Muscular Dystrophy, Becker: Clinical Trials

5 trials for Muscular Dystrophy, Becker, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 recruiting, 1 active not recruiting, 1 completed, 1 not yet recruiting. 2 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable2Completed 1, Recruiting 1

Follow Muscular Dystrophy, Becker: new trials by email Literature Review of Muscular Dystrophy, Becker trials Research Report on Muscular Dystrophy, Becker

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese Children
No interventions are applied; participants are followed for natural history observation only - Muscular Dystrophy, Becker, Muscular Dystrophy
Not yet recruitingWest China Second University Hospital5002026-04-202026-04-06
Transcriptomic Analysis to Put an End to Misdiagnosis in Patients With Rare Muscle Diseases
ARN extraction from muscle biopsies - Rare Genetic Muscle Diseases, Muscular Dystrophy, Duchenne
Not applicableRecruitingAssistance Publique Hopitaux De Marseille502025-03-012025-02-18
Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
Blood sample - Invasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, Including, Sickle Cell Disease
RecruitingAssistance Publique - Hôpitaux de Paris5502024-10-232026-10-21
Defining Endpoints in Becker Muscular Dystrophy
Becker Muscular Dystrophy, Muscular Dystrophies
Active not recruitingVirginia Commonwealth University802022-04-132026-09-03
User-centred Assistive System for Arm Functions in Neuromuscular Subjects
Assistive device (Armon Ayura) test, Assistive device (Jaeco Wrex) test - Muscular Dystrophies, Muscular Dystrophy, Duchenne
Not applicableCompletedPolitecnico di Milano382017-06-162019-12-10

Narrower conditions

Muscular Dystrophy, Duchenne (5)  ·  Muscular Dystrophies (3)  ·  Anemia, Sickle Cell (1)  ·  Cystic Fibrosis (1)  ·  Fragile X Syndrome (1)  ·  Glycogen Storage Disease Type II (1)  ·  Hemophilia A (1)  ·  Hemophilia B (1)  ·  Huntington Disease (1)  ·  Hydrocephalus, X-linked (1)  ·  Limb-girdle muscular dystrophy type 2A (1)  ·  Myotonia Congenita (1)  ·  Myotonic Dystrophy (1)  ·  Neurofibromatoses (1)  ·  Neurofibromatosis-Noonan syndrome (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5)  ·  Genetic Diseases, Inborn (5)  ·  Genetic Diseases, X-Linked (5)  ·  Muscular Diseases (5)  ·  Muscular Disorders, Atrophic (5)  ·  Musculoskeletal Diseases (5)  ·  Nervous System Diseases (5)  ·  Neuromuscular Diseases (5)  ·  Brain Diseases (2)  ·  Central Nervous System Diseases (2)  ·  Heredodegenerative Disorders, Nervous System (2)  ·  Muscular Dystrophies (2)  ·  Myotonic Disorders (2)  ·  Neurodegenerative Diseases (2)  ·  Abnormalities, Multiple (1)

Interventions

Blood Specimen Collection (1)  ·  Self-Help Devices (1)

Sponsors

Assistance Publique - Hôpitaux de Paris (1)  ·  Assistance Publique Hopitaux De Marseille (1)  ·  Politecnico di Milano (1)  ·  Virginia Commonwealth University (1)  ·  West China Second University Hospital (1)

Countries

France (2)  ·  China (1)  ·  Italy (1)  ·  New Zealand (1)  ·  United Kingdom (1)  ·  United States (1)

Top investigators

Alessandra Pedrocchi, Prof (1)  ·  Nicholas E. Johnson, MD (1)

Results publications

PMID 33407580, PMID 37591308