Wilson Disease: Clinical Trials

2 trials for Wilson Disease, newest first

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2 completed. 2 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 32Completed 2

Follow Wilson Disease: new trials by email Literature Review of Wilson Disease trials Research Report on Wilson Disease

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Trientine Tetrahydrochloride (TETA 4HCL) for the Treatment of Wilson's Disease
Penicillamine (D1-W12), TETA 4HCL (W12-60), Penicillamine (W12-W60) - Wilson Disease
Phase 3CompletedOrphalan772018-09-032025-07-02
Study of Tetrathiomolybdate in Patients With Wilson Disease
tetrathiomolybdate, trientine - Wilson Disease
Phase 3CompletedNational Center for Research Resources (NCRR)901994-01-012006-05-09

Narrower conditions

Hepatolenticular Degeneration (2)  ·  Metabolism, Inborn Errors (1)  ·  Rare Diseases (1)

Broader conditions

Basal Ganglia Diseases (2)  ·  Brain Diseases (2)  ·  Brain Diseases, Metabolic (2)  ·  Brain Diseases, Metabolic, Inborn (2)  ·  Central Nervous System Diseases (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Digestive System Diseases (2)  ·  Genetic Diseases, Inborn (2)  ·  Heredodegenerative Disorders, Nervous System (2)  ·  Liver Diseases (2)  ·  Metabolic Diseases (2)  ·  Metal Metabolism, Inborn Errors (2)  ·  Movement Disorders (2)  ·  Nervous System Diseases (2)  ·  Neurodegenerative Diseases (2)

Interventions

Penicillamine (1)  ·  Trientine (1)  ·  tetrathiomolybdate (1)

Sponsors

National Center for Research Resources (NCRR) (1)  ·  Orphalan (1)

Countries

United States (2)  ·  Belgium (1)  ·  Brazil (1)  ·  Denmark (1)  ·  France (1)  ·  Germany (1)  ·  Italy (1)  ·  Poland (1)  ·  United Kingdom (1)

Top investigators

George J. Brewer (1)

Results publications

PMID 36183738, PMID 39139457, PMID 41831608