Neutropenia, severe chronic: Clinical Trials

6 trials for Neutropenia, severe chronic, newest first

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2 terminated, 1 enrolling by invitation, 1 recruiting, 1 unknown. 3 Phase 2, 2 Phase 1, 1 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 23Enrolling by invitation 1, Terminated 1, Withdrawn 1
Phase 12Enrolling by invitation 1, Withdrawn 1
Phase 41Terminated 1

Follow Neutropenia, severe chronic: new trials by email Literature Review of Neutropenia, severe chronic trials Research Report on Neutropenia, severe chronic

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Shwachman-Diamond Syndrome Global Patient Survey and Partnering Platform
Shwachman-Diamond Syndrome, SDS
RecruitingShwachman-Diamond Syndrome Alliance Inc80002024-02-072025-05-31
ANF-Rho in the Treatment of Chronic Neutropenia
ANF-Rho - Neutropenia, Severe Chronic
Phase 1 / Phase 2WithdrawnProlong Pharmaceuticals2015-10-012019-03-06
Sequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency Diseases
CD3/CD19 negative allogeneic hematopoietic stem cells - Severe Combined Immunodeficiency (SCID), Immunodeficiency With Predominant T-cell Defect, Unspecified
Phase 1 / Phase 2Enrolling by invitationPaul Szabolcs162013-06-202025-12-15
Immunogenicity, Safety, and Efficacy of Zarzio®/Filgrastim HEXAL® in Patients With Severe Chronic Neutropenia
Filgrastim - Severe Chronic Neutropenia
Phase 4TerminatedSandoz62011-07-012016-03-28
Study of Ezatiostat (Telintra Tablets) for Treatment of Severe Chronic Neutropenia
Ezatiostat Hydrochloride - Severe Chronic Neutropenia
Phase 2TerminatedTelik92009-04-012013-11-25
International Registry for Severe Chronic Neutropenia
Neutropenia
UnknownNational Center for Research Resources (NCRR)10001994-06-012020-10-22

Narrower conditions

Neutropenia (2)  ·  Common Variable Immunodeficiency (1)  ·  Congenital Bone Marrow Failure Syndromes (1)  ·  Exocrine Pancreatic Insufficiency (1)  ·  Granulomatous Disease, Chronic (1)  ·  Hematologic Diseases (1)  ·  Immunologic Deficiency Syndromes (1)  ·  Job Syndrome (1)  ·  Lymphoma, Follicular (1)  ·  Myelodysplastic Syndromes (1)  ·  Neoplastic Syndromes, Hereditary (1)  ·  Neutropenia, Severe Congenital, Autosomal Recessive 3 (1)  ·  Pancytopenia (1)  ·  Primary Immunodeficiency Diseases (1)

Broader conditions

Cytopenia (4)  ·  Hemic and Lymphatic Diseases (4)  ·  Hematologic Diseases (3)  ·  Leukocyte Disorders (3)  ·  Leukopenia (3)  ·  Agranulocytosis (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Disease Attributes (2)  ·  Genetic Diseases, Inborn (2)  ·  Immune System Diseases (2)  ·  Infant, Newborn, Diseases (2)  ·  Metabolic Diseases (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Pathologic Processes (2)  ·  Pathological Conditions, Signs and Symptoms (2)

Interventions

Filgrastim (1)  ·  gamma-Glu-S-BzCys-PhGly diethyl ester (1)  ·  pegfilgrastim (1)  ·  pegylated granulocyte colony-stimulating factor (1)

Sponsors

National Center for Research Resources (NCRR) (1)  ·  Paul Szabolcs (1)  ·  Prolong Pharmaceuticals (1)  ·  Sandoz (1)  ·  Shwachman-Diamond Syndrome Alliance Inc (1)  ·  Telik (1)

Countries

United States (4)  ·  Germany (2)  ·  Australia (1)  ·  Canada (1)  ·  Sweden (1)  ·  United Kingdom (1)

Top investigators

David Chandler Dale (1)  ·  Gail Brown, MD (1)  ·  Hemant Misra, PhD (1)  ·  Paul Szabolcs, MD (1)  ·  Roumen Nakov, MD, PhD (1)