2 completed. 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Completed 2 |
Follow Citrullinemia: new trials by email Literature Review of Citrullinemia trials Research Report on Citrullinemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Human Heterologous Liver Cells for Infusion in Children With Urea Cycle Disorders Human Heterologous Liver Cells - Urea Cycle Disorders, Carbamoylphosphate Synthetase I Deficiency | Phase 2 | Completed | Cytonet GmbH & Co. KG | 12 | 2008-07-01 | 2016-02-08 |
| Pilot Study For Hypothermia Treatment In Hyperammonemic Encephalopathy In Neonates And Very Young Infants Therapeutic Hypothermia, Standard of Care Therapy - Urea Cycle Disorders, Organic Acidemias | Phase 2 | Completed | Uta Lichter-Konecki | 5 | 2007-08-01 | 2015-06-01 |
Ornithine Carbamoyltransferase Deficiency Disease (2) · Urea Cycle Disorders, Inborn (2) · Argininosuccinic Aciduria (1) · Brain Diseases (1) · Brain Edema (1) · Carbamoyl-Phosphate Synthase I Deficiency Disease (1) · Coma (1) · Hyperammonemia (1) · Lethargy (1) · Methylmalonic acidemia (1) · Propionic Acidemia (1) · Seizures (1)
Amino Acid Metabolism, Inborn Errors (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Central Nervous System Diseases (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Genetic Diseases, X-Linked (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Nervous System Diseases (2) · Nutritional and Metabolic Diseases (2) · Brain Diseases (1) · Consciousness Disorders (1) · Mitochondrial Diseases (1) · Neurobehavioral Manifestations (1)
Continuous Renal Replacement Therapy (1) · Cool-Down Exercise (1) · Cryotherapy (1) · Dialysis (1) · Hypothermia, Induced (1) · Renal Dialysis (1)
Cytonet GmbH & Co. KG (1) · Uta Lichter-Konecki (1)
Germany (1) · United States (1)
Georg Hoffmann, Prof. (1) · Uta Lichter-Konecki, MD, PhD (1)