2 recruiting, 1 completed, 1 withdrawn. 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Withdrawn 1 |
Follow ALD (Adrenoleukodystrophy): new trials by email Literature Review of ALD (Adrenoleukodystrophy) trials Research Report on ALD (Adrenoleukodystrophy)
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Study to Assess PXL065 in Subjects With Adrenomyeloneuropathy (AMN) Form of X-linked Adrenoleukodystrophy (X-ALD or ALD) PXL065 - ALD (Adrenoleukodystrophy) | Phase 2 | Withdrawn | Poxel SA | 2023-09-01 | 2024-12-16 | |
| Adrenoleukodystrophy National Registry Study Medical Record Abstraction, Biospecimen Sample Collection - ALD (Adrenoleukodystrophy), Adrenoleukodystrophy | Recruiting | Masonic Cancer Center, University of Minnesota | 1000 | 2019-05-01 | 2026-05-12 | |
| LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies Leukodystrophy, White Matter Disease | Completed | Children's Hospital of Philadelphia | 236 | 2017-01-06 | 2025-11-10 | |
| The Myelin Disorders Biorepository Project Leukodystrophy, White Matter Disease | Recruiting | Children's Hospital of Philadelphia | 12000 | 2016-12-08 | 2025-10-23 |
Adrenoleukodystrophy (4) · Aicardi-Goutieres syndrome (2) · Alexander Disease (2) · Alexanders leukodystrophy (2) · Allan-Herndon-Dudley syndrome (2) · Attention Deficit Disorder with Hyperactivity (2) · CADASIL (2) · Canavan Disease (2) · Charcot-Marie-Tooth Disease (2) · Cockayne Syndrome (2) · Gangliosidoses (2) · Gangliosidoses, GM2 (2) · Leukodystrophy, Globoid Cell (2) · Leukodystrophy, Hypomyelinating, 5 (2) · Leukodystrophy, Hypomyelinating, 6 (2)
Adrenal Gland Diseases (4) · Adrenal Insufficiency (4) · Brain Diseases (4) · Brain Diseases, Metabolic (4) · Brain Diseases, Metabolic, Inborn (4) · Central Nervous System Diseases (4) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4) · Demyelinating Diseases (4) · Endocrine System Diseases (4) · Genetic Diseases, Inborn (4) · Genetic Diseases, X-Linked (4) · Hereditary Central Nervous System Demyelinating Diseases (4) · Heredodegenerative Disorders, Nervous System (4) · Intellectual Disability (4) · Metabolic Diseases (4)
Children's Hospital of Philadelphia (2) · Masonic Cancer Center, University of Minnesota (1) · Poxel SA (1)
United States (3)
U01NS106845 (1), U54NS115052 (1)