Blood Coagulation Disorders: Clinical Trials

21 trials for Blood Coagulation Disorders, newest first

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21 active not recruiting. 21 Phase 2, 7 Phase 1, 2 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 221Active not recruiting 21
Phase 17Active not recruiting 7
Phase 32Active not recruiting 2

Follow Blood Coagulation Disorders: new trials by email Literature Review of Blood Coagulation Disorders trials Research Report on Blood Coagulation Disorders

Trials (filtered) newest first · largest first

All 21 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Fecal Microbiota Transplantation for Steroid-resistant or Relapsed Immune Thrombocytopenia
Fecal microbiota transplantation - Immune Thrombocytopenia (ITP)
Phase 2Active not recruitingPeking University People's Hospital422026-01-102026-07-29
Real-World Joint Outcomes After Selective Transition to Low-Dose Emicizumab in Pediatric Hemophilia A
Switching to low dose emicizumab - Hemophilia A Patient
Phase 2 / Phase 3Active not recruitingChulalongkorn University182025-06-012026-02-27
Study of CM313 (SC) Injection in Subjects With Primary Immune Thrombocytopenia (ITP)
CM313 injection, placebo - Primary Immune Thrombocytopenia
Phase 2Active not recruitingKeymed Biosciences Co.Ltd622024-11-112025-04-23
A Randomized, Double-blind, Placebo-controlled, and Multi-center Clinical Study of CM313 in the Treatment of Immune Thrombocytopenia
CM313 Injection, Placebo Injection - Immune Thrombocytopenia, Treatment
Phase 2Active not recruitingInstitute of Hematology & Blood Diseases Hospital, China452024-01-162024-12-30
A Study of Ianalumab (VAY736) in Patients With Primary Immune Thrombocytopenia (ITP) Previously Treated With at Least Two Lines of Therapies
Ianalumab - Primary Immune Thrombocytopenia (ITP)
Phase 2Active not recruitingNovartis Pharmaceuticals412023-08-162026-10-20
A Trial of the Safety and Efficacy of Single-Dose Administration of ANB-010 in Subjects With Hemophilia A
ANB-010, dose 1, ANB-010, dose 2, ANB-010, dose 3 - Hemophilia A
Phase 1 / Phase 2Active not recruitingBiocad502023-07-262025-04-24
To Evaluate the Safety and Efficacy of GS1191-0445 Injection in the Treatment of Severe Hemophilia A
GS1191-0445 injection - Severe Hemophilia A
Phase 1 / Phase 2Active not recruitingGritgen Therapeutics Co., Ltd.72023-07-102026-05-06
A Phase 1/2 Study to Investigate Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of HMB-001 in Glanzmann Thrombasthenia
HMB-001 - Glanzmann Thrombasthenia
Phase 1 / Phase 2Active not recruitingHemab ApS572022-12-132026-09-25
A Single-arm, Multicenter Study to Assess the Efficacy, Safety, and Tolerability of P1101 in Adults With ET
Ropeginterferon alfa-2b-njft (P1101) - Essential Thrombocythemia
Phase 2Active not recruitingPharmaEssentia912022-09-292025-08-13
Evaluation of the Safety and Efficacy of Hemophilia B Gene Therapy Drug
Single dose intravenous injection of BBM-H901 - Hemophilia B
Phase 2 / Phase 3Active not recruitingShanghai Xinzhi BioMed Co., Ltd.322021-12-302026-04-01
A Multicenter Randomized Open-label Study of Diammonium Glycyrrhizinate Enteric-coated Capsule Plus DXM Versus DXM in Treatment of ITP
dexamethasone, diammonium glycyrrhizinate enteric-coated capsule - Immune Thrombocytopenia
Phase 2Active not recruitingShandong University1062021-08-212026-01-26
IMG-7289 in Patients With Essential Thrombocythemia (ET) or Polycythemia Vera (PV)
IMG-7289 - Essential Thrombocythemia, Polycythemia Vera
Phase 2Active not recruitingTerrence J Bradley, MD42020-10-022026-01-07
Hematology, IMG-7289, LSD1 (Lysine-Specific Demethylase 1) Inhibitor, Essential Thrombocythemia (ET), Ph 2
IMG-7289 - Thrombocythemia, Essential
Phase 2Active not recruitingThe University of Texas Health Science Center at San Antonio92020-04-092026-10-22
Azacitidine, Venetoclax, and Pevonedistat in Treating Patients With Newly Diagnosed Acute Myeloid Leukemia
Azacitidine, Pevonedistat, Venetoclax - Acute Myeloid Leukemia, Atypical Chronic Myeloid Leukemia, BCR-ABL1 Negative
Phase 1 / Phase 2Active not recruitingM.D. Anderson Cancer Center402019-02-272026-07-16
Topotecan Hydrochloride and Carboplatin With or Without Veliparib in Treating Advanced Myeloproliferative Disorders and Acute Myeloid Leukemia or Chronic Myelomonocytic Leukemia
Carboplatin, Topotecan, Topotecan Hydrochloride - Acute Myeloid Leukemia, Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome
Phase 2Active not recruitingNational Cancer Institute (NCI)252018-09-242026-06-23
Gene Therapy for Haemophilia A.
AAV2/8-HLP-FVIII-V3 - Hemophilia A
Phase 1 / Phase 2Active not recruitingUniversity College, London142017-06-142025-03-05
The Ruxo-BEAT Trial in Patients With High-risk Polycythemia Vera or High-risk Essential Thrombocythemia
Ruxolitinib, BAT - Polycythemia Vera (PV), Essential Thrombocythemia (ET)
Phase 2Active not recruitingRWTH Aachen University2072015-10-012026-08-13
Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome
Autologous CD34+ cells transduced with WASP lentiviral vector - Wiskott-Aldrich Syndrome
Phase 1 / Phase 2Active not recruitingGenethon102014-09-012021-06-03
Long-term Study Evaluating the Effect of Givinostat in Patients With Chronic Myeloproliferative Neoplasms
givinostat - Chronic Myeloproliferative Neoplasms
Phase 2Active not recruitingItalfarmaco902013-03-012025-04-30
Open-Label Single Ascending Dose of Adeno-associated Virus Serotype 8 Factor IX Gene Therapy in Adults With Hemophilia B
AskBio009 - Hemophilia B
Phase 1 / Phase 2Active not recruitingBaxalta now part of Shire302013-02-112026-03-20

Showing 20 of 21. Sign in to see all of them.

Narrower conditions

Thrombocythemia, Essential (8)  ·  Polycythemia Vera (6)  ·  Purpura, Thrombocytopenic, Idiopathic (5)  ·  Hemophilia A (4)  ·  Myeloproliferative Disorders (4)  ·  Primary Myelofibrosis (4)  ·  Leukemia, Myeloid, Acute (3)  ·  Leukemia, Myeloid, Chronic, Atypical, BCR-ABL Negative (3)  ·  Leukemia, Myelomonocytic, Chronic (3)  ·  Hemophilia B (2)  ·  Leukemia, Neutrophilic, Chronic (2)  ·  Myelodysplastic Syndromes (2)  ·  Myelodysplastic-Myeloproliferative Diseases (2)  ·  Thrombocytosis (2)  ·  Anemia, Aplastic (1)

Broader conditions

Hematologic Diseases (21)  ·  Hemic and Lymphatic Diseases (21)  ·  Hemorrhagic Disorders (21)  ·  Blood Platelet Disorders (14)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (9)  ·  Pathologic Processes (9)  ·  Pathological Conditions, Signs and Symptoms (9)  ·  Blood Coagulation Disorders, Inherited (8)  ·  Bone Marrow Diseases (8)  ·  Genetic Diseases, Inborn (8)  ·  Immune System Diseases (7)  ·  Bone Marrow Neoplasms (6)  ·  Coagulation Protein Disorders (6)  ·  Cytopenia (6)

Interventions

bomedemstat (2)  ·  Azacitidine (1)  ·  BAX 335 (1)  ·  Busulfan (1)  ·  Carboplatin (1)  ·  Cyclophosphamide (1)  ·  Cyclosporine (1)  ·  Dexamethasone (1)  ·  Drug Evaluation (1)  ·  Etoposide (1)  ·  Fecal Microbiota Transplantation (1)  ·  Melphalan (1)  ·  Methotrexate (1)  ·  Mycophenolic Acid (1)  ·  Peripheral Blood Stem Cell Transplantation (1)

Sponsors

Baxalta now part of Shire (1)  ·  Biocad (1)  ·  Chulalongkorn University (1)  ·  City of Hope Medical Center (1)  ·  Genethon (1)  ·  Gritgen Therapeutics Co., Ltd. (1)  ·  Hemab ApS (1)  ·  Institute of Hematology & Blood Diseases Hospital, China (1)  ·  Italfarmaco (1)  ·  Keymed Biosciences Co.Ltd (1)  ·  M.D. Anderson Cancer Center (1)  ·  National Cancer Institute (NCI) (1)  ·  Novartis Pharmaceuticals (1)  ·  Peking University People's Hospital (1)  ·  PharmaEssentia (1)

Countries

United States (9)  ·  China (7)  ·  United Kingdom (5)  ·  France (3)  ·  Germany (3)  ·  Italy (3)  ·  Argentina (1)  ·  Australia (1)  ·  Belgium (1)  ·  Canada (1)  ·  Malaysia (1)  ·  Netherlands (1)  ·  Poland (1)  ·  Russia (1)  ·  South Korea (1)

Top investigators

Lei Zhang, MD (2)  ·  Alessandro Rambaldi, MD (1)  ·  Arina V Zinkina-Orikhan, PhD (1)  ·  Auayporn P. Nademanee, MD (1)  ·  Caifeng Yang, Master (1)  ·  Keith W Pratz (1)  ·  Lei Zhang (1)  ·  Ming Hou, MD,PhD (1)  ·  Nicholas Short (1)  ·  Oleh Zagrijtschuk, MD, PhD (1)  ·  Pratima Chowdary, MD (1)  ·  Steffen Koschmieder, Prof. Dr. (1)  ·  Terrence J Bradley, MD (1)

Results publications

PMID 30003118, PMID 33067633, PMID 33609248, PMID 35075289, PMID 36564535, PMID 37422688, PMID 37592092, PMID 40330782, PMID 40441148, PMID 41120215, PMID 41180128, PMID 41266685, PMID 42178778, PMID 42306077

NIH funding

2016 (1), P30CA033572 (1), UM1CA186691 (1)