1 not yet recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Not yet recruiting 1 |
| Phase 2 | 1 | Not yet recruiting 1 |
Follow Hereditary Spastic Paraplegia Type 50: new trials by email Literature Review of Hereditary Spastic Paraplegia Type 50 trials Research Report on Hereditary Spastic Paraplegia Type 50
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47) BFB-101 (AAV9-CBh-AP4B1) - HSP, Hereditary Spastic Paraplegia | Phase 1 / Phase 2 | Not yet recruiting | BlackfinBio Ltd | 5 | 2025-08-01 | 2025-04-28 |
Movement Disorders (1) · Muscle Spasticity (1) · Spastic Paraplegia, Hereditary (1)
Central Nervous System Diseases (1) · Congenital Abnormalities (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Hereditary Sensory and Motor Neuropathy (1) · Heredodegenerative Disorders, Nervous System (1) · Muscle Hypertonia (1) · Muscular Diseases (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Nervous System Malformations (1) · Neurodegenerative Diseases (1) · Neurologic Manifestations (1) · Neuromuscular Diseases (1) · Neuromuscular Manifestations (1)
BlackfinBio Ltd (1)
United States (1)