3 completed, 3 recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
| Phase 2 | 1 | Completed 1 |
Follow CMT: new trials by email Literature Review of CMT trials Research Report on CMT
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Multi-omic Approach to the Identification of Novel Biomarkers in Early Charcot-Marie-Tooth 1A Disease (CMT1A) CMT, CMT (Charcot Marie Tooth Disease) | Recruiting | University Medical Center Goettingen | 70 | 2025-03-24 | 2026-04-13 | |
| TREMOR IN CHARCOT-MARIE-TOOTH CMT, CMT (Charcot Marie Tooth Disease) | Recruiting | University Medical Center Goettingen | 75 | 2024-07-30 | 2026-05-06 | |
| The Safety and Tolerability of Engensis (VM202) in Patients With Charcot-Marie-Tooth Disease Subtype 1A (CMT1A) Engensis (VM202) - CMT | Phase 1 / Phase 2 | Completed | Helixmith Co., Ltd. | 12 | 2020-09-21 | 2025-10-06 |
| Analysis of Pain and Quality of Life in Patients With Charcot-Marie-Tooth Neuropathy (CMT) CMT | Completed | University Medical Center Goettingen | 200 | 2019-06-03 | 2020-11-05 | |
| LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies Leukodystrophy, White Matter Disease | Completed | Children's Hospital of Philadelphia | 236 | 2017-01-06 | 2025-11-10 | |
| The Myelin Disorders Biorepository Project Leukodystrophy, White Matter Disease | Recruiting | Children's Hospital of Philadelphia | 12000 | 2016-12-08 | 2025-10-23 |
Charcot-Marie-Tooth Disease (4) · Adrenoleukodystrophy (2) · Aicardi-Goutieres syndrome (2) · Alexander Disease (2) · Alexanders leukodystrophy (2) · Allan-Herndon-Dudley syndrome (2) · Attention Deficit Disorder with Hyperactivity (2) · CADASIL (2) · Canavan Disease (2) · Cockayne Syndrome (2) · Gangliosidoses (2) · Gangliosidoses, GM2 (2) · Leukodystrophy, Globoid Cell (2) · Leukodystrophy, Hypomyelinating, 5 (2) · Leukodystrophy, Hypomyelinating, 6 (2)
Congenital Abnormalities (4) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4) · Genetic Diseases, Inborn (4) · Hereditary Sensory and Motor Neuropathy (4) · Heredodegenerative Disorders, Nervous System (4) · Nervous System Diseases (4) · Nervous System Malformations (4) · Neurodegenerative Diseases (4) · Neuromuscular Diseases (4) · Peripheral Nervous System Diseases (4) · Polyneuropathies (4) · Abnormalities, Multiple (2) · Adrenal Gland Diseases (2) · Adrenal Insufficiency (2) · Arthritis (2)
University Medical Center Goettingen (3) · Children's Hospital of Philadelphia (2) · Helixmith Co., Ltd. (1)
Germany (3) · United States (2) · South Korea (1)
Adeline Vanderver, MD (2) · Michael W Sereda (1)
PMID 32342562, PMID 32749716, PMID 41787447
U01NS106845 (1), U54NS115052 (1)