AMN Gene Mutation: Clinical Trials

1 trial for AMN Gene Mutation, newest first

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1 terminated. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Terminated 1
Phase 21Terminated 1

Follow AMN Gene Mutation: new trials by email Literature Review of AMN Gene Mutation trials Research Report on AMN Gene Mutation

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Evaluate Administration of SBT101 Gene Therapy in Adult Patients With Adrenomyeloneuropathy (AMN)
SBT101 Treatment - AMN, AMN Gene Mutation
Phase 1 / Phase 2TerminatedSwanBio Therapeutics, Inc.92022-11-172026-08-26

Narrower conditions

Adrenal Insufficiency (1)  ·  Adrenoleukodystrophy (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Demyelinating Diseases (1)  ·  Hereditary Central Nervous System Demyelinating Diseases (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Leukoencephalopathies (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Paraplegia (1)  ·  Peroxisomal Disorders (1)  ·  Spastic Paraplegia, Hereditary (1)

Broader conditions

Adrenal Gland Diseases (1)  ·  Brain Diseases (1)  ·  Central Nervous System Diseases (1)  ·  Congenital Abnormalities (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Endocrine System Diseases (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Hereditary Sensory and Motor Neuropathy (1)  ·  Intellectual Disability (1)  ·  Nervous System Diseases (1)  ·  Nervous System Malformations (1)  ·  Neurobehavioral Manifestations (1)  ·  Neurodegenerative Diseases (1)  ·  Neurologic Manifestations (1)

Sponsors

SwanBio Therapeutics, Inc. (1)

Countries

Netherlands (1)  ·  United States (1)