MLD: Clinical Trials

4 trials for MLD, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 completed, 2 recruiting. 1 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable1Completed 1

Follow MLD: new trials by email Literature Review of MLD trials Research Report on MLD

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Manual Lymphatic Drainage Before and After Total Knee Replacement, a Single-center Observer-blinded Randomized Controlled Trial
Manual Lymphatic Drainage - Total Knee Arthroplasty, Manual Lymphatic Drainage
Not applicableCompletedMoritz Wagner1122021-03-012023-08-02
LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies
Leukodystrophy, White Matter Disease
CompletedChildren's Hospital of Philadelphia2362017-01-062025-11-10
The Myelin Disorders Biorepository Project
Leukodystrophy, White Matter Disease
RecruitingChildren's Hospital of Philadelphia120002016-12-082025-10-23
Longitudinal Study of Neurodegenerative Disorders
Palliative Care, Hematopoetic Stem Cell Transplantation - MLD, Krabbe Disease
RecruitingUniversity of Pittsburgh15002012-01-112026-02-09

Narrower conditions

Leukodystrophy, Globoid Cell (3)  ·  Leukoencephalopathies (3)  ·  Multiple Sulfatase Deficiency Disease (3)  ·  Pelizaeus-Merzbacher Disease (3)  ·  Adrenoleukodystrophy (2)  ·  Aicardi-Goutieres syndrome (2)  ·  Alexander Disease (2)  ·  Alexanders leukodystrophy (2)  ·  Allan-Herndon-Dudley syndrome (2)  ·  Attention Deficit Disorder with Hyperactivity (2)  ·  CADASIL (2)  ·  Canavan Disease (2)  ·  Charcot-Marie-Tooth Disease (2)  ·  Cockayne Syndrome (2)  ·  Gangliosidoses (2)

Broader conditions

Musculoskeletal Diseases (4)  ·  Arthritis (3)  ·  Bone Diseases (3)  ·  Bone Diseases, Developmental (3)  ·  Brain Diseases (3)  ·  Brain Diseases, Metabolic (3)  ·  Brain Diseases, Metabolic, Inborn (3)  ·  Carbohydrate Metabolism, Inborn Errors (3)  ·  Central Nervous System Diseases (3)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Connective Tissue Diseases (3)  ·  Demyelinating Diseases (3)  ·  Genetic Diseases, Inborn (3)  ·  Genetic Diseases, X-Linked (3)  ·  Hereditary Central Nervous System Demyelinating Diseases (3)

Interventions

Manual Lymphatic Drainage (1)  ·  Palliative Care (1)

Sponsors

Children's Hospital of Philadelphia (2)  ·  Moritz Wagner (1)  ·  University of Pittsburgh (1)

Countries

United States (3)  ·  Austria (1)

Top investigators

Adeline Vanderver, MD (2)

Results publications

PMID 32342562, PMID 32749716

NIH funding

U01NS106845 (1), U54NS115052 (1)