Citrullinemia: Clinical Trials

2 trials for Citrullinemia, newest first

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2 completed. 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 22Completed 2

Follow Citrullinemia: new trials by email Literature Review of Citrullinemia trials Research Report on Citrullinemia

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Human Heterologous Liver Cells for Infusion in Children With Urea Cycle Disorders
Human Heterologous Liver Cells - Urea Cycle Disorders, Carbamoylphosphate Synthetase I Deficiency
Phase 2CompletedCytonet GmbH & Co. KG122008-07-012016-02-08
Pilot Study For Hypothermia Treatment In Hyperammonemic Encephalopathy In Neonates And Very Young Infants
Therapeutic Hypothermia, Standard of Care Therapy - Urea Cycle Disorders, Organic Acidemias
Phase 2CompletedUta Lichter-Konecki52007-08-012015-06-01

Narrower conditions

Ornithine Carbamoyltransferase Deficiency Disease (2)  ·  Urea Cycle Disorders, Inborn (2)  ·  Argininosuccinic Aciduria (1)  ·  Brain Diseases (1)  ·  Brain Edema (1)  ·  Carbamoyl-Phosphate Synthase I Deficiency Disease (1)  ·  Coma (1)  ·  Hyperammonemia (1)  ·  Lethargy (1)  ·  Methylmalonic acidemia (1)  ·  Propionic Acidemia (1)  ·  Seizures (1)

Broader conditions

Amino Acid Metabolism, Inborn Errors (2)  ·  Brain Diseases, Metabolic (2)  ·  Brain Diseases, Metabolic, Inborn (2)  ·  Central Nervous System Diseases (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Genetic Diseases, X-Linked (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)  ·  Nervous System Diseases (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Brain Diseases (1)  ·  Consciousness Disorders (1)  ·  Mitochondrial Diseases (1)  ·  Neurobehavioral Manifestations (1)

Interventions

Continuous Renal Replacement Therapy (1)  ·  Cool-Down Exercise (1)  ·  Cryotherapy (1)  ·  Dialysis (1)  ·  Hypothermia, Induced (1)  ·  Renal Dialysis (1)

Sponsors

Cytonet GmbH & Co. KG (1)  ·  Uta Lichter-Konecki (1)

Countries

Germany (1)  ·  United States (1)

Top investigators

Georg Hoffmann, Prof. (1)  ·  Uta Lichter-Konecki, MD, PhD (1)