1 completed. 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
Follow Leukocyte Adhesion Deficiency: new trials by email Literature Review of Leukocyte Adhesion Deficiency trials Research Report on Leukocyte Adhesion Deficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Bone Marrow Transplant With Abatacept for Non-Malignant Diseases Abatacept - Hurler Syndrome, Fanconi Anemia | Phase 1 | Completed | Emory University | 10 | 2014-01-01 | 2019-12-26 |
Anemia, Aplastic (1) · Anemia, Diamond-Blackfan (1) · Anemia, Sickle Cell (1) · Chediak-Higashi Syndrome (1) · Dyskeratosis Congenita (1) · Fanconi Anemia (1) · Granulomatous Disease, Chronic (1) · Leukocyte adhesion deficiency type 1 (1) · Lymphohistiocytosis, Hemophagocytic (1) · Mucopolysaccharidosis I (1) · Neutropenia, Severe Congenital, Autosomal Recessive 3 (1) · Shwachman-Diamond Syndrome (1) · Thrombasthenia (1) · Wiskott-Aldrich Syndrome (1) · beta-Thalassemia (1)
Albinism (1) · Anemia (1) · Anemia, Hemolytic (1) · Anemia, Hemolytic, Congenital (1) · Anemia, Hypoplastic, Congenital (1) · Blood Coagulation Disorders (1) · Blood Coagulation Disorders, Inherited (1) · Blood Platelet Disorders (1) · Bone Marrow Diseases (1) · Bone Marrow Failure Disorders (1) · Carbohydrate Metabolism, Inborn Errors (1) · Chronic Disease (1) · Congenital Abnormalities (1) · Congenital Bone Marrow Failure Syndromes (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)
Abatacept (1)
Emory University (1)
United States (1)
John T Horan, MD (1)