ALD (Adrenoleukodystrophy): Clinical Trials

1 trial for ALD (Adrenoleukodystrophy), newest first

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1 withdrawn. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Withdrawn 1

Follow ALD (Adrenoleukodystrophy): new trials by email Literature Review of ALD (Adrenoleukodystrophy) trials Research Report on ALD (Adrenoleukodystrophy)

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study to Assess PXL065 in Subjects With Adrenomyeloneuropathy (AMN) Form of X-linked Adrenoleukodystrophy (X-ALD or ALD)
PXL065 - ALD (Adrenoleukodystrophy)
Phase 2WithdrawnPoxel SA2023-09-012024-12-16

Narrower conditions

Adrenoleukodystrophy (1)

Broader conditions

Adrenal Gland Diseases (1)  ·  Adrenal Insufficiency (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Demyelinating Diseases (1)  ·  Endocrine System Diseases (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Hereditary Central Nervous System Demyelinating Diseases (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Intellectual Disability (1)  ·  Leukoencephalopathies (1)

Sponsors

Poxel SA (1)