Craniofacial Abnormalities: Clinical Trials

3 trials for Craniofacial Abnormalities, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

3 active not recruiting. 3 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 23Active not recruiting 3

Follow Craniofacial Abnormalities: new trials by email Literature Review of Craniofacial Abnormalities trials Research Report on Craniofacial Abnormalities

Trials (filtered) newest first · largest first

All 3 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study of Vosoritide in Children With Noonan Syndrome With Inadequate Growth During or After Human Growth Hormone Treatment
Vosoritide Injection - Noonan Syndrome
Phase 2Active not recruitingBioMarin Pharmaceutical302024-11-222026-09-23
Vosoritide for Selected Genetic Causes of Short Stature
Vosoritide - Short Stature
Phase 2Active not recruitingAndrew Dauber562020-08-042026-03-18
Efficacy of Amicar for Children Having Craniofacial Surgery
Amicar (ε-aminocaproic acid), normal saline - Craniosynostosis
Phase 2Active not recruitingChildren's National Research Institute222014-10-012026-04-07

Narrower conditions

Dwarfism (2)  ·  Noonan Syndrome (2)  ·  Bone Diseases (1)  ·  Craniosynostoses (1)  ·  Hypochondroplasia (1)  ·  Musculoskeletal Diseases (1)

Broader conditions

Bone Diseases, Developmental (3)  ·  Congenital Abnormalities (3)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Musculoskeletal Abnormalities (3)  ·  Bone Diseases (2)  ·  Cardiovascular Abnormalities (2)  ·  Cardiovascular Diseases (2)  ·  Connective Tissue Diseases (2)  ·  Endocrine System Diseases (2)  ·  Genetic Diseases, Inborn (2)  ·  Heart Defects, Congenital (2)  ·  Heart Diseases (2)  ·  Musculoskeletal Diseases (2)  ·  Skin and Connective Tissue Diseases (2)

Interventions

vosoritide (2)  ·  Aminocaproic Acid (1)  ·  Saline Solution (1)

Sponsors

Andrew Dauber (1)  ·  BioMarin Pharmaceutical (1)  ·  Children's National Research Institute (1)

Countries

United States (3)  ·  Australia (1)  ·  Canada (1)  ·  France (1)  ·  Germany (1)  ·  Italy (1)  ·  Spain (1)

Top investigators

Andrew Dauber, MS MMSc (1)  ·  Srijaya K Reddy, MD, MBA (1)

Results publications

PMID 38813446