervous System Diseases (3) · Pituitary Diseases (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Brain Injuries (1) · Brain Injuries, Traumatic (1)
Capsules (1) · Human Growth Hormone (1) · lonapegsomatropin (1) · vosoritide (1)
Ascendis Pharma A/S (1) · BioMarin Pharmaceutical (1) · Kexing Biopharm Co., Ltd. (1) · Lumos Pharma (1) · VA Office of Research and Development (1)
United States (4) · Australia (2) · Italy (2) · Romania (2) · South Korea (2) · United Kingdom (2) · Argentina (1) · Canada (1) · Chile (1) · China (1) · France (1) · Germany (1) · India (1) · Japan (1) · New Zealand (1)
2018 (1)