3 completed, 1 enrolling by invitation, 1 unknown, 1 withdrawn. 1 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Completed 1 |
| Phase 3 | 1 | Completed 1 |
Follow Miyoshi myopathy: new trials by email Literature Review of Miyoshi myopathy trials Research Report on Miyoshi myopathy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Clinical, Immunological, Morphological and Genetic Characteristics of Patients With Dysferlinopathy (LGMD R2) in the RF Dysferlinopathy, Miyoshi Myopathy | Enrolling by invitation | Artgen Biotech | 100 | 2020-01-15 | 2025-06-27 | |
| Clinical Outcome Study for Dysferlinopathy Dysferlinopathy, LGMD2B Now Classified as LGMDR2 | Unknown | Newcastle-upon-Tyne Hospitals NHS Trust | 200 | 2012-09-01 | 2022-07-26 | |
| Dysferlinopathy Protein in Peripheral Blood Monocytes. Protein analysis - Muscular Dystrophies, Limb-Girdle Muscular Dystrophy Type 2B | Completed | Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau | 149 | 2012-02-01 | 2024-07-18 | |
| Evaluation of Limb-Girdle Muscular Dystrophy Becker Muscular Dystrophy, Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency) | Completed | Cooperative International Neuromuscular Research Group | 60 | 2009-04-01 | 2014-03-07 | |
| Genetic Study of Familial and Sporadic ALS/Motor Neuron Disease, Miyoshi Myopathy and Other Neuromuscular Disorders Amyotrophic Lateral Sclerosis, Frontotemporal Dementia | Withdrawn | University of Massachusetts, Worcester | 2009-01-01 | 2024-09-19 | ||
| Deflazacort in Dysferlinopathies deflazacort, placebo - LGMD2B, Miyoshi Myopathy | Phase 2 / Phase 3 | Completed | Ludwig-Maximilians - University of Munich | 25 | 2003-09-01 | 2015-09-02 |
Muscular Dystrophies (5) · Limb-girdle muscular dystrophy, type 2B (4) · Dysferlinopathy (3) · Amyotrophic Lateral Sclerosis (1) · Amyotrophic lateral sclerosis 1 (1) · Frontotemporal Dementia (1) · Motor Neuron Disease (1) · Muscular Dystrophies, Limb-Girdle (1) · Muscular Dystrophy, Duchenne (1) · Myopathy, Distal, with Anterior Tibial Onset (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5) · Genetic Diseases, Inborn (5) · Muscular Diseases (5) · Muscular Disorders, Atrophic (5) · Musculoskeletal Diseases (5) · Nervous System Diseases (5) · Neuromuscular Diseases (5) · Brain Diseases (1) · Central Nervous System Diseases (1) · Dementia (1) · Frontotemporal Lobar Degeneration (1) · Genetic Diseases, X-Linked (1) · Mental Disorders (1) · Metabolic Diseases (1) · Neurocognitive Disorders (1)
Adrenal Cortex Hormones (1) · deflazacort (1)
Artgen Biotech (1) · Cooperative International Neuromuscular Research Group (1) · Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau (1) · Ludwig-Maximilians - University of Munich (1) · Newcastle-upon-Tyne Hospitals NHS Trust (1) · University of Massachusetts, Worcester (1)
United States (3) · Spain (2) · Chile (1) · Denmark (1) · France (1) · Germany (1) · Italy (1) · Japan (1) · Russia (1) · South Korea (1) · United Kingdom (1)
Carolina Tesi-Rocha, M.D. (1) · Maggie C. Walter, MD (1) · Meredith K James (1) · Robert H Brown Jr., D Phil,MD (1) · Roman Deev, PhD (1) · Susan Sparks, M.D., Ph.D. (1) · Volker Straub (1)
PMID 19251627, PMID 19734901, PMID 20582942, PMID 20685689, PMID 20801717, PMID 21438137, PMID 22801503, PMID 23152587, PMID 23406536, PMID 29378789, PMID 29735511, PMID 30626655, PMID 35047756, PMID 37553796, PMID 38365661, PMID 39973465