MELAS: Clinical Trials

2 trials for MELAS, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 completed. 2 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Completed 2
Phase 21Completed 1

Follow MELAS: new trials by email Literature Review of MELAS trials Research Report on MELAS

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Promoting Resilience in Stress Management (PRISM) and Clinical-focused Narrative (CFN) Pilot in Adults With Primary Mitochondrial Disease (PMD).
Promoting Resilience in Stress Management (PRISM), Clinical-focused narrative (CFN) - Mitochondrial Diseases, Mitochondrial Myopathies
Phase 1 / Phase 2CompletedChildren's Hospital of Philadelphia162023-09-222024-11-29
A Dose-escalating Clinical Trial With KH176
KH176, placebo - MELAS, LHON
Phase 1CompletedKhondrion BV322015-05-012021-10-18

Narrower conditions

MELAS Syndrome (2)  ·  Mitochondrial Diseases (2)  ·  Leigh Disease (1)  ·  MERRF Syndrome (1)  ·  Mitochondrial Encephalomyopathies (1)  ·  Mitochondrial Myopathies (1)

Broader conditions

Brain Diseases (2)  ·  Brain Diseases, Metabolic (2)  ·  Brain Diseases, Metabolic, Inborn (2)  ·  Cardiovascular Diseases (2)  ·  Central Nervous System Diseases (2)  ·  Cerebral Small Vessel Diseases (2)  ·  Cerebrovascular Disorders (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)  ·  Muscular Diseases (2)  ·  Musculoskeletal Diseases (2)  ·  Nervous System Diseases (2)  ·  Neuromuscular Diseases (2)

Interventions

6-hydroxy-2,5,7,8-tetramethylchroman-2-carboxylic acid (1)

Sponsors

Children's Hospital of Philadelphia (1)  ·  Khondrion BV (1)

Countries

Belgium (1)  ·  United States (1)

Top investigators

Elizabeth M McCormick, MS (1)

Results publications

PMID 29037240

NIH funding

U54NS078059 (1)