Hypomorphic RAG2 Deficiency: Clinical Trials

1 trial for Hypomorphic RAG2 Deficiency, newest first

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1 recruiting. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Recruiting 1

Follow Hypomorphic RAG2 Deficiency: new trials by email Literature Review of Hypomorphic RAG2 Deficiency trials Research Report on Hypomorphic RAG2 Deficiency

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Hematopoietic Stem Cell Transplantation (HSCT) for Common Variable Immunodeficiency (CVID) and Other Autoimmune Manifestations of Primary Immune Regulatory Disorders (PIRD)
Hematopoietic stem cell transplant (HSCT) - Common Variable Immunodeficiency (CVID), Primary Immune Regulatory Disorder
Phase 2RecruitingPaul Szabolcs252026-05-042026-05-15

Narrower conditions

Common Variable Immunodeficiency (1)  ·  DiGeorge Syndrome (1)  ·  Granulomatous Disease, Chronic (1)  ·  Hyper-IgM Immunodeficiency Syndrome (1)  ·  Immune Dysregulation, Polyendocrinopathy, Enteropathy, X-Linked Syndrome (1)  ·  Intestinal Diseases (1)  ·  Severe Combined Immunodeficiency (1)

Broader conditions

22q11 Deletion Syndrome (1)  ·  Abnormalities, Multiple (1)  ·  Blood Protein Disorders (1)  ·  Cardiovascular Abnormalities (1)  ·  Cardiovascular Diseases (1)  ·  Chromosome Disorders (1)  ·  Chronic Disease (1)  ·  Congenital Abnormalities (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Craniofacial Abnormalities (1)  ·  DNA Repair-Deficiency Disorders (1)  ·  Digestive System Diseases (1)  ·  Disease Attributes (1)  ·  Dysgammaglobulinemia (1)  ·  Endocrine System Diseases (1)

Interventions

Stem Cell Transplantation (1)

Sponsors

Paul Szabolcs (1)

Countries

United States (1)

Top investigators

Paul Szabolcs, MD (1)