Gene Mutation: Clinical Trials

4 trials for Gene Mutation, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 unknown, 1 completed, 1 recruiting. 1 Early Phase 1, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Early Phase 11Completed 1
Phase 31Recruiting 1

Follow Gene Mutation: new trials by email Literature Review of Gene Mutation trials Research Report on Gene Mutation

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety and Tolerance of RAG-17 in Amyotrophic Lateral Sclerosis Patients With SOD1 Gene Mutation
RAG-17 - Gene Mutation
Early Phase 1CompletedBeijing Tiantan Hospital62023-05-242025-04-24
Effects of Different Genetic Mutations on Prognosis in sMPLC Adenocarcinoma Patients
KAPA Hyper Prep Kit + Agilent SureSelectQXT - Gene Mutation
UnknownThe First Hospital of Jilin University202019-04-222021-10-14
Omics-based Precision Medicine of Epilepsy
non - Epilepsy Idiopathic, Clinical Disease and/or Syndrome
UnknownFudan University100002017-11-252017-11-30
The Cancer of the Pancreas Screening-5 CAPS5)Study
Secretin, MRI, Tumor marker gene test with CA19-9 - Pancreas Cancer, Peutz-Jeghers Syndrome (PJS)
Phase 3RecruitingJohns Hopkins University90002014-01-062026-10-22

Narrower conditions

Amyotrophic Lateral Sclerosis (1)  ·  Breast Neoplasms (1)  ·  Colorectal Neoplasms, Hereditary Nonpolyposis (1)  ·  Disease (1)  ·  Dysplastic Nevus Syndrome (1)  ·  Hereditary Sensory and Autonomic Neuropathies (1)  ·  Hereditary pancreatitis (1)  ·  Pancreatic Neoplasms (1)  ·  Peutz-Jeghers Syndrome (1)

Broader conditions

Metabolic Diseases (2)  ·  Nervous System Diseases (2)  ·  Neurodegenerative Diseases (2)  ·  Neuromuscular Diseases (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Breast Diseases (1)  ·  Central Nervous System Diseases (1)  ·  Colonic Diseases (1)  ·  Colorectal Neoplasms (1)  ·  Congenital Abnormalities (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  DNA Repair-Deficiency Disorders (1)  ·  Digestive System Diseases (1)  ·  Digestive System Neoplasms (1)  ·  Endocrine Gland Neoplasms (1)

Interventions

CA-19-9 Antigen (1)  ·  Secretin (1)

Sponsors

Beijing Tiantan Hospital (1)  ·  Fudan University (1)  ·  Johns Hopkins University (1)  ·  The First Hospital of Jilin University (1)

Countries

China (3)  ·  United States (1)

Top investigators

Michael Goggins, MD (1)  ·  YiLong Wang (1)

Results publications

PMID 31197699, PMID 31676359, PMID 33161160, PMID 34149034, PMID 42458007

NIH funding

R01CA176828 (1), U01CA210170 (1)