Genetic Disorder: Clinical Trials

6 trials for Genetic Disorder, newest first

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6 completed. 6 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 36Completed 6

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Trials (filtered) newest first · largest first

All 6 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Investigating the Long-term Efficacy and Safety of Two Doses of NN-220 (Somatropin) in Short Stature Due to Noonan Syndrome
somatropin - Genetic Disorder, Noonan Syndrome
Phase 3CompletedNovo Nordisk A/S512013-08-192020-08-10
Genetic Testing of Noonan Subjects Previously Treated With Norditropin®. An Extension to Trial GHNOO-1658
somatropin - Genetic Disorder, Noonan Syndrome
Phase 3CompletedNovo Nordisk A/S222008-09-012023-08-09
Evaluating Acceptance of New Liquid Somatropin Formulation in Children With Growth Hormone Deficiency
somatropin - Growth Hormone Disorder, Growth Hormone Deficiency in Children
Phase 3CompletedNovo Nordisk A/S1682000-10-232017-02-27
Induction of Puberty With 17-beta Estradiol in Girls With Turner Syndrome
17-beta estradiol - Genetic Disorder, Turner Syndrome
Phase 3CompletedNovo Nordisk A/S501998-07-232017-02-28
Somatropin Effect on Linear Growth and Final Height in Subjects With Noonan Syndrome
somatropin - Genetic Disorder, Noonan Syndrome
Phase 3CompletedNovo Nordisk A/S241990-06-012017-01-18
Use of Somatropin in Turner Syndrome
somatropin - Genetic Disorder, Turner Syndrome
Phase 3CompletedNovo Nordisk A/S571987-09-142017-02-28

Narrower conditions

Genetic Diseases, Inborn (6)  ·  Noonan Syndrome (3)  ·  Turner Syndrome (3)

Broader conditions

Cardiovascular Abnormalities (6)  ·  Cardiovascular Diseases (6)  ·  Congenital Abnormalities (6)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (6)  ·  Heart Defects, Congenital (6)  ·  Heart Diseases (6)  ·  Chromosome Disorders (3)  ·  Connective Tissue Diseases (3)  ·  Craniofacial Abnormalities (3)  ·  Disorders of Sex Development (3)  ·  Endocrine System Diseases (3)  ·  Female Urogenital Diseases (3)  ·  Female Urogenital Diseases and Pregnancy Complications (3)  ·  Gonadal Disorders (3)  ·  Gonadal Dysgenesis (3)

Interventions

Human Growth Hormone (5)  ·  Estradiol (1)

Sponsors

Novo Nordisk A/S (6)

Countries

Sweden (2)  ·  Israel (1)  ·  Japan (1)  ·  Spain (1)  ·  United Kingdom (1)

Results publications

PMID 16203673, PMID 29109363, PMID 32269181, PMID 41285480

NIH funding

2005 (1), 2008 (1)