APECED: Clinical Trials

4 trials for APECED, newest first

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3 completed, 1 recruiting. .

Follow APECED: new trials by email Literature Review of APECED trials Research Report on APECED

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Conception of a Diagnosis, Prognosis and Therapeutic Decision Tool for Patients With Autoimmunity and Inflammation
Collection of samples - Autoimmune Lymphoproliferative Syndrome, Autoimmune Cytopenia
CompletedInstitut National de la Santé Et de la Recherche Médicale, France3252021-09-072026-09-18
Participation in a Research Registry for Immune Disorders
Primary Immunodeficiencies, APECED
CompletedNational Human Genome Research Institute (NHGRI)7162013-09-302023-07-20
Natural History of Individuals With Immune System Problems That Lead to Fungal Infections
Chronic Mucocutaneous Candidiasis, Invasive Aspergillosis
RecruitingNational Institute of Allergy and Infectious Diseases (NIAID)12002012-11-052026-08-24
Evaluation Genotypic, Phenotypic and Prognosis APECED Syndrome
APECED
CompletedUniversity Hospital, Lille292009-07-302025-12-26

Narrower conditions

Polyendocrinopathies, Autoimmune (4)  ·  Primary Immunodeficiency Diseases (2)  ·  Arthritis, Juvenile (1)  ·  Autoimmune Diseases (1)  ·  Autoimmune Lymphoproliferative Syndrome (1)  ·  Autoimmune enteropathy (1)  ·  Candidiasis, Chronic Mucocutaneous (1)  ·  Diabetes Mellitus, Type 1 (1)  ·  Hepatitis, Autoimmune (1)  ·  Invasive Fungal Infections (1)  ·  Lupus Erythematosus, Systemic (1)  ·  Lymphohistiocytosis, Hemophagocytic (1)  ·  Mycoses (1)  ·  Purpura, Thrombocytopenic, Idiopathic (1)  ·  Wiskott-Aldrich Syndrome (1)

Broader conditions

Endocrine System Diseases (4)  ·  Immune System Diseases (4)  ·  Autoimmune Diseases (3)  ·  Blood Coagulation Disorders (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Cytopenia (2)  ·  Genetic Diseases, Inborn (2)  ·  Hematologic Diseases (2)  ·  Hemic and Lymphatic Diseases (2)  ·  Hemorrhagic Disorders (2)  ·  Immunologic Deficiency Syndromes (2)  ·  Pathologic Processes (2)  ·  Pathological Conditions, Signs and Symptoms (2)  ·  Skin and Connective Tissue Diseases (2)  ·  Arthritis (1)

Sponsors

Institut National de la Santé Et de la Recherche Médicale, France (1)  ·  National Human Genome Research Institute (NHGRI) (1)  ·  National Institute of Allergy and Infectious Diseases (NIAID) (1)  ·  University Hospital, Lille (1)

Countries

France (2)  ·  United States (2)

Top investigators

Elizabeth K Garabedian, R.N. (1)  ·  Emmanuelle Proust-Lemoine, MD (1)  ·  Michail S Lionakis, M.D. (1)

Results publications

PMID 29619656, PMID 31095438, PMID 32557834, PMID 36875114, PMID 38605470