1 recruiting. 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Recruiting 1 |
Follow Hypomorphic RAG2 Deficiency: new trials by email Literature Review of Hypomorphic RAG2 Deficiency trials Research Report on Hypomorphic RAG2 Deficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Hematopoietic Stem Cell Transplantation (HSCT) for Common Variable Immunodeficiency (CVID) and Other Autoimmune Manifestations of Primary Immune Regulatory Disorders (PIRD) Hematopoietic stem cell transplant (HSCT) - Common Variable Immunodeficiency (CVID), Primary Immune Regulatory Disorder | Phase 2 | Recruiting | Paul Szabolcs | 25 | 2026-05-04 | 2026-05-15 |
Common Variable Immunodeficiency (1) · DiGeorge Syndrome (1) · Granulomatous Disease, Chronic (1) · Hyper-IgM Immunodeficiency Syndrome (1) · Immune Dysregulation, Polyendocrinopathy, Enteropathy, X-Linked Syndrome (1) · Intestinal Diseases (1) · Severe Combined Immunodeficiency (1)
22q11 Deletion Syndrome (1) · Abnormalities, Multiple (1) · Blood Protein Disorders (1) · Cardiovascular Abnormalities (1) · Cardiovascular Diseases (1) · Chromosome Disorders (1) · Chronic Disease (1) · Congenital Abnormalities (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Craniofacial Abnormalities (1) · DNA Repair-Deficiency Disorders (1) · Digestive System Diseases (1) · Disease Attributes (1) · Dysgammaglobulinemia (1) · Endocrine System Diseases (1)
Paul Szabolcs (1)
United States (1)