DMD: Clinical Trials

6 trials for DMD, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

3 active not recruiting, 3 recruiting. 6 Phase 2, 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 26Active not recruiting 3, Recruiting 3
Phase 11Recruiting 1

Follow DMD: new trials by email Literature Review of DMD trials Research Report on DMD

Trials (filtered) newest first · largest first

All 6 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients
VM100 Nutritional Supplement - Duchenne Muscular Dystrophy, Duchenne Disease
Phase 2RecruitingUniversity of Florida202026-07-272026-10-08
Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients
SAT-3247, Placebo - Duchenne Muscular Dystrophy, Duchenne
Phase 2Active not recruitingSatellos Bioscience, Inc.512025-12-082026-10-02
A Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of BBM-D101 in the Treatment of Duchenne Muscular Dystrophy.
Single dose intravenous of BBM-D101 - DMD
Phase 1 / Phase 2RecruitingBelief BioMed (Beijing) Co., Ltd92025-07-312025-12-04
Vasodilator and Exercise Study for DMD (VASO-REx)
Tadalafil, Placebo, Exercise Training - Duchenne Muscular Dystrophy, Duchenne Disease
Phase 2RecruitingUniversity of Florida502024-06-052026-05-15
NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)
NS-089/NCNP-02 - Duchenne Muscular Dystrophy, Exon 44
Phase 2Active not recruitingNS Pharma, Inc.202024-02-222026-09-15
Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 Skipping
AOC 1044 - DMD, Duchenne Muscular Dystrophy
Phase 2Active not recruitingAvidity Biosciences, Inc.392024-01-222026-07-30

Narrower conditions

Muscular Dystrophy, Duchenne (5)  ·  Muscular Dystrophies (3)  ·  Tabes Dorsalis (2)  ·  Aneurysm (1)  ·  Fatigue (1)  ·  Motor Activity (1)  ·  Neuromuscular Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5)  ·  Genetic Diseases, Inborn (5)  ·  Genetic Diseases, X-Linked (5)  ·  Muscular Diseases (5)  ·  Muscular Disorders, Atrophic (5)  ·  Musculoskeletal Diseases (5)  ·  Nervous System Diseases (5)  ·  Neuromuscular Diseases (4)  ·  Bacterial Infections (2)  ·  Bacterial Infections and Mycoses (2)  ·  Central Nervous System Bacterial Infections (2)  ·  Central Nervous System Diseases (2)  ·  Central Nervous System Infections (2)  ·  Gram-Negative Bacterial Infections (2)  ·  Infections (2)

Interventions

Exercise (1)  ·  Tadalafil (1)

Sponsors

University of Florida (2)  ·  Avidity Biosciences, Inc. (1)  ·  Belief BioMed (Beijing) Co., Ltd (1)  ·  NS Pharma, Inc. (1)  ·  Satellos Bioscience, Inc. (1)

Countries

United States (5)  ·  Australia (2)  ·  Canada (2)  ·  Belgium (1)  ·  China (1)  ·  Japan (1)  ·  New Zealand (1)  ·  Poland (1)  ·  Serbia (1)  ·  South Korea (1)  ·  Spain (1)  ·  Turkey (Türkiye) (1)  ·  United Kingdom (1)

Top investigators

Carmen Castrillo, MD (1)  ·  Tanja Taivassalo, MD (1)  ·  Tanja Taivassalo, Ph.D. (1)  ·  Yi Dai, MD (1)

NIH funding

2025 (1), R21AR079755 (1)