Aplastic Anemia: Clinical Trials

6 trials for Aplastic Anemia, newest first

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6 completed. 6 Phase 3, 4 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 36Completed 6
Phase 24Completed 4

Follow Aplastic Anemia: new trials by email Literature Review of Aplastic Anemia trials Research Report on Aplastic Anemia

Trials (filtered) newest first · largest first

All 6 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Assess Efficacy and Safety of PF-06462700 in Japanese Participants With Aplastic Anemia
PF-06462700 - Aplastic Anemia
Phase 3CompletedPfizer32020-07-252022-04-27
Study of AMG531 (Romiplostim) in Patients With Aplastic Anemia
Romiplostim - Aplastic Anemia
Phase 2 / Phase 3CompletedKyowa Kirin Co., Ltd.242019-12-032022-05-26
Study of AMG531(Romiplostim) in Patients With Aplastic Anemia
Romiplostim - Aplastic Anemia
Phase 2 / Phase 3CompletedKyowa Kirin Co., Ltd.172019-04-252022-05-26
Study of Romiplostim(AMG531) in Subjects With Aplastic Anemia
Romiplostim - Aplastic Anemia
Phase 2 / Phase 3CompletedKyowa Kirin Co., Ltd.462016-05-012024-07-16
Stem Cell Transplant (SCT) for Dyskeratosis Congenita or SAA
Campath 1H, Cyclophosphamide, Fludarabine - Dyskeratosis Congenita, Aplastic Anemia
Phase 2 / Phase 3CompletedMasonic Cancer Center, University of Minnesota362007-08-012017-12-05
Phase III Randomized Study of Cyclophosphamide With or Without Antithymocyte Globulin Before Bone Marrow Transplantation in Patients With Aplastic Anemia
Anti-thymocyte globulin, Cyclophosphamide, Bone marrow transplantation - Aplastic Anemia
Phase 3CompletedRoswell Park Cancer Institute2241998-09-012018-03-12

Narrower conditions

Anemia, Aplastic (6)  ·  Dyskeratosis Congenita (1)  ·  Hematologic Diseases (1)  ·  Rare Diseases (1)

Broader conditions

Anemia (6)  ·  Bone Marrow Diseases (6)  ·  Bone Marrow Failure Disorders (6)  ·  Hemic and Lymphatic Diseases (6)  ·  Hematologic Diseases (5)  ·  Congenital Abnormalities (1)  ·  Congenital Bone Marrow Failure Syndromes (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Disease Attributes (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Pathologic Processes (1)  ·  Pathological Conditions, Signs and Symptoms (1)  ·  Skin Abnormalities (1)  ·  Skin Diseases (1)

Interventions

romiplostim (3)  ·  Antilymphocyte Serum (2)  ·  Bone Marrow Transplantation (2)  ·  Cyclophosphamide (2)  ·  Alemtuzumab (1)  ·  Methylprednisolone (1)  ·  Radiotherapy (1)  ·  Stem Cell Transplantation (1)  ·  Whole-Body Irradiation (1)  ·  fludarabine (1)  ·  fludarabine phosphate (1)  ·  thymoglobulin (1)

Sponsors

Kyowa Kirin Co., Ltd. (3)  ·  Masonic Cancer Center, University of Minnesota (1)  ·  Pfizer (1)  ·  Roswell Park Cancer Institute (1)

Countries

Japan (4)  ·  United States (2)  ·  South Korea (1)

Top investigators

Jakub Tolar, M.D., Ph.D. (1)

Results publications

PMID 20383216, PMID 36441357, PMID 40593138