Leukocyte Adhesion Deficiency: Clinical Trials

1 trial for Leukocyte Adhesion Deficiency, newest first

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1 completed. 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Bone Marrow Transplant With Abatacept for Non-Malignant Diseases
Abatacept - Hurler Syndrome, Fanconi Anemia
Phase 1CompletedEmory University102014-01-012019-12-26

Narrower conditions

Anemia, Aplastic (1)  ·  Anemia, Diamond-Blackfan (1)  ·  Anemia, Sickle Cell (1)  ·  Chediak-Higashi Syndrome (1)  ·  Dyskeratosis Congenita (1)  ·  Fanconi Anemia (1)  ·  Granulomatous Disease, Chronic (1)  ·  Leukocyte adhesion deficiency type 1 (1)  ·  Lymphohistiocytosis, Hemophagocytic (1)  ·  Mucopolysaccharidosis I (1)  ·  Neutropenia, Severe Congenital, Autosomal Recessive 3 (1)  ·  Shwachman-Diamond Syndrome (1)  ·  Thrombasthenia (1)  ·  Wiskott-Aldrich Syndrome (1)  ·  beta-Thalassemia (1)

Broader conditions

Albinism (1)  ·  Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Anemia, Hypoplastic, Congenital (1)  ·  Blood Coagulation Disorders (1)  ·  Blood Coagulation Disorders, Inherited (1)  ·  Blood Platelet Disorders (1)  ·  Bone Marrow Diseases (1)  ·  Bone Marrow Failure Disorders (1)  ·  Carbohydrate Metabolism, Inborn Errors (1)  ·  Chronic Disease (1)  ·  Congenital Abnormalities (1)  ·  Congenital Bone Marrow Failure Syndromes (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)

Interventions

Abatacept (1)

Sponsors

Emory University (1)

Countries

United States (1)

Top investigators

John T Horan, MD (1)