1 terminated. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Terminated 1 |
| Phase 2 | 1 | Terminated 1 |
Follow AMN Gene Mutation: new trials by email Literature Review of AMN Gene Mutation trials Research Report on AMN Gene Mutation
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Evaluate Administration of SBT101 Gene Therapy in Adult Patients With Adrenomyeloneuropathy (AMN) SBT101 Treatment - AMN, AMN Gene Mutation | Phase 1 / Phase 2 | Terminated | SwanBio Therapeutics, Inc. | 9 | 2022-11-17 | 2026-08-26 |
Adrenal Insufficiency (1) · Adrenoleukodystrophy (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Demyelinating Diseases (1) · Hereditary Central Nervous System Demyelinating Diseases (1) · Heredodegenerative Disorders, Nervous System (1) · Leukoencephalopathies (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Paraplegia (1) · Peroxisomal Disorders (1) · Spastic Paraplegia, Hereditary (1)
Adrenal Gland Diseases (1) · Brain Diseases (1) · Central Nervous System Diseases (1) · Congenital Abnormalities (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Endocrine System Diseases (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Hereditary Sensory and Motor Neuropathy (1) · Intellectual Disability (1) · Nervous System Diseases (1) · Nervous System Malformations (1) · Neurobehavioral Manifestations (1) · Neurodegenerative Diseases (1) · Neurologic Manifestations (1)
SwanBio Therapeutics, Inc. (1)
Netherlands (1) · United States (1)