Down Syndrome: Clinical Trials

1 trial for Down Syndrome, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 terminated. 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 11Terminated 1

Follow Down Syndrome: new trials by email Literature Review of Down Syndrome trials Research Report on Down Syndrome

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Hero: A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics (PK) and Pharmacodynamics (PD) of ION269 in Participants With Down Syndrome (DS) at Risk for Alzheimer's Disease (AD)
ION269 - Alzheimer Disease, Down Syndrome
Phase 1TerminatedIonis Pharmaceuticals, Inc.12024-12-202026-02-20

Narrower conditions

Alzheimer Disease (1)

Broader conditions

Abnormalities, Multiple (1)  ·  Brain Diseases (1)  ·  Central Nervous System Diseases (1)  ·  Chromosome Disorders (1)  ·  Congenital Abnormalities (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Dementia (1)  ·  Genetic Diseases, Inborn (1)  ·  Intellectual Disability (1)  ·  Mental Disorders (1)  ·  Nervous System Diseases (1)  ·  Neurobehavioral Manifestations (1)  ·  Neurocognitive Disorders (1)  ·  Neurodegenerative Diseases (1)  ·  Neurologic Manifestations (1)

Sponsors

Ionis Pharmaceuticals, Inc. (1)

Countries

Spain (1)  ·  United States (1)

NIH funding

2023 (1)