3 enrolling by invitation. 3 Phase 2, 2 Phase 1, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 3 | Enrolling by invitation 3 |
| Phase 1 | 2 | Enrolling by invitation 2 |
| Phase 3 | 1 | Enrolling by invitation 1 |
Follow Primary Immunodeficiency Diseases: new trials by email Literature Review of Primary Immunodeficiency Diseases trials Research Report on Primary Immunodeficiency Diseases
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Base-Edited Hematopoietic Stem/Progenitor Cell X-Linked Severe Combined Immunodeficiency Gene Therapy Plerixafor, Filgrastim, Palifermin - X-linked Severe Combined Immunodeficiency, X-SCID | Phase 1 / Phase 2 | Enrolling by invitation | National Institute of Allergy and Infectious Diseases (NIAID) | 18 | 2025-05-09 | 2026-10-13 |
| Extension Study of Oral PHA-022121 for Acute Treatment of Angioedema Attacks in Patients With Hereditary Angioedema deucrictibant - Hereditary Angioedema, Hereditary Angioedema Type I | Phase 2 / Phase 3 | Enrolling by invitation | Pharvaris Netherlands B.V. | 150 | 2022-12-28 | 2026-07-21 |
| Sequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency Diseases CD3/CD19 negative allogeneic hematopoietic stem cells - Severe Combined Immunodeficiency (SCID), Immunodeficiency With Predominant T-cell Defect, Unspecified | Phase 1 / Phase 2 | Enrolling by invitation | Paul Szabolcs | 16 | 2013-06-20 | 2025-12-15 |
Angioedemas, Hereditary (1) · Common Variable Immunodeficiency (1) · Granulomatous Disease, Chronic (1) · Hereditary Angioedema Type III (1) · Hereditary Angioedema Types I and II (1) · Job Syndrome (1) · Neutropenia, severe chronic (1) · Severe Combined Immunodeficiency (1) · Wiskott-Aldrich Syndrome (1) · X-Linked Combined Immunodeficiency Diseases (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Genetic Diseases, Inborn (3) · Immune System Diseases (3) · Immunologic Deficiency Syndromes (3) · Genetic Diseases, X-Linked (2) · Infant, Newborn, Diseases (2) · Angioedema (1) · Blood Coagulation Disorders (1) · Blood Coagulation Disorders, Inherited (1) · Cardiovascular Diseases (1) · Chronic Disease (1) · Cytopenia (1) · DNA Repair-Deficiency Disorders (1) · Disease Attributes (1)
Busulfan (1) · Fibroblast Growth Factor 7 (1) · Filgrastim (1) · plerixafor (1)
National Institute of Allergy and Infectious Diseases (NIAID) (1) · Paul Szabolcs (1) · Pharvaris Netherlands B.V. (1)
United States (3) · Argentina (1) · Australia (1) · Austria (1) · Brazil (1) · Bulgaria (1) · Canada (1) · Czechia (1) · France (1) · Germany (1) · Hong Kong (1) · Hungary (1) · Israel (1) · Italy (1) · Japan (1)
Paul Szabolcs, MD (1) · Suk S De Ravin, M.D. (1)
2023 (1)