3 recruiting, 1 active not recruiting. 2 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Recruiting 2 |
| Phase 3 | 1 | Recruiting 1 |
Follow Muscular Dystrophy in Children: new trials by email Literature Review of Muscular Dystrophy in Children trials Research Report on Muscular Dystrophy in Children
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients VM100 Nutritional Supplement - Duchenne Muscular Dystrophy, Duchenne Disease | Phase 2 | Recruiting | University of Florida | 20 | 2026-07-27 | 2026-10-08 |
| Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO) Zeleciment Rostudirsen (DYNE-251), Placebo - Duchenne Muscular Dystrophy (DMD), Muscular Dystrophy, Duchenne | Phase 3 | Recruiting | Dyne Therapeutics | 90 | 2026-06-01 | 2026-05-27 |
| Vasodilator and Exercise Study for DMD (VASO-REx) Tadalafil, Placebo, Exercise Training - Duchenne Muscular Dystrophy, Duchenne Disease | Phase 2 | Recruiting | University of Florida | 50 | 2024-06-05 | 2026-05-15 |
| Defining Endpoints in Becker Muscular Dystrophy Becker Muscular Dystrophy, Muscular Dystrophies | Active not recruiting | Virginia Commonwealth University | 80 | 2022-04-13 | 2026-09-03 |
Muscular Dystrophies (4) · Muscular Dystrophy, Duchenne (4) · Tabes Dorsalis (2) · Aneurysm (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Fatigue (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Motor Activity (1) · Myotonic Dystrophy (1) · Neuromuscular Diseases (1)
Muscular Diseases (4) · Muscular Disorders, Atrophic (4) · Musculoskeletal Diseases (4) · Nervous System Diseases (4) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Genetic Diseases, Inborn (3) · Genetic Diseases, X-Linked (3) · Neuromuscular Diseases (3) · Bacterial Infections (2) · Bacterial Infections and Mycoses (2) · Central Nervous System Bacterial Infections (2) · Central Nervous System Diseases (2) · Central Nervous System Infections (2) · Gram-Negative Bacterial Infections (2) · Infections (2)
University of Florida (2) · Dyne Therapeutics (1) · Virginia Commonwealth University (1)
United States (4) · New Zealand (1) · United Kingdom (1)
Nicholas E. Johnson, MD (1) · Tanja Taivassalo, MD (1) · Tanja Taivassalo, Ph.D. (1)
2025 (1), R21AR079755 (1)