Transient Neonatal Diabetes Mellitus: Clinical Trials

2 trials for Transient Neonatal Diabetes Mellitus, newest first

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1 active not recruiting, 1 recruiting. .

Follow Transient Neonatal Diabetes Mellitus: new trials by email Literature Review of Transient Neonatal Diabetes Mellitus trials Research Report on Transient Neonatal Diabetes Mellitus

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Early Check: Expanded Screening in Newborns
Confirmatory Testing - Spinal Muscular Atrophy, Fragile X Syndrome
Active not recruitingRTI International300002018-10-152026-07-01
IDMet (RaDiCo Cohort) (RaDiCo-IDMet)
Silver Russell Syndrome, Beckwith-Wiedemann Syndrome
RecruitingInstitut National de la Santé Et de la Recherche Médicale, France20002017-03-102026-02-12

Narrower conditions

Angelman Syndrome (2)  ·  Prader-Willi Syndrome (2)  ·  3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency (1)  ·  3-Hydroxyacyl-CoA Dehydrogenase Deficiency (1)  ·  3-methylcrotonyl CoA carboxylase 1 deficiency (1)  ·  3-methylcrotonyl CoA carboxylase 2 deficiency (1)  ·  Acidemia, isovaleric (1)  ·  Acrodermatitis enteropathica (1)  ·  Adenine phosphoribosyltransferase deficiency (1)  ·  Adrenal hyperplasia, congenital, type 5 (1)  ·  Adrenocorticotropic hormone deficiency (1)  ·  Amaurosis congenita of Leber, type 2 (1)  ·  Anemia, Sickle Cell (1)  ·  Aortic Stenosis, Supravalvular (1)  ·  Arginine-Glycine Amidinotransferase Deficiency (1)

Broader conditions

Abnormalities, Multiple (2)  ·  Bone Diseases (2)  ·  Bone Diseases, Metabolic (2)  ·  Calcium Metabolism Disorders (2)  ·  Central Nervous System Diseases (2)  ·  Chromosome Disorders (2)  ·  Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Dwarfism (2)  ·  Endocrine System Diseases (2)  ·  Genetic Diseases, Inborn (2)  ·  Imprinting Disorders (2)  ·  Intellectual Disability (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)

Sponsors

Institut National de la Santé Et de la Recherche Médicale, France (1)  ·  RTI International (1)

Countries

France (1)  ·  United States (1)

Top investigators

Curt Scharfe, MD, PhD (1)

Results publications

PMID 31315600, PMID 35142618