GBA1 Parkinson Disease: Clinical Trials

2 trials for GBA1 Parkinson Disease, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 not yet recruiting, 1 withdrawn. 1 Not applicable, 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Not applicable1Not yet recruiting 1
Phase 11Withdrawn 1
Phase 21Withdrawn 1

Follow GBA1 Parkinson Disease: new trials by email Literature Review of GBA1 Parkinson Disease trials Research Report on GBA1 Parkinson Disease

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Understanding Alpha-Synuclein Spread in Parkinson's Disease Through Blood Biomarkers and Neuroimaging
brain imaging, blood draw, Skin biopsy - Parkinson's Disease (PD), GBA1 Parkinson Disease
Not applicableNot yet recruitingUniversity of Pavia1602026-05-112026-05-01
A Clinical Trial of CAP-003 Gene Therapy in Adult Patients With GBA1 Associated Parkinson's Disease
gene therapy - GBA1 Parkinson Disease
Phase 1 / Phase 2WithdrawnCapsida Biotherapeutics, Inc.2025-08-182026-06-22

Narrower conditions

Parkinson Disease (2)  ·  Mitochondrial Diseases (1)  ·  REM Sleep Behavior Disorder (1)

Broader conditions

Basal Ganglia Diseases (2)  ·  Brain Diseases (2)  ·  Central Nervous System Diseases (2)  ·  Movement Disorders (2)  ·  Nervous System Diseases (2)  ·  Neurodegenerative Diseases (2)  ·  Parkinsonian Disorders (2)  ·  Synucleinopathies (2)  ·  Mental Disorders (1)  ·  Metabolic Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Parasomnias (1)  ·  REM Sleep Parasomnias (1)  ·  Sleep Wake Disorders (1)

Interventions

Blood Specimen Collection (1)  ·  Genetic Therapy (1)  ·  Neuroimaging (1)

Sponsors

Capsida Biotherapeutics, Inc. (1)  ·  University of Pavia (1)

Countries

Italy (1)  ·  United States (1)

Top investigators

Melanie Brandabur, MD (1)