2 enrolling by invitation. 2 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Enrolling by invitation 2 |
| Phase 2 | 1 | Enrolling by invitation 1 |
Follow Blood Coagulation Disorders: new trials by email Literature Review of Blood Coagulation Disorders trials Research Report on Blood Coagulation Disorders
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Phase 1b Long-term Extension Trial of RAY121 in Immunological Diseases (RAINBOW-LTE Trial) RAY121 - Antiphospholipid Syndrome (APS), Bullous Pemphigoid (BP) | Phase 1 | Enrolling by invitation | Chugai Pharmaceutical | 144 | 2024-12-09 | 2026-07-17 |
| Sequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency Diseases CD3/CD19 negative allogeneic hematopoietic stem cells - Severe Combined Immunodeficiency (SCID), Immunodeficiency With Predominant T-cell Defect, Unspecified | Phase 1 / Phase 2 | Enrolling by invitation | Paul Szabolcs | 16 | 2013-06-20 | 2025-12-15 |
Antiphospholipid Syndrome (1) · Behcet Syndrome (1) · Common Variable Immunodeficiency (1) · Dermatomyositis (1) · Granulomatous Disease, Chronic (1) · Job Syndrome (1) · Neutropenia, severe chronic (1) · Pemphigoid, Bullous (1) · Purpura, Thrombocytopenic, Idiopathic (1) · Severe Combined Immunodeficiency (1) · Wiskott-Aldrich Syndrome (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Cytopenia (2) · Genetic Diseases, Inborn (2) · Hematologic Diseases (2) · Hemic and Lymphatic Diseases (2) · Hemorrhagic Disorders (2) · Immune System Diseases (2) · Pathologic Processes (2) · Pathological Conditions, Signs and Symptoms (2) · Autoimmune Diseases (1) · Blood Coagulation Disorders, Inherited (1) · Blood Platelet Disorders (1) · Cardiovascular Diseases (1) · Chronic Disease (1)
Chugai Pharmaceutical (1) · Paul Szabolcs (1)
Australia (1) · Austria (1) · Bulgaria (1) · Canada (1) · Croatia (1) · Czechia (1) · France (1) · Germany (1) · Hungary (1) · Italy (1) · Japan (1) · Netherlands (1) · Norway (1) · Poland (1) · Portugal (1)