Gene Mutation: Clinical Trials

1 trial for Gene Mutation, newest first

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1 completed. 1 Early Phase 1.

By phase and status

PhaseTrialsStatus
Early Phase 11Completed 1

Follow Gene Mutation: new trials by email Literature Review of Gene Mutation trials Research Report on Gene Mutation

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety and Tolerance of RAG-17 in Amyotrophic Lateral Sclerosis Patients With SOD1 Gene Mutation
RAG-17 - Gene Mutation
Early Phase 1CompletedBeijing Tiantan Hospital62023-05-242025-04-24

Narrower conditions

Amyotrophic Lateral Sclerosis (1)

Broader conditions

Central Nervous System Diseases (1)  ·  Metabolic Diseases (1)  ·  Motor Neuron Disease (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)  ·  Neuromuscular Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Proteostasis Deficiencies (1)  ·  Spinal Cord Diseases (1)  ·  TDP-43 Proteinopathies (1)

Sponsors

Beijing Tiantan Hospital (1)

Countries

China (1)

Top investigators

YiLong Wang (1)

Results publications

PMID 42458007