AMN Gene Mutation: Clinical Trials

2 trials for AMN Gene Mutation, newest first

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2 terminated. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Terminated 1
Phase 21Terminated 1

Follow AMN Gene Mutation: new trials by email Literature Review of AMN Gene Mutation trials Research Report on AMN Gene Mutation

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Evaluate Administration of SBT101 Gene Therapy in Adult Patients With Adrenomyeloneuropathy (AMN)
SBT101 Treatment - AMN, AMN Gene Mutation
Phase 1 / Phase 2TerminatedSwanBio Therapeutics, Inc.92022-11-172026-08-26
Study of Disease Progression in Adults With Inherited Forms of Spastic Paraplegia
Natural History Observation - AMN, AMN Gene Mutation
TerminatedSwanBio Therapeutics, Inc.652021-06-212025-10-30

Narrower conditions

Adrenal Insufficiency (2)  ·  Adrenoleukodystrophy (2)  ·  Brain Diseases, Metabolic (2)  ·  Brain Diseases, Metabolic, Inborn (2)  ·  Demyelinating Diseases (2)  ·  Hereditary Central Nervous System Demyelinating Diseases (2)  ·  Heredodegenerative Disorders, Nervous System (2)  ·  Leukoencephalopathies (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)  ·  Paraplegia (2)  ·  Peroxisomal Disorders (2)  ·  Spastic Paraplegia, Hereditary (2)

Broader conditions

Adrenal Gland Diseases (2)  ·  Brain Diseases (2)  ·  Central Nervous System Diseases (2)  ·  Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Endocrine System Diseases (2)  ·  Genetic Diseases, Inborn (2)  ·  Genetic Diseases, X-Linked (2)  ·  Hereditary Sensory and Motor Neuropathy (2)  ·  Intellectual Disability (2)  ·  Nervous System Diseases (2)  ·  Nervous System Malformations (2)  ·  Neurobehavioral Manifestations (2)  ·  Neurodegenerative Diseases (2)  ·  Neurologic Manifestations (2)

Sponsors

SwanBio Therapeutics, Inc. (2)

Countries

Netherlands (2)  ·  United States (2)  ·  Germany (1)