Muscular Dystrophy, Duchenne: Clinical Trials

85 trials for Muscular Dystrophy, Duchenne, newest first

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44 completed, 15 unknown, 8 recruiting, 7 not yet recruiting. 85 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable85Completed 44, Unknown 15, Recruiting 8, Not yet recruiting 7, Enrolling by invitation 5, Active not recruiting 2, Terminated 2, Withdrawn 2

Follow Muscular Dystrophy, Duchenne: new trials by email Literature Review of Muscular Dystrophy, Duchenne trials Research Report on Muscular Dystrophy, Duchenne

Trials (filtered) newest first · largest first

All 85 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Urotherapy Education for Families of Children With Duchenne Muscular Dystrophy
Urotherapy Education - Duchenne Muscular Dystrophy (DMD), Lower Urinary Tract Symptoms (LUTS)
Not applicableNot yet recruitingLokman Hekim University502026-11-012026-09-15
Intermittent vs Alternate Daily Regimen of Prednisolone in Ambulatory Boys With Duchenne Muscular Dystrophy
Alternate-day prednisolone, Intermittent prednisolone - Duchenne Muscular Dystrophy
Not applicableNot yet recruitingMuhammad Aamir Latif402026-09-152026-08-26
Self-Efficacy Enhancement Among Online Support Group of Primary Caregivers of Children With Neuro Muscular Dystrophy
Multicomponent Intervention - Duchenne Muscular Dystrophy (DMD), Spinal Muscular Atrophy (SMA)
Not applicableActive not recruitingAga Khan University342026-08-152026-10-09
Digital Monitoring of Upper Limb Function in Non-Ambulant DMD
Performance of the Upper Limb (PUL) Test, Brook test, Dynamometric measurements of muscle strength - Duchenne Muscular Dystrophy (DMD)
Not applicableNot yet recruitingCentre Hospitalier Universitaire de Liege502026-07-302026-06-23
DMD and Gamified Physiotherapy
Gamified Mobile Physiotherapy Exercise Application, Standard Home Exercise Instructions - Duchenne Muscular Dystrophy (DMD)
Not applicableNot yet recruitingBaşak Çağla Arslan462026-05-082026-01-27
Can External Vagus Nerve Stimulation Reduce Systemic Levels of Inflammatory Mediators in Duchenne Muscular Dystrophy Patients?
Transcutaneous auricular vagus nerve stimulation - Duchenne Muscular Dystrophy (DMD)
Not applicableEnrolling by invitationtaVNS AB202026-04-132026-04-24
A Study to Evaluate the Safety and Tolerability of Rituxan in Duchenne Muscular Dystrophy
Rituxan treatment - Duchenne Muscular Dystrophy (DMD)
Not applicableNot yet recruitingPeking Union Medical College Hospital52026-03-232026-03-16
Urinary Titin Biomarker in DMD
Descending stair walk - Duchenne Muscular Dystrophy (DMD), Becker's Muscular Dystrophy (BMD)
Not applicableRecruitingChildren's Hospital of Philadelphia502026-03-042026-04-08
Evaluation of the Role of miR-1 in the Pathogenesis and as a Biomarker in Muscular Dystrophies and Congenital Myopathies
dosage of blood biomarker miR1 - Duchenne / Becker Muscular Dystrophy, Dystrophia Myotonica 1
Not applicableRecruitingUniversity Hospital, Clermont-Ferrand1042026-02-112026-02-25
The Effect of Dual-tasking Program on Cognitive and Physical Functions and Independence in Activities of Daily Living in Children With Duchenne Muscular Dystrophy: A Single-blind Randomized Controlled Trial
Conventional physiotherapy program, Conventional physiotherapy program + Dual task program - Duchenne Muscular Dystrophy (DMD)
Not applicableEnrolling by invitationLokman Hekim University162026-01-142026-01-27
Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn Screening
MAIJU, Syde, Questionnaires - Spinal Muscular Atrophy (SMA), Duchenne Muscular Dystrophy (DMD)
Not applicableRecruitingCentre Hospitalier Universitaire de Liege1002025-12-012025-12-16
Transition to Adulthood in People With Muscular Dystrophy
VIRTUAL REALITY - Duchenne / Becker Muscular Dystrophy
Not applicableNot yet recruitingIRCCS Eugenio Medea2502025-09-012025-08-03
The Effect of Virtual Reality Applications on Upper Extremity Functions in Patients With Duchenne Muscular Dystrophy
Virtual Reality + Conventional Physiotherapy, Conventional Physiotherapy, Formative Usability Evaluation of the VR Rehabilitation Platform - Duchenne Muscular Dystrophy (DMD), Virtual Reality
Not applicableRecruitingIstanbul University362025-08-152026-05-19
Fear of Falling in Muscular Dystrophy
Motor rehabilitation, Motor Rehabilitation and Cognitive Behavioral Therapy - Fear of Falling, Duchenne Muscular Dystrophy (DMD)
Not applicableRecruitingUniversita di Verona1002025-07-022025-08-19
Gamified Occupational Therapy for Adolescents With Duchenne Muscular Dystrophy
Gamified occupational therapy programme, Classic occupational therapy programme - Duchenne Muscular Dystrophy, Gamification
Not applicableRecruitingBaşak Çağla Arslan202025-05-012026-01-27
Virtual Reality and Whole Body Vibration on Muscle Strength and Balance in Children With DMD
virtual reality, whole body vibration - Duchenne Muscular Dystrophy (DMD)
Not applicableCompletedCairo University502025-04-112026-01-14
Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.
Digital respiratory intervention program - Duchenne Muscular Dystrophy, Becker Muscular Dystrophy
Not applicableEnrolling by invitationUniversity of Malaga122025-02-052025-04-01
Transcriptomic Analysis to Put an End to Misdiagnosis in Patients With Rare Muscle Diseases
ARN extraction from muscle biopsies - Rare Genetic Muscle Diseases, Muscular Dystrophy, Duchenne
Not applicableRecruitingAssistance Publique Hopitaux De Marseille502025-01-232026-10-28
Effects of Lumbopelvic Stabilization-based Physiotherapy and Rehabilitation Training in Duchenne Muscular Dystrophy
Exercise, Urotherapy - Duchenne Muscular Dystrophy (DMD), Lower Urinary Track Symptoms
Not applicableNot yet recruitingLokman Hekim University342024-12-012024-10-16
Nutritional Status and Therapy in DMD Patients
Individualised dietary intervention - Duchenne Muscular Dystrophy (DMD)
Not applicableCompletedAnkara University92024-11-182025-11-21

Showing 20 of 85. Sign in to see all of them.

Narrower conditions

Muscular Dystrophies (10)  ·  Muscular Atrophy, Spinal (8)  ·  Neuromuscular Diseases (5)  ·  Motor Activity (4)  ·  Muscular Dystrophy, Facioscapulohumeral (4)  ·  Cardiomyopathies (3)  ·  Muscular Dystrophies, Limb-Girdle (3)  ·  Myotonia Congenita (3)  ·  Amyotrophic Lateral Sclerosis (2)  ·  Cerebral Palsy (2)  ·  Lower Urinary Tract Symptoms (2)  ·  Myotonic Dystrophy (2)  ·  Psychological Well-Being (2)  ·  Angelman Syndrome (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (85)  ·  Genetic Diseases, Inborn (85)  ·  Genetic Diseases, X-Linked (85)  ·  Muscular Disorders, Atrophic (85)  ·  Musculoskeletal Diseases (85)  ·  Muscular Diseases (84)  ·  Nervous System Diseases (84)  ·  Neuromuscular Diseases (80)  ·  Muscular Dystrophies (75)  ·  Neurodegenerative Diseases (13)  ·  Central Nervous System Diseases (11)  ·  Motor Neuron Disease (9)  ·  Spinal Cord Diseases (9)  ·  Behavior (7)  ·  Nutritional and Metabolic Diseases (6)

Interventions

Telerehabilitation (2)  ·  5-nitro-2-(3-phenylpropylamino)benzoic acid (1)  ·  Acceptance and Commitment Therapy (1)  ·  Adiponectin (1)  ·  Adrenocorticotropic Hormone (1)  ·  Athletic Tape (1)  ·  Blood Sedimentation (1)  ·  Blood Specimen Collection (1)  ·  Breathing Exercises (1)  ·  C-Reactive Protein (1)  ·  Cholesterol (1)  ·  Cognitive Behavioral Therapy (1)  ·  Complement C3 (1)  ·  Complement C4 (1)  ·  Contrast Media (1)

Sponsors

Hacettepe University (7)  ·  Lokman Hekim University (5)  ·  Centre Hospitalier Universitaire de Liege (3)  ·  Assistance Publique - Hôpitaux de Paris (2)  ·  Başak Çağla Arslan (2)  ·  Cairo University (2)  ·  IRCCS Eugenio Medea (2)  ·  Nationwide Children's Hospital (2)  ·  Seoul National University Hospital (2)  ·  University Hospital, Montpellier (2)  ·  University of Florida (2)  ·  University of Malaga (2)  ·  University of Sao Paulo (2)  ·  AbiliTech Medical Inc. (1)  ·  Aga Khan University (1)

Countries

Turkey (Türkiye) (21)  ·  United States (13)  ·  France (9)  ·  Egypt (5)  ·  Belgium (4)  ·  Italy (4)  ·  Spain (3)  ·  United Kingdom (3)  ·  Brazil (2)  ·  China (2)  ·  Czechia (2)  ·  Germany (2)  ·  Pakistan (2)  ·  Poland (2)  ·  South Korea (2)

Top investigators

Carlos BM Monteiro, Ph.D. (2)  ·  Numan Bulut, R.A (2)  ·  Aleksandar Radunovic (1)  ·  Alessandra Pedrocchi, Prof (1)  ·  Angela Caldwell, PhD (1)  ·  Anne Wheeler, PhD (1)  ·  Benjamin Kozyak, MD (1)

Results publications

PMID 34779542, PMID 11751186, PMID 15302625, PMID 16055882, PMID 17136445, PMID 17385269, PMID 17711917, PMID 21921156, PMID 22224768, PMID 22463839, PMID 22496194, PMID 22665702, PMID 23447789, PMID 24459612, PMID 25196721, PMID 25554404, PMID 26608622, PMID 28219442, PMID 28397169, PMID 28971520, PMID 28987470, PMID 29395989, PMID 29395990, PMID 30287669, PMID 30420291, PMID 30761066, PMID 31792454, PMID 33407580, PMID 33724264, PMID 34905152, PMID 35192788, PMID 37672897, PMID 37990809, PMID 38018736, PMID 38089167, PMID 38427368, PMID 38685111, PMID 3894415, PMID 39063545, PMID 39648851, PMID 41071520, PMID 41620441, PMID 41926354, PMID 42530145

NIH funding

2025 (1), R01HL131975 (1), R21AR064949 (1), U01NS134672 (1)