2 terminated. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Terminated 1 |
| Phase 2 | 1 | Terminated 1 |
Follow AMN Gene Mutation: new trials by email Literature Review of AMN Gene Mutation trials Research Report on AMN Gene Mutation
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Evaluate Administration of SBT101 Gene Therapy in Adult Patients With Adrenomyeloneuropathy (AMN) SBT101 Treatment - AMN, AMN Gene Mutation | Phase 1 / Phase 2 | Terminated | SwanBio Therapeutics, Inc. | 9 | 2022-11-17 | 2026-08-26 |
| Study of Disease Progression in Adults With Inherited Forms of Spastic Paraplegia Natural History Observation - AMN, AMN Gene Mutation | Terminated | SwanBio Therapeutics, Inc. | 65 | 2021-06-21 | 2025-10-30 |
Adrenal Insufficiency (2) · Adrenoleukodystrophy (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Demyelinating Diseases (2) · Hereditary Central Nervous System Demyelinating Diseases (2) · Heredodegenerative Disorders, Nervous System (2) · Leukoencephalopathies (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Paraplegia (2) · Peroxisomal Disorders (2) · Spastic Paraplegia, Hereditary (2)
Adrenal Gland Diseases (2) · Brain Diseases (2) · Central Nervous System Diseases (2) · Congenital Abnormalities (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Endocrine System Diseases (2) · Genetic Diseases, Inborn (2) · Genetic Diseases, X-Linked (2) · Hereditary Sensory and Motor Neuropathy (2) · Intellectual Disability (2) · Nervous System Diseases (2) · Nervous System Malformations (2) · Neurobehavioral Manifestations (2) · Neurodegenerative Diseases (2) · Neurologic Manifestations (2)
SwanBio Therapeutics, Inc. (2)
Netherlands (2) · United States (2) · Germany (1)