DNA Repair-Deficiency Disorders: Clinical Trials

3 trials for DNA Repair-Deficiency Disorders, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 completed, 1 unknown, 1 withdrawn. 3 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 43Completed 1, Unknown 1, Withdrawn 1

Follow DNA Repair-Deficiency Disorders: new trials by email Literature Review of DNA Repair-Deficiency Disorders trials Research Report on DNA Repair-Deficiency Disorders

Trials (filtered) newest first · largest first

All 3 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Retroviral Insertion Site Methodology Study
Strimvelis - Immune System Diseases
Phase 4WithdrawnFondazione Telethon2020-06-252024-01-29
Response of Individuals With Ataxia-Telangiectasia to Metformin and Pioglitazone
Metformin, Pioglitazone - Ataxia-Telangiectasia
Phase 4CompletedNHS Tayside272016-09-292017-12-04
Status of Growth Hormone/ Insulin-like Growth Factor-1 (GH/IGF-1) Axis and Growth Failure in Ataxia Telangiectasia (AT)
Somatropin, Clonidine, L-Arginin-Hydrochloride, Estradiol valerate - Ataxia Telangiectasia, Growth Failure
Phase 4UnknownJohann Wolfgang Goethe University Hospital242010-01-012010-07-05

Narrower conditions

Ataxia Telangiectasia (2)  ·  Failure to Thrive (1)  ·  Immune System Diseases (1)  ·  Severe Combined Immunodeficiency (1)  ·  Severe combined immunodeficiency due to adenosine deaminase deficiency (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Genetic Diseases, Inborn (3)  ·  Immunologic Deficiency Syndromes (3)  ·  Metabolic Diseases (3)  ·  Nutritional and Metabolic Diseases (3)  ·  Primary Immunodeficiency Diseases (3)  ·  Ataxia (2)  ·  Brain Diseases (2)  ·  Cardiovascular Diseases (2)  ·  Central Nervous System Diseases (2)  ·  Cerebellar Ataxia (2)  ·  Cerebellar Diseases (2)  ·  Dyskinesias (2)  ·  Immune System Diseases (2)

Interventions

Clonidine (1)  ·  Estradiol (1)  ·  Growth Hormone (1)  ·  Human Growth Hormone (1)  ·  Metformin (1)  ·  Pioglitazone (1)

Sponsors

Fondazione Telethon (1)  ·  Johann Wolfgang Goethe University Hospital (1)  ·  NHS Tayside (1)

Countries

Germany (1)  ·  United Kingdom (1)

Top investigators

Ewan Pearson, MD PhD (1)  ·  Fondazione Telethon (1)  ·  Stefan Zielen, Prof. Dr. (1)